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1دورية أكاديمية
المؤلفون: Bulcaen, Mattijs, Kortleven, Phéline, Liu, Ronald B., Maule, Giulia, Dreano, Elise, Kelly, Mairead, Ensinck, Marjolein M., Thierie, Sam, Smits, Maxime, Ciciani, Matteo, Hatton, Aurelie, Chevalier, Benoit, Ramalho, Anabela S., Casadevall i Solvas, Xavier, Debyser, Zeger, Vermeulen, François, Gijsbers, Rik, Sermet-Gaudelus, Isabelle, Cereseto, Anna, Carlon, Marianne S.
المصدر: In Cell Reports Medicine 21 May 2024 5(5)
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2دورية أكاديمية
المؤلفون: Tiroille, Victor, Krug, Adrien, Bokobza, Emma, Kahi, Michel, Bulcaen, Mattijs, Ensinck, Marjolein M., Geurts, Maarten H., Hendriks, Delilah, Vermeulen, François, Larbret, Frédéric, Gutierrez-Guerrero, Alejandra, Chen, Yu, Van Zundert, Indra, Rocha, Susana, Rios, Anne C., Medaer, Louise, Gijsbers, Rik, Mangeot, Philippe E., Clevers, Hans, Carlon, Marianne S., Bost, Frédéric, Verhoeyen, Els
المصدر: In Molecular Therapy - Nucleic Acids June 2023
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3دورية أكاديمية
المؤلفون: Qu, Jia-Huan, Ordutowski, Henry, Van Tricht, Charlotte, Verbruggen, Ruben, Barcenas Gallardo, Alicia, Bulcaen, Mattijs, Ciwinska, Marta, Gutierrez Cisneros, Carolina, Devriese, Christophe, Guluzade, Sona, Janssens, Xander, Kornblum, Sophie, Lu, Yuansheng, Marolt, Nika, Nanjappan, Chezhiyan, Rutten, Eline, Vanhauwaert, Eline, Geukens, Nick, Thomas, Debby, Dal Dosso, Francesco, Safdar, Saba, Spasic, Dragana, Lammertyn, Jeroen
المصدر: In Biosensors and Bioelectronics 15 June 2022 206
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4دورية أكاديمية
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5دورية أكاديمية
المؤلفون: Bulcaen, Mattijs, Carlon, Marianne S.
المصدر: Science; 6/14/2024, Vol. 384 Issue 6701, p1175-1176, 2p, 1 Diagram
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6دورية
المؤلفون: Bulcaen, Mattijs, Kortleven, Phéline, Liu, Ronald B., Maule, Giulia, Dreano, Elise, Kelly, Mairead, Ensinck, Marjolein M., Thierie, Sam, Smits, Maxime, Ciciani, Matteo, Hatton, Aurelie, Chevalier, Benoit, Ramalho, Anabela S., Casadevall i Solvas, Xavier, Debyser, Zeger, Vermeulen, François, Gijsbers, Rik, Sermet-Gaudelus, Isabelle, Cereseto, Anna, Carlon, Marianne S.
المصدر: Cell Reports Medicine; May 2024, Vol. 5 Issue: 5
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7دورية أكاديمية
المؤلفون: Maule G; Department CIBIO, University of Trento, Trento, Italy; Institute of Biophysics, National Research Council, Trento, Italy., Ensinck M; Molecular Virology and Gene Therapy, Department of Pharmaceutical and Pharmacological Sciences, KU Leuven, Flanders, Belgium., Bulcaen M; Molecular Virology and Gene Therapy, Department of Pharmaceutical and Pharmacological Sciences, KU Leuven, Flanders, Belgium., Carlon MS; Molecular Virology and Gene Therapy, Department of Pharmaceutical and Pharmacological Sciences, KU Leuven, Flanders, Belgium. Electronic address: marianne.carlon@kuleuven.be.
المصدر: Progress in molecular biology and translational science [Prog Mol Biol Transl Sci] 2021; Vol. 182, pp. 185-224. Date of Electronic Publication: 2021 Jan 28.
نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't; Review
بيانات الدورية: Publisher: Elsevier/AP Country of Publication: Netherlands NLM ID: 101498165 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1878-0814 (Electronic) Linking ISSN: 18771173 NLM ISO Abbreviation: Prog Mol Biol Transl Sci Subsets: MEDLINE
مواضيع طبية MeSH: Cystic Fibrosis*/genetics , Cystic Fibrosis*/therapy, Cystic Fibrosis Transmembrane Conductance Regulator/genetics ; Gene Editing ; Humans ; Mutant Proteins ; Mutation/genetics