المؤلفون: Esposito F; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Dell'Aquila F; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy; Medical Genetics, Department of Advanced Biomedical Sciences, University of Naples Federico II, Naples, Italy., Rhiel M; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany; Center for Chronic Immunodeficiency (CCI), Medical Center - University of Freiburg, Freiburg, Germany., Auricchio S; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Chmielewski KO; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany; Center for Chronic Immunodeficiency (CCI), Medical Center - University of Freiburg, Freiburg, Germany; PhD Program, Faculty of Biology, University of Freiburg, Freiburg, Germany., Andrieux G; Institute of Medical Bioinformatics and Systems Medicine, Medical Center - University of Freiburg, Freiburg, Germany; Faculty of Medicine, University of Freiburg, Freiburg, Germany., Ferla R; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Horrach PS; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Padmanabhan A; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Di Cunto R; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Notaro S; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Santeularia ML; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Boerries M; Institute of Medical Bioinformatics and Systems Medicine, Medical Center - University of Freiburg, Freiburg, Germany; Faculty of Medicine, University of Freiburg, Freiburg, Germany; German Cancer Consortium (DKTK), Partner site Freiburg, a partnership between DKFZ and Medical Center - University of Freiburg, Freiburg, Germany., Dell'Anno M; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Nusco E; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Padula A; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Nutarelli S; Department of Life Science and Public Health, Catholic University of the Sacred Heart, Rome, Italy., Cornu TI; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany; Center for Chronic Immunodeficiency (CCI), Medical Center - University of Freiburg, Freiburg, Germany; Faculty of Medicine, University of Freiburg, Freiburg, Germany., Sorrentino NC; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy; Department of Clinical Medicine and Surgery, University of Naples Federico II, Naples, Italy., Piccolo P; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy., Trapani I; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy; Medical Genetics, Department of Advanced Biomedical Sciences, University of Naples Federico II, Naples, Italy., Cathomen T; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany; Center for Chronic Immunodeficiency (CCI), Medical Center - University of Freiburg, Freiburg, Germany; Faculty of Medicine, University of Freiburg, Freiburg, Germany; German Cancer Consortium (DKTK), Partner site Freiburg, a partnership between DKFZ and Medical Center - University of Freiburg, Freiburg, Germany., Auricchio A; Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy; Gene Therapy Joint lab, Dept. of Advanced Biomedical Sciences and Dept. of Translational Medicine, University of Naples 'Federico II', Naples, Italy. Electronic address: auricchio@tigem.it.

المصدر: Cell reports. Medicine [Cell Rep Med] 2024 Jul 16; Vol. 5 (7), pp. 101619. Date of Electronic Publication: 2024 Jun 18.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 101766894 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-3791 (Electronic) Linking ISSN: 26663791 NLM ISO Abbreviation: Cell Rep Med Subsets: MEDLINE

مواضيع طبية MeSH: Dependovirus*/genetics , Liver*/metabolism , Liver*/pathology , Disease Models, Animal* , Genetic Vectors*/genetics, Animals ; Mice ; Hepatocytes/metabolism ; Humans ; Virus Integration/genetics ; CRISPR-Cas Systems/genetics ; Transgenes ; Genetic Diseases, Inborn/genetics ; Genetic Diseases, Inborn/therapy ; Genetic Therapy/methods ; Mice, Inbred C57BL ; Albumins/genetics ; Albumins/metabolism