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1دورية أكاديمية
المؤلفون: Benson, MonikaAff1, Aff2, Albanese, AlbertoAff2, Aff3, Bhatia, Kailash P., Cavillon, Pascale, Cuffe, Lorraine, König, Kathrin, Reinhard, CarolaAff2, Aff8, Graessner, HolmAff2, Aff8, IDs13023022022704_cor8
المصدر: Orphanet Journal of Rare Diseases. 17(1)
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2دورية أكاديمية
المؤلفون: Gorbenko, Oleks, Cavillon, Pascale, Giles, Rachel H., Kolarova, Teodora, Marks, Muriël, Cardone, Antonella, Bagga, SandeepAff7, IDs40900022003340_cor7, Nolan, Claire
المصدر: Research Involvement and Engagement. 8(1)
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