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1دورية أكاديمية
المؤلفون: Bailey H. Duhon, Eric C. Bielefeld, Yin Ren, Jerusha Naidoo
المصدر: Frontiers in Audiology and Otology, Vol 2 (2024)
مصطلحات موضوعية: gene therapy, sensorineural hearing loss, AAV vectors, clinical trials, spiral ganglion neurons, hair cells, Medicine
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Ambra Cappelletto, Edoardo Alfì, Nina Volf, Thi Van Anh Vu, Francesca Bortolotti, Giulio Ciucci, Simone Vodret, Marco Fantuz, Martina Perin, Andrea Colliva, Giacomo Rozzi, Matilde Rossi, Giulia Ruozi, Lorena Zentilin, Roman Vuerich, Daniele Borin, Romano Lapasin, Silvano Piazza, Mattia Chiesa, Daniela Lorizio, Luca Triboli, Sandeep Kumar, Gaia Morello, Claudio Tripodo, Maurizio Pinamonti, Giulia Maria Piperno, Federica Benvenuti, Alessandra Rustighi, Hanjoong Jo, Stefano Piccolo, Giannino Del Sal, Alessandro Carrer, Mauro Giacca, Serena Zacchigna
المصدر: Journal of Experimental & Clinical Cancer Research, Vol 43, Iss 1, Pp 1-14 (2024)
مصطلحات موضوعية: In vivo screening, Cancer, Cell invasiveness, AAV vectors, Gene therapy, Biotherapeutics, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1756-9966
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3دورية أكاديمية
المؤلفون: Junping Zhang, Dylan A. Frabutt, Matthew Chrzanowski, Ning Li, Lohra M. Miller, Jiahe Tian, Patrick L. Mulcrone, Anh K. Lam, Benjamin E. Draper, Martin F. Jarrold, Roland W. Herzog, Weidong Xiao
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101206- (2024)
مصطلحات موضوعية: Adeno-associated virus, self-complementary AAV vectors, covalently closed-end double-stranded AAV, transduction, genome integrity, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Martin Bentler, Romain Hardet, Moritz Ertelt, Daniela Rudolf, Dorota Kaniowska, Andreas Schneider, Florian W.R. Vondran, Clara T. Schoeder, Marion Delphin, Julie Lucifora, Michael Ott, Ulrich T. Hacker, Sahil Adriouch, Hildegard Büning
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 576-592 (2023)
مصطلحات موضوعية: AAV vectors, innate immune responses, adaptive immune responses, Toll-like receptor, MyD88, capsid engineering, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Jakob Shoti, Keyun Qing, Geoffrey D. Keeler, Dongsheng Duan, Barry J. Byrne, Arun Srivastava
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 31, Iss , Pp 101147- (2023)
مصطلحات موضوعية: AAV vectors, gene transfer, gene expression, gene therapy, muscle diseases, capsid-modifications, genome-modifications, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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6دورية أكاديمية
المؤلفون: Arun Srivastava
المصدر: Molecular Therapy: Nucleic Acids, Vol 32, Iss , Pp 949-959 (2023)
مصطلحات موضوعية: MT: Delivery Strategies, AAV vectors, gene expression, immune response, human-tropism, gene therapy, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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7دورية أكاديمية
المؤلفون: Fuhua Wu, Shuang Luo, Yongshun Zhang, Yangsen Ou, Hairui Wang, Zhaofei Guo, Chunting He, Shuting Bai, Penghui He, Min Jiang, Xiaoyan Chen, Guangsheng Du, Xun Sun
المصدر: Acta Pharmaceutica Sinica B, Vol 13, Iss 5, Pp 2219-2233 (2023)
مصطلحات موضوعية: AAV vectors, Capsid engineering, Vaccine, Antigen structure design, SARS-CoV-2, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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8دورية أكاديمية
المؤلفون: Rita Ferla, Fabio Dell’Aquila, Monica Doria, Maria Ferraiuolo, Alessia Noto, Fabiana Grazioli, Virginia Ammendola, Francesco Testa, Paolo Melillo, Carolina Iodice, Giulia Risca, Novella Tedesco, Pierre Romain le Brun, Enrico Maria Surace, Francesca Simonelli, Stefania Galimberti, Maria Grazia Valsecchi, Jean-Brice Marteau, Philippe Veron, Stefano Colloca, Alberto Auricchio
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 396-411 (2023)
مصطلحات موضوعية: Usher Syndrome type 1B, retinitis pigmentosa, gene therapy, dual AAV vectors, non-human primates, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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9دورية أكاديمية
المؤلفون: Cappelletto, Ambra, Alfì, EdoardoAff1, Aff2, Volf, Nina, Vu, Thi Van Anh, Bortolotti, Francesca, Ciucci, Giulio, Vodret, Simone, Fantuz, MarcoAff3, Aff4, Perin, Martina, Colliva, Andrea, Rozzi, Giacomo, Rossi, Matilde, Ruozi, Giulia, Zentilin, Lorena, Vuerich, RomanAff1, Aff2, Borin, Daniele, Lapasin, Romano, Piazza, SilvanoAff7, Aff8, Chiesa, Mattia, Lorizio, Daniela, Triboli, LucaAff2, Aff10, Kumar, Sandeep, Morello, Gaia, Tripodo, ClaudioAff12, Aff13, Pinamonti, Maurizio, Piperno, Giulia Maria, Benvenuti, Federica, Rustighi, AlessandraAff2, Aff10, Jo, Hanjoong, Piccolo, Stefano, Del Sal, GianninoAff2, Aff10, Aff16, Carrer, AlessandroAff3, Aff4, Giacca, MauroAff5, Aff17, Aff18, Zacchigna, SerenaAff1, Aff18, IDs13046023029424_cor34
المصدر: Journal of Experimental & Clinical Cancer Research. 43(1)
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10دورية أكاديمية
المؤلفون: Ren Song, Katja Pekrun, Themasap A. Khan, Feijie Zhang, Sergiu P. Paşca, Mark A. Kay
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 73-88 (2022)
مصطلحات موضوعية: blood brain barrier, CNS capsids, transwell, human BBB, central nervous system, chimeric AAV vectors, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource