-
1دورية أكاديمية
المؤلفون: Nancy Chen, David E. Ehmann, Robert Crooker, Katayoun Derakhchan, Xiaodong Fang, Brian Felice, Elizabeth J. Galbreath, Charles Glaus, Hongbo Gu, Yan Huang, Christine Li, Xing Li, Nan Liu, Kathleen Palmieri, Damir Simic, Joseph Sypek, Susan Thompson, Christopher T. Winkelmann, Vivian W. Choi
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 29, Iss , Pp 286-302 (2023)
مصطلحات موضوعية: gene therapy, AAV, MPS II, cross-correction, non-human primates, iduronate-2-sulfatase, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
-
2
المؤلفون: Laura Ortiz, Brian Felice, Stephen Fox, Michael Marchiori, Divyani Patel, Jason Adam Wasserman
المصدر: Western Journal of Emergency Medicine. 24
مصطلحات موضوعية: Emergency Medicine, General Medicine
-
3
المؤلفون: Hana Fikree, Teresa Leah Wright, James Blackwell, Brian Felice, Jeffrey W. Card, Lois A. Haighton
المصدر: Regulatory Toxicology and Pharmacology. 73:595-606
مصطلحات موضوعية: Biological Products, Drug Industry, biology, Chemistry, Microgram, Endogeny, General Medicine, Pharmacology, Toxicology, Multi product, Risk Assessment, Antibody fragments, law.invention, law, Manufacturing Industry, Toxicity, Recombinant DNA, biology.protein, Humans, Potency, Antibody, Drug Contamination
-
4
المؤلفون: Pericles Calias, Teresa Leah Wright, Michael W. Heartlein, Mark T. Butt, Jing Pan, Robert B. Boyd, Brian Felice, Richard Pfeifer, Juan Ruiz
المصدر: Toxicologic Pathology. 39:879-892
مصطلحات موضوعية: Male, No-observed-adverse-effect level, Idursulfase, Central nervous system, Iduronate Sulfatase, Toxicology, Pathology and Forensic Medicine, Meninges, Lysosomal storage disease, Animals, Medicine, Enzyme Replacement Therapy, Subcutaneous port, Molecular Biology, Injections, Spinal, No-Observed-Adverse-Effect Level, Dose-Response Relationship, Drug, business.industry, Hunter syndrome, Infusion Pumps, Implantable, Cell Biology, Enzyme replacement therapy, medicine.disease, Spinal cord, Immunohistochemistry, Macaca fascicularis, medicine.anatomical_structure, Case-Control Studies, Anesthesia, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::45aa5c8bf1be47df9991526d2d347954
https://doi.org/10.1177/0192623311409595 -
5
المؤلفون: Mark T. Butt, Robert B. Boyd, Pericles Calias, Michael W. Heartlein, Brian Felice, Juan Ruiz, Richard Pfeifer
المصدر: Drug delivery and translational research. 2(3)
مصطلحات موضوعية: Pathology, medicine.medical_specialty, business.industry, Mucopolysaccharidosis, medicine.medical_treatment, Central nervous system, Meninges, Pharmaceutical Science, medicine.disease, Spinal cord, Cerebrospinal fluid, medicine.anatomical_structure, Anesthesia, Lysosomal storage disease, Medicine, business, Perineurium, Saline
-
6
المؤلفون: Jing Pan, Brian Felice, Nancy Savioli, Michael W. Heartlein, Richard Pfeifer, Jason Lotterhand, Pericles Calias, Mary Alessandrini, Nan Liu, Jan Powell, Teresa Leah Wright, Yan Huang
المصدر: Molecular Genetics and Metabolism. 102:S10
مصطلحات موضوعية: business.industry, Idursulfase, Endocrinology, Diabetes and Metabolism, medicine.medical_treatment, Colocalization, Iduronate-2-sulfatase, Pharmacology, Biochemistry, Anterograde axonal transport, Staining, Endocrinology, Vacuolization, Genetics, Medicine, Immunohistochemistry, business, Molecular Biology, Saline, medicine.drug