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1دورية أكاديمية
المؤلفون: Qi Tang, Hassan H. Fakih, Mohammad Zain UI Abideen, Samuel R. Hildebrand, Khashayar Afshari, Katherine Y. Gross, Jacquelyn Sousa, Allison S. Maebius, Christina Bartholdy, Pia Pernille Søgaard, Malene Jackerott, Vignesh Hariharan, Ashley Summers, Xueli Fan, Ken Okamura, Kathryn R. Monopoli, David A. Cooper, Dimas Echeverria, Brianna Bramato, Nicholas McHugh, Raymond C. Furgal, Karen Dresser, Sarah J. Winter, Annabelle Biscans, Jane Chuprin, Nazgol-Sadat Haddadi, Shany Sherman, Ümmügülsüm Yıldız-Altay, Mehdi Rashighi, Jillian M. Richmond, Claire Bouix-Peter, Carine Blanchard, Adam Clauss, Julia F. Alterman, Anastasia Khvorova, John E. Harris
المصدر: Nature Communications, Vol 14, Iss 1, Pp 1-15 (2023)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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2دورية أكاديمية
المؤلفون: Kyounghee Min, Batuhan Yenilmez, Mark Kelly, Dimas Echeverria, Michael Elleby, Lawrence M Lifshitz, Naideline Raymond, Emmanouela Tsagkaraki, Shauna M Harney, Chloe DiMarzio, Hui Wang, Nicholas McHugh, Brianna Bramato, Brett Morrison, Jeffery D Rothstein, Anastasia Khvorova, Michael P Czech
المصدر: eLife, Vol 12 (2024)
مصطلحات موضوعية: NASH, NAFLD, stellate cells, liver fibrosis, RNAi therapeutics, AAV, Medicine, Science, Biology (General), QH301-705.5
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Shun-Yun Cheng, Jillian Caiazzi, Annabelle Biscans, Julia F. Alterman, Dimas Echeverria, Nicholas McHugh, Matthew Hassler, Samson Jolly, Delaney Giguere, Joris Cipi, Anastasia Khvorova, Claudio Punzo
المصدر: Molecular Therapy: Nucleic Acids, Vol 35, Iss 1, Pp 102088- (2024)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, siRNA, photoreceptors, gene silencing, IRD, inherited retinal dystrophy, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Kathryn R. Monopoli, Dmitry Korkin, Anastasia Khvorova
المصدر: Molecular Therapy: Nucleic Acids, Vol 33, Iss , Pp 93-109 (2023)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, siRNA, RNA interference, machine learning, artificial intelligence, oligonucleotides, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Hassan H. Fakih, Qi Tang, Ashley Summers, Minwook Shin, Julianna E. Buchwald, Rosemary Gagnon, Vignesh N. Hariharan, Dimas Echeverria, David A. Cooper, Jonathan K. Watts, Anastasia Khvorova, Hanadi F. Sleiman
المصدر: Molecular Therapy: Nucleic Acids, Vol 34, Iss , Pp 102080- (2023)
مصطلحات موضوعية: MT: Delivery Strategies, oligonucleotide therapeutics, siRNAs, protein binding, albumin, drug delivery, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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6دورية أكاديمية
المؤلفون: Hector Ribeiro Benatti, Rachel D. Prestigiacomo, Toloo Taghian, Rachael Miller, Robert King, Matthew J. Gounis, Ugur Celik, Stephanie Bertrand, Susan Tuominen, Lindsey Bierfeldt, Elizabeth Parsley, Jillian Gallagher, Erin F. Hall, Abigail W. McElroy, Miguel Sena-Esteves, Anastasia Khvorova, Neil Aronin, Heather L. Gray-Edwards
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 31, Iss , Pp 101122- (2023)
مصطلحات موضوعية: oligonucleotide safety assessment, large animal model, CNS drug administration, CSF drug delivery, i.c.v. injection, Ommaya reservoir, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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7دورية أكاديمية
المؤلفون: Faith Conroy, Rachael Miller, Julia F. Alterman, Matthew R. Hassler, Dimas Echeverria, Bruno M. D. C. Godinho, Emily G. Knox, Ellen Sapp, Jaquelyn Sousa, Ken Yamada, Farah Mahmood, Adel Boudi, Kimberly Kegel-Gleason, Marian DiFiglia, Neil Aronin, Anastasia Khvorova, Edith L. Pfister
المصدر: Nature Communications, Vol 13, Iss 1, Pp 1-14 (2022)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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8دورية أكاديمية
المؤلفون: Bruno M.D.C. Godinho, Emily G. Knox, Samuel Hildebrand, James W. Gilbert, Dimas Echeverria, Zachary Kennedy, Reka A. Haraszti, Chantal M. Ferguson, Andrew H. Coles, Annabelle Biscans, Jillian Caiazzi, Julia F. Alterman, Matthew R. Hassler, Anastasia Khvorova
المصدر: Molecular Therapy: Nucleic Acids, Vol 29, Iss , Pp 116-132 (2022)
مصطلحات موضوعية: oligonucleotide, PEGylation, extrahepatic, GalNAc, siRNA conjugates, RNA interference, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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9دورية أكاديمية
المؤلفون: Sarah M. Davis, Vignesh N. Hariharan, Agnes Lo, Anton A. Turanov, Dimas Echeverria, Jacquelyn Sousa, Nicholas McHugh, Annabelle Biscans, Julia F. Alterman, S. Ananth Karumanchi, Melissa J. Moore, Anastasia Khvorova
المصدر: Molecular Therapy: Nucleic Acids, Vol 29, Iss , Pp 135-149 (2022)
مصطلحات موضوعية: siRNA therapeutics, oligonucleotides, preeclampsia, oligonucleotide drug design, extrahepatic delivery, angiogenic disorders, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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10دورية أكاديمية
المؤلفون: Bruno M. D. C. Godinho, Anastasia Khvorova
المصدر: Saúde & Tecnologia, Iss 21 (2022)
مصطلحات موضوعية: ARN interferência, siRNA, miRNA, Oligonucleotídios para terapêutica, Desenvolvimento de novos fármacos, Medicine
وصف الملف: electronic resource