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1دورية أكاديمية
المؤلفون: Sara H. Osum, Eunice I. Oribamise, Stanislas M.A.S. Corbière, Mandy Taisto, Tyler Jubenville, Alex Coutts, Mark N. Kirstein, James Fisher, Christopher Moertel, Ming Du, David Bedwell, David A. Largaespada, Adrienne L. Watson
المصدر: Molecular Therapy: Nucleic Acids, Vol 33, Iss , Pp 227-239 (2023)
مصطلحات موضوعية: MT: Delivery Strategies, neurofibromatosis, nonsense suppression, minipig, preclinical models, pharmacokinetics, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Núria Catasús, Inma Rosas, Sandra Bonache, Alex Negro, Miguel Torres-Martin, Adrià Plana-Pla, Hector Salvador, Eduard Serra, Ignacio Blanco, Elisabeth Castellanos
المصدر: Molecular Therapy: Nucleic Acids, Vol 30, Iss , Pp 493-505 (2022)
مصطلحات موضوعية: MT: oligonucleotides: therapies and applications, neurofibromatosis type 2, antisense therapy, antisense oligomers, genotype-phenotype correlations, Merlin, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: André Leier, Marc Moore, Hui Liu, Michael Daniel, Alexis M. Hyde, Ludwine Messiaen, Bruce R. Korf, Jamuna Selvakumaran, Lukasz Ciszewski, Laura Lambert, Jeremy Foote, Margaret R. Wallace, Robert A. Kesterson, George Dickson, Linda Popplewell, Deeann Wallis
المصدر: Molecular Therapy: Nucleic Acids, Vol 28, Iss , Pp 261-278 (2022)
مصطلحات موضوعية: MT: Oligonucletides: Therapies and Applications, neurofibromatosis type I, Ras/Raf/MAPK pathway, exon skipping, antisense oligo therapeutics, animal models, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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4
المؤلفون: Ulrich Müller, Linda Popplewell, Tatiana T. Marquez Lago, Deeann Wallis, Ann T. Chen, Bruce R. Korf, André Leier, Robert A. Kesterson, David M. Bedwell, Kim M. Keeling, George Dickson, Jiangbing Zhou
المصدر: Molecular Therapy: Nucleic Acids, Vol 20, Iss, Pp 739-753 (2020)
Molecular Therapy. Nucleic Acidsمصطلحات موضوعية: 0301 basic medicine, Bioinformatics, medicine.disease_cause, Article, Viral vector, 03 medical and health sciences, 0302 clinical medicine, Drug Discovery, medicine, CRISPR, Loss function, Neurofibromatosis type I, Mutation, biology, business.industry, lcsh:RM1-950, Genetic disorder, medicine.disease, Neurofibromin 1, Exon skipping, 030104 developmental biology, lcsh:Therapeutics. Pharmacology, 030220 oncology & carcinogenesis, biology.protein, Molecular Medicine, business