-
1دورية أكاديمية
المؤلفون: Katelyn E. Masiuk, Ruixue Zhang, Kyle Osborne, Roger P. Hollis, Beatriz Campo-Fernandez, Donald B. Kohn
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 13, Iss , Pp 390-398 (2019)
وصف الملف: electronic resource
-
2دورية أكاديمية
المؤلفون: Caroline Y. Kuo, Joseph D. Long, Beatriz Campo-Fernandez, Satiro de Oliveira, Aaron R. Cooper, Zulema Romero, Megan D. Hoban, Alok V. Joglekar, Georgia R. Lill, Michael L. Kaufman, Sorel Fitz-Gibbon, Xiaoyan Wang, Roger P. Hollis, Donald B. Kohn
المصدر: Cell Reports, Vol 23, Iss 9, Pp 2606-2616 (2018)
مصطلحات موضوعية: X-linked hyper-IgM syndrome, gene editing, gene therapy, primary immunodeficiency, CD40 ligand, hematopoietic stem cell, CRISPR/Cas9, TALEN, Biology (General), QH301-705.5
وصف الملف: electronic resource
-
3دورية أكاديمية
المؤلفون: Zulema Romero, Beatriz Campo-Fernandez, Jennifer Wherley, Michael L Kaufman, Fabrizia Urbinati, Aaron R Cooper, Megan D Hoban, Kismet M Baldwin, Dianne Lumaquin, Xiaoyan Wang, Shantha Senadheera, Roger P Hollis, Donald B Kohn
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 2, Iss , Pp - (2015)
وصف الملف: electronic resource
-
4دورية أكاديمية
المؤلفون: Valerie Podhraski, Beatriz Campo-Fernandez, Hildegard Wörle, Paolo Piatti, Harald Niederegger, Günther Böck, Dmitry V Fyodorov, Alexandra Lusser
المصدر: PLoS ONE, Vol 5, Iss 4, p e10120 (2010)
وصف الملف: electronic resource
-
5
المؤلفون: Antoni Ribas, Beata Berent-Maoz, Paula J. Kaplan-Lefko, Paula Cabrera, Xiaoyan Wang, Donald B. Kohn, Begonya Comin-Anduix, David Baltimore, Owen N. Witte, Lili Yang, Alexander Nguyen, Celia Adelson, Eric H. Gschweng, Kenneth Cornetta, Daniela Bischof, Beatriz Campo-Fernandez, Roger P. Hollis, Gay M. Crooks, Amelie Montel-Hagen, Christopher S. Seet, Brad Bolon, Jeffrey L. Goodwin, Justin D. Saco, Mignonette H. Macabali, Jia Pang, Marie Desiles S. Komenan, Agustin Vega-Crespo, Nhat A. Truong, Gardenia C. Cheung-Lau, James McCabe, Ameya S. Champhekar, Ruixue Zhang, Salemiz Sandoval, Paige E. Krystofinski, Angel Garcia-Diaz, Giulia Parisi, Cristina Puig-Saus
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a236dda1faa85487df2772f809b017e3
https://doi.org/10.1158/1078-0432.22468605.v1 -
6
المؤلفون: Antoni Ribas, Beata Berent-Maoz, Paula J. Kaplan-Lefko, Paula Cabrera, Xiaoyan Wang, Donald B. Kohn, Begonya Comin-Anduix, David Baltimore, Owen N. Witte, Lili Yang, Alexander Nguyen, Celia Adelson, Eric H. Gschweng, Kenneth Cornetta, Daniela Bischof, Beatriz Campo-Fernandez, Roger P. Hollis, Gay M. Crooks, Amelie Montel-Hagen, Christopher S. Seet, Brad Bolon, Jeffrey L. Goodwin, Justin D. Saco, Mignonette H. Macabali, Jia Pang, Marie Desiles S. Komenan, Agustin Vega-Crespo, Nhat A. Truong, Gardenia C. Cheung-Lau, James McCabe, Ameya S. Champhekar, Ruixue Zhang, Salemiz Sandoval, Paige E. Krystofinski, Angel Garcia-Diaz, Giulia Parisi, Cristina Puig-Saus
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0977b77b6344a53461ba7d218f922c66
https://doi.org/10.1158/1078-0432.c.6527007.v1 -
7
المؤلفون: Rebecca A. Sosa, Thomas Mone, Bita V. Naini, Donald B. Kohn, Elaine F. Reed, Kristina Wheeler, Beatriz Campo-Fernandez, Alejandra Davila, Donald J. Chaffin, Joseph DiNorcia, Fady M. Kaldas, Aaron Cohen, Erik L. Lum, Jeffrey L. Veale, Neil M. Kogut
المصدر: Transplantation.
مصطلحات موضوعية: Transplantation
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::e33e1272679abda044361dddfd1b4821
https://pubmed.ncbi.nlm.nih.gov/35974436 -
8
المؤلفون: Shanna L. White, Thomas D. Lee, Traci Toy, Judith E. Carroll, Lilian Polsky, Beatriz Campo Fernandez, Alejandra Davila, Donald B. Kohn, Vivian Y. Chang
المصدر: Blood advances, vol 6, iss 21
مصطلحات موضوعية: Pediatric, Transplantation, Human Genome, Hematology, Genetic Therapy, Regenerative Medicine, Stem Cell Research, Good Health and Well Being, Stem Cell Research - Nonembryonic - Human, Genetics, Humans, Severe Combined Immunodeficiency, Clonal Hematopoiesis, Child, Busulfan, Cancer, Biotechnology
وصف الملف: application/pdf
-
9
المؤلفون: Donald B. Kohn, Claire Booth, Kit L. Shaw, Jinhua Xu-Bayford, Elizabeth Garabedian, Valentina Trevisan, Denise A. Carbonaro-Sarracino, Kajal Soni, Dayna Terrazas, Katie Snell, Alan Ikeda, Diego Leon-Rico, Theodore B. Moore, Karen F. Buckland, Ami J. Shah, Kimberly C. Gilmour, Satiro De Oliveira, Christine Rivat, Gay M. Crooks, Natalia Izotova, John Tse, Stuart Adams, Sally Shupien, Hilory Ricketts, Alejandra Davila, Chilenwa Uzowuru, Amalia Icreverzi, Provaboti Barman, Beatriz Campo Fernandez, Roger P. Hollis, Maritess Coronel, Allen Yu, Krista M. Chun, Christian E. Casas, Ruixue Zhang, Serena Arduini, Frances Lynn, Mahesh Kudari, Andrea Spezzi, Marco Zahn, Rene Heimke, Ivan Labik, Roberta Parrott, Rebecca H. Buckley, Lilith Reeves, Kenneth Cornetta, Robert Sokolic, Michael Hershfield, Manfred Schmidt, Fabio Candotti, Harry L. Malech, Adrian J. Thrasher, H. Bobby Gaspar
المصدر: N Engl J Med
The New England journal of medicine, vol 384, iss 21مصطلحات موضوعية: Adenosine Deaminase, Genetic enhancement, 030204 cardiovascular system & hematology, Regenerative Medicine, Medical and Health Sciences, 0302 clinical medicine, Adenosine deaminase, Stem Cell Research - Nonembryonic - Human, Agammaglobulinemia, immune system diseases, Medicine, Prospective Studies, 030212 general & internal medicine, Child, 6.2 Cellular and gene therapies, biology, Hematopoietic Stem Cell Transplantation, hemic and immune systems, Gene Therapy, General Medicine, Progression-Free Survival, Child, Preschool, Development of treatments and therapeutic interventions, Autologous, Biotechnology, congenital, hereditary, and neonatal diseases and abnormalities, Adolescent, Genetic Vectors, Transplantation, Autologous, Article, 03 medical and health sciences, Clinical Research, General & Internal Medicine, Genetics, Humans, Lymphocyte Count, Preschool, Transplantation, Severe combined immunodeficiency, 5.2 Cellular and gene therapies, business.industry, Extramural, Lentivirus, Evaluation of treatments and therapeutic interventions, Infant, nutritional and metabolic diseases, Genetic Therapy, Stem Cell Research, medicine.disease, Adenosine deaminase deficiency, enzymes and coenzymes (carbohydrates), Good Health and Well Being, Primary immunodeficiency, Cancer research, biology.protein, Severe Combined Immunodeficiency, business, Ex vivo
وصف الملف: application/pdf
-
10
المؤلفون: Grace McAuley, Gloria Yiu, Gregory A. Newby, Beatriz Campo Fernandez, Xiaomeng Wu, Patrick Chang, Kelcee Everette, Zulema Romero Garcia, David R. Liu, Gay M. Crooks, Donald B. Kohn
المصدر: Blood. 140:1641-1642
مصطلحات موضوعية: Immunology, Cell Biology, Hematology, Biochemistry
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::c333c038dc239f5bf60286bb6611c2f6
https://doi.org/10.1182/blood-2022-170634