المؤلفون: Bolous NS, Bhatt N, Bhakta N, Neufeld EJ, Davidoff AM, Reiss UM

المصدر: Journal of Blood Medicine, Vol Volume 13, Pp 559-580 (2022)

مصطلحات موضوعية: global health, health equity, cost-effectiveness, adeno-associated virus vector, factor viii, factor ix, Diseases of the blood and blood-forming organs, RC633-647.5

وصف الملف: electronic resource

Relation: https://www.dovepress.com/gene-therapy-and-hemophilia-where-do-we-go-from-here-peer-reviewed-fulltext-article-JBM; https://doaj.org/toc/1179-2736

URL الوصول: https://doaj.org/article/5a22e7b6b1ac4cdcacb1bfec1a4a8bea

المؤلفون: Srinivasan S; Department of Pediatric Oncology, Tata Memorial Hospital and ACTREC, Tata Memorial Centre, Homi Bhabha National Institute, Mumbai, India., Bolous NS; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Batra A; Department of Transfusion Medicine, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India., Bharti S; Department of Microbiology, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India., Singh N; Department of Hematopathology, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India., Shaikh T; Department of Pediatric Oncology, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India., Yadav A; Department of Cytogenetics, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India., Kanwar V; Department of Pediatric Oncology, Homi Bhabha Cancer Hospital and Mahamana Pandit Madan Mohan Malaviya Cancer Centre, Tata Memorial Centre, Homi Bhabha National Institute, Varanasi, Uttar Pradesh, India.

المصدر: Pediatric blood & cancer [Pediatr Blood Cancer] 2024 Aug 10, pp. e31242. Date of Electronic Publication: 2024 Aug 10.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: John Wiley Country of Publication: United States NLM ID: 101186624 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1545-5017 (Electronic) Linking ISSN: 15455009 NLM ISO Abbreviation: Pediatr Blood Cancer Subsets: MEDLINE

المؤلفون: Bolous NS; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Chokwenda-Makore N; Department of Paediatrics and Child Health, Faculty of Medicine and Health Sciences, University of Zimbabwe, Harare, Zimbabwe., Bonilla M; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Chingo G; Department of Pediatric Oncology, Cancer Disease Hospital, Lusaka, Zambia., Kambugu J; Department of Pediatric Oncology, Uganda Cancer Institute, Kampala, Uganda., Mulindwa JM; Department of Pediatric Oncology, Cancer Disease Hospital, Lusaka, Zambia., Noleb M; Department of Pediatric Oncology, Uganda Cancer Institute, Kampala, Uganda., Chitsike I; Department of Paediatrics and Child Health, Faculty of Medicine and Health Sciences, University of Zimbabwe, Harare, Zimbabwe., Bhakta N; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, Tennessee, USA.

المصدر: Cancer [Cancer] 2024 Apr 01; Vol. 130 (7), pp. 1112-1124. Date of Electronic Publication: 2023 Dec 15.

نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural

بيانات الدورية: Publisher: Wiley Country of Publication: United States NLM ID: 0374236 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1097-0142 (Electronic) Linking ISSN: 0008543X NLM ISO Abbreviation: Cancer Subsets: MEDLINE

مواضيع طبية MeSH: Neoplasms*/therapy, Humans ; Child ; Developing Countries ; Vulnerable Populations ; Cost-Benefit Analysis ; Health Care Costs

المؤلفون: Bolous NS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN 38105, USA., Mercredi P; Independant Researcher., Bonilla M; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN 38105, USA., Friedrich P; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN 38105, USA., Bhakta N; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN 38105, USA., Metzger ML; Médecins Sans Frontières, Geneva 1202, Switzerland., Gassant PY; Nos Petit Frères et Sœurs-St Damien Hospital, Port-au-Prince 6124, Haiti.

المصدر: Ecancermedicalscience [Ecancermedicalscience] 2024 Feb 28; Vol. 18, pp. 1675. Date of Electronic Publication: 2024 Feb 28 (Print Publication: 2024).

نوع المنشور: Journal Article

بيانات الدورية: Publisher: ecancer Country of Publication: England NLM ID: 101392236 Publication Model: eCollection Cited Medium: Print ISSN: 1754-6605 (Print) Linking ISSN: 17546605 NLM ISO Abbreviation: Ecancermedicalscience Subsets: PubMed not MEDLINE

المؤلفون: Ritter J; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: julie.ritter@stjude.org., Allen S; University of South Carolina, Columbia, SC, USA., Cohen PD; Johns Hopkins Hospital, Baltimore, MD, USA., Fajardo AF; Department of Pediatrics, McMaster University, Hamilton, ON, Canada., Marx K; Prometheus Federal Services, Washington, DC, USA., Loggetto P; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Auste C; Cancer Warriors Foundation, Manila, Philippines., Lewis H; CHOC Childhood Cancer Foundation South Africa, Rivonia, South Africa., de Sá Rodrigues KE; Pediatric Department, Barretos Cancer Hospital, São Paulo, Brazil., Hussain S; Komodo Health, San Francisco, CA, USA., Omotola A; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Bolous NS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Thirumurthy H; Department of Medical Ethics and Health Policy, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Essue BM; Institute of Health Policy, Management and Evaluation, University of Toronto, ON, Canada., Steliarova-Foucher E; Cancer Surveillance Branch, International Agency for Research on Cancer, Lyon, France., Huang IC; Department of Epidemiology and Cancer Control, St Jude Children's Research Hospital, Memphis, TN, USA., Meheus F; Cancer Surveillance Branch, International Agency for Research on Cancer, Lyon, France., Bhakta N; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA; Department of Epidemiology and Cancer Control, St Jude Children's Research Hospital, Memphis, TN, USA.

المصدر: The Lancet. Oncology [Lancet Oncol] 2023 Sep; Vol. 24 (9), pp. e364-e375.

نوع المنشور: Systematic Review; Journal Article; Review

بيانات الدورية: Publisher: Lancet Pub. Group Country of Publication: England NLM ID: 100957246 Publication Model: Print Cited Medium: Internet ISSN: 1474-5488 (Electronic) Linking ISSN: 14702045 NLM ISO Abbreviation: Lancet Oncol Subsets: MEDLINE

مواضيع طبية MeSH: Financial Stress* , Neoplasms*/epidemiology, Humans ; Adolescent ; Child ; Income

المؤلفون: Ehrlich BS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA; Warren Alpert Medical School, Brown University, Providence, RI, USA., McNeil MJ; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Pham LTD; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Chen Y; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Rivera J; Department of Pediatric Emergency Medicine, Hospital Infantil Teletón de Oncología, Querétaro, México., Acuna C; Department of Pediatric Intensive Care, Dr Luis Calvo Mackenna Children's Hospital, Santiago, Chile., Sniderman L; Northern Alberta Children's Cancer Program, Stollery Children's Hospital, Edmonton, AB, Canada., Sakaan FM; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Aceituno AM; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA; Pediatric Intensive Care Unit, Unidad Nacional de Oncología Pediátrica, Guatemala City, Guatemala., Villegas CA; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Force LM; Department of Health Metrics Sciences and Department of Pediatrics, Division of Pediatric Hematology/Oncology, University of Washington, Seattle, WA, USA., Bolous NS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Wiphatphumiprates PP; Rhodes College, Memphis, TN, USA., Slone JS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Carrillo AK; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Gillipelli SR; Baylor College of Medicine, Houston, TX, USA., Duffy C; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Arias AV; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Devidas M; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Rodriguez-Galindo C; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Mukkada S; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA., Agulnik A; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: asya.agulnik@stjude.org.

المصدر: The Lancet. Oncology [Lancet Oncol] 2023 Sep; Vol. 24 (9), pp. 967-977. Date of Electronic Publication: 2023 Jul 27.

نوع المنشور: Meta-Analysis; Systematic Review; Journal Article; Research Support, N.I.H., Extramural

بيانات الدورية: Publisher: Lancet Pub. Group Country of Publication: England NLM ID: 100957246 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1474-5488 (Electronic) Linking ISSN: 14702045 NLM ISO Abbreviation: Lancet Oncol Subsets: MEDLINE

مواضيع طبية MeSH: Developing Countries* , Neoplasms*/therapy, Humans ; Child ; Income ; Poverty

المؤلفون: Habashy C; Division of Pediatric Hematology-Oncology, University of North Carolina, Chapel Hill, NC, USA., Yemeke TT; Eshelman School of Pharmacy, University of North Carolina, Chapel Hill, NC, USA., Bolous NS; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, TN, USA., Chen Y; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, TN, USA., Ozawa S; Eshelman School of Pharmacy, University of North Carolina, Chapel Hill, NC, USA., Bhakta N; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, TN, USA., Alexander TB; Division of Pediatric Hematology-Oncology, University of North Carolina, Chapel Hill, NC, USA.

المصدر: EClinicalMedicine [EClinicalMedicine] 2023 May 18; Vol. 60, pp. 102005. Date of Electronic Publication: 2023 May 18 (Print Publication: 2023).

نوع المنشور: Journal Article

بيانات الدورية: Publisher: The Lancet Country of Publication: England NLM ID: 101733727 Publication Model: eCollection Cited Medium: Internet ISSN: 2589-5370 (Electronic) Linking ISSN: 25895370 NLM ISO Abbreviation: EClinicalMedicine Subsets: PubMed not MEDLINE

المؤلفون: Bolous NS; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, Tennessee, USA., Graetz DE; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, Tennessee, USA., Ashrafian H; Institute of Global Health Innovation, Imperial College London, London, UK.; Department of Surgery and Cancer, Imperial College London, London, UK., Barlow J; Business School, Imperial College London, London, UK., Bhakta N; Department of Global Pediatric Medicine, St Jude Children's Research Hospital, Memphis, Tennessee, USA., Sounderajah V; Institute of Global Health Innovation, Imperial College London, London, UK.; Department of Surgery and Cancer, Imperial College London, London, UK., Dowdeswell B; Management Center Innsbruck, Internationale Hochschule GmbH, Innsbruck, Austria.

المصدر: Journal of health organization and management [J Health Organ Manag] 2022 Dec 19; Vol. ahead-of-print (ahead-of-print).

نوع المنشور: Case Reports

بيانات الدورية: Publisher: Emerald Country of Publication: England NLM ID: 101179473 Publication Model: Print Cited Medium: Internet ISSN: 1758-7247 (Electronic) Linking ISSN: 14777266 NLM ISO Abbreviation: J Health Organ Manag

مواضيع طبية MeSH: State Medicine* , Delivery of Health Care*, Humans ; Leadership ; Health Facilities ; United Kingdom

المؤلفون: Soliman R; Department of Continuing Education, University of Oxford, UK.; Health Economics and Value Unit, Children's Cancer Hospital Egypt - 57357, Egypt., Oke J; Centre for Evidence-Based Medicine (CEBM), Nuffield Department of Primary Care Health Sciences, University of Oxford, Oxford, UK., Sidhom I; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Bhakta N; Global Paediatric Medicine Department, St. Jude Children's Research Hospital, USA., Bolous NS; Global Paediatric Medicine Department, St. Jude Children's Research Hospital, USA., Tarek N; Health Economics and Value Unit, Children's Cancer Hospital Egypt - 57357, Egypt., Ahmed S; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Abdelrahman H; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Moussa E; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Clinical Oncology Department, Menoufia University, Egypt., Zamzam M; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Fawzy M; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Zekri W; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Hafez H; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Sedky M; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatrics Department, National Research Centre, Cairo, Egypt., Hammad M; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Elzomor H; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Ahmed S; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Awad M; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, Nasser Institute for Research and Treatment, Cairo, Egypt., Abdelhameed S; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Mohsen E; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Clinical Oncology Department, Beni-suef University, Egypt., Shalaby L; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Eweida W; Chief Operating Office, Children's Cancer Hospital Egypt - 57357, Egypt., Abouelnaga S; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt.; Chief Executive Office, Children's Cancer Hospital Egypt - 57357, Egypt., Elhaddad A; Paediatric Oncology Department, Children's Cancer Hospital Egypt - 57357, Egypt.; Paediatric Oncology Department, National Cancer Institute, Cairo University, Egypt., Heneghan C; Centre for Evidence-Based Medicine (CEBM), Nuffield Department of Primary Care Health Sciences, University of Oxford, Oxford, UK.

المصدر: EClinicalMedicine [EClinicalMedicine] 2022 Nov 04; Vol. 55, pp. 101729. Date of Electronic Publication: 2022 Nov 04 (Print Publication: 2023).

نوع المنشور: Journal Article

بيانات الدورية: Publisher: The Lancet Country of Publication: England NLM ID: 101733727 Publication Model: eCollection Cited Medium: Internet ISSN: 2589-5370 (Electronic) Linking ISSN: 25895370 NLM ISO Abbreviation: EClinicalMedicine Subsets: PubMed not MEDLINE

المؤلفون: Soliman R; Department for Continuing Education, University of Oxford, Oxford, UK.; Health Economics and Value Unit, Children's Cancer Hospital, Cairo, Egypt., Heneghan C; Centre for Evidence Based Medicine, Nuffield Department of Primary Care Health Sciences, University of Oxford, Oxford, UK., Bolous NS; Department of Global Pediatric Medicine, St. Jude Children's Research Hospital, Memphis, TN, USA., Sidhom I; Department of Pediatric Oncology, Children's Cancer Hospital, Cairo, Egypt.; Department of Pediatric Oncology, National Cancer Institute, Cairo University, Cairo, Egypt., Ahmed S; Department of Pediatric Oncology, Children's Cancer Hospital, Cairo, Egypt.; Department of Pediatric Oncology, National Cancer Institute, Cairo University, Cairo, Egypt., Roberts N; Oxford Bodleian Health Care Libraries, University of Oxford, Oxford, UK., Oke J; Centre for Evidence Based Medicine, Nuffield Department of Primary Care Health Sciences, University of Oxford, Oxford, UK., Elhaddad A; Department of Pediatric Oncology, Children's Cancer Hospital, Cairo, Egypt.; Department of Pediatric Oncology, National Cancer Institute, Cairo University, Cairo, Egypt.

المصدر: Expert review of hematology [Expert Rev Hematol] 2022 Apr; Vol. 15 (4), pp. 345-357. Date of Electronic Publication: 2022 May 04.

نوع المنشور: Journal Article; Systematic Review; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: Taylor & Francis Country of Publication: England NLM ID: 101485942 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1747-4094 (Electronic) Linking ISSN: 17474094 NLM ISO Abbreviation: Expert Rev Hematol Subsets: MEDLINE

مواضيع طبية MeSH: Leukemia, Myeloid, Acute*/therapy , Precursor Cell Lymphoblastic Leukemia-Lymphoma*/drug therapy, Child ; Cost-Benefit Analysis ; Health Care Costs ; Humans ; Immunotherapy, Adoptive ; Recurrence ; Young Adult