-
1دورية أكاديمية
المؤلفون: Eike A Strathmann, Miriam Peters, Seyyedmohsen Hosseinibarkooie, Frank W Rigo, C Frank Bennett, Phillip G Zaworski, Karen S Chen, Michael Nothnagel, Brunhilde Wirth
المصدر: PLoS ONE, Vol 13, Iss 9, p e0203398 (2018)
وصف الملف: electronic resource
-
2دورية أكاديمية
المؤلفون: Sydney R Coffey, Robert M Bragg, Shawn Minnig, Seth A Ament, Jeffrey P Cantle, Anne Glickenhaus, Daniel Shelnut, José M Carrillo, Dominic D Shuttleworth, Julie-Anne Rodier, Kimihiro Noguchi, C Frank Bennett, Nathan D Price, Holly B Kordasiewicz, Jeffrey B Carroll
المصدر: PLoS ONE, Vol 12, Iss 4, p e0175968 (2017)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1932-6203
-
3دورية أكاديمية
المؤلفون: Hui-Min Cheng, Yijuang Chern, I-Hui Chen, Chia-Rung Liu, Sih-Huei Li, Seung J Chun, Frank Rigo, C Frank Bennett, Ning Deng, Yanan Feng, Chyuan-Sheng Lin, Yu-Ting Yan, Stanley N Cohen, Tzu-Hao Cheng
المصدر: PLoS Genetics, Vol 11, Iss 3, p e1005043 (2015)
وصف الملف: electronic resource
-
4دورية أكاديمية
المؤلفون: Niels H Skotte, Amber L Southwell, Michael E Østergaard, Jeffrey B Carroll, Simon C Warby, Crystal N Doty, Eugenia Petoukhov, Kuljeet Vaid, Holly Kordasiewicz, Andrew T Watt, Susan M Freier, Gene Hung, Punit P Seth, C Frank Bennett, Eric E Swayze, Michael R Hayden
المصدر: PLoS ONE, Vol 9, Iss 9, p e107434 (2014)
وصف الملف: electronic resource
-
5دورية أكاديمية
المؤلفون: Yimin Hua, Timothy A Vickers, Brenda F Baker, C Frank Bennett, Adrian R Krainer
المصدر: PLoS Biology, Vol 5, Iss 4, p e73 (2007)
مصطلحات موضوعية: Biology (General), QH301-705.5
وصف الملف: electronic resource
-
6دورية أكاديمية
المؤلفون: Moira A. McMahon, Meghdad Rahdar, Swagatam Mukhopadhyay, Huynh-Hoa Bui, Christopher Hart, Sagar Damle, Margo Courtney, Michael W. Baughn, Don W. Cleveland, C. Frank Bennett
المصدر: Molecular Therapy: Nucleic Acids, Vol 32, Iss , Pp 289-301 (2023)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, antisense oligonucleotide, ASO, CRISPR-Cas, gene activation, GOLGA8, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
-
7دورية أكاديمية
المؤلفون: Anixa Muiños-Bühl, Roman Rombo, Karen K. Ling, Eleonora Zilio, Frank Rigo, C. Frank Bennett, Brunhilde Wirth
المصدر: International Journal of Molecular Sciences, Vol 24, Iss 4, p 4198 (2023)
مصطلحات موضوعية: antisense oligonucleotide, genetic modifier, hiPSCs, neuromuscular disorder, NCALD, SMA, Biology (General), QH301-705.5, Chemistry, QD1-999
وصف الملف: electronic resource
-
8
المؤلفون: Catherine J. Mummery, Anne Börjesson-Hanson, Daniel J. Blackburn, Everard G. B. Vijverberg, Peter Paul De Deyn, Simon Ducharme, Michael Jonsson, Anja Schneider, Juha O. Rinne, Albert C. Ludolph, Ralf Bodenschatz, Holly Kordasiewicz, Eric E. Swayze, Bethany Fitzsimmons, Laurence Mignon, Katrina M. Moore, Chris Yun, Tiffany Baumann, Dan Li, Daniel A. Norris, Rebecca Crean, Danielle L. Graham, Ellen Huang, Elena Ratti, C. Frank Bennett, Candice Junge, Roger M. Lane
المساهمون: Neurology, Amsterdam Neuroscience - Neurodegeneration, Molecular Neuroscience and Ageing Research (MOLAR)
المصدر: Nature medicine 29(6), 1437-1447 (2023). doi:10.1038/s41591-023-02326-3
Mummery, C J, Börjesson-Hanson, A, Blackburn, D J, Vijverberg, E G B, de Deyn, P P, Ducharme, S, Jonsson, M, Schneider, A, Rinne, J O, Ludolph, A C, Bodenschatz, R, Kordasiewicz, H, Swayze, E E, Fitzsimmons, B, Mignon, L, Moore, K M, Yun, C, Baumann, T, Li, D, Norris, D A, Crean, R, Graham, D L, Huang, E, Ratti, E, Bennett, C F, Junge, C & Lane, R M 2023, ' Tau-targeting antisense oligonucleotide MAPTRx in mild Alzheimer’s disease : a phase 1b, randomized, placebo-controlled trial ', Nature Medicine, vol. 29, no. 6, pp. 1437-1447 . https://doi.org/10.1038/s41591-023-02326-3
Nature Medicine. Nature Publishing Group
Nature Medicine, 29, 1437-1447. Nature Publishing Groupمصطلحات موضوعية: General Medicine, ddc:610, General Biochemistry, Genetics and Molecular Biology
وصف الملف: application/pdf
-
9
المؤلفون: Michael W. Baughn, Ze’ev Melamed, Jone López-Erauskin, Melinda S. Beccari, Karen Ling, Aamir Zuberi, Maximilliano Presa, Elena Gonzalo-Gil, Roy Maimon, Sonia Vazquez-Sanchez, Som Chaturvedi, Mariana Bravo-Hernández, Vanessa Taupin, Stephen Moore, Jonathan W. Artates, Eitan Acks, I. Sandra Ndayambaje, Ana R. Agra de Almeida Quadros, Paayman Jafar-nejad, Frank Rigo, C. Frank Bennett, Cathleen Lutz, Clotilde Lagier-Tourenne, Don W. Cleveland
المصدر: Science. 379:1140-1149
مصطلحات موضوعية: Multidisciplinary
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::710b73726aca4d21e6200a041157f60b
https://doi.org/10.1126/science.abq5622 -
10
المؤلفون: Charles A Thornton, Richard Thomas Moxley, Katy Eichinger, Chad Heatwole, Laurence Mignon, W David Arnold, Tetsuo Ashizawa, John W Day, Gersham Dent, Matthew K Tanner, Tina Duong, Ericka P Greene, Laura Herbelin, Nicholas E Johnson, Wendy King, John T Kissel, Doris G Leung, Donovan J Lott, Daniel A Norris, Evan M Pucillo, Wendy Schell, Jeffrey M Statland, Nikia Stinson, Sub H Subramony, Shuting Xia, Kathie M Bishop, C Frank Bennett
المصدر: The Lancet Neurology. 22:218-228
مصطلحات موضوعية: Neurology (clinical)