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المؤلفون: Burdo TH; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA. burdot@temple.edu., Chen C; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Kaminski R; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Sariyer IK; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Mancuso P; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Donadoni M; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Smith MD; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Sariyer R; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Caocci M; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Liao S; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Liu H; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Huo W; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Zhao H; Center for Biostatistics and Epidemiology, Department of Biomedical Education and Data Science, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Misamore J; BioQual, Inc., Rockville, MD, USA., Lewis MG; BioQual, Inc., Rockville, MD, USA., Simonyan V; Embleema, Metuchen, NJ, USA., Thompson EE; Embleema, Metuchen, NJ, USA., Xu EY; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Cradick TJ; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Gordon J; Excision BioTherapeutics, Inc., San Francisco, CA, USA. jgordon@excisionbio.com., Khalili K; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA. kkhalili@temple.edu.

المصدر: Gene therapy [Gene Ther] 2024 Jul; Vol. 31 (7-8), pp. 434-435.

نوع المنشور: Published Erratum

بيانات الدورية: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: PubMed not MEDLINE; MEDLINE

المؤلفون: Burdo TH; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA. burdot@temple.edu., Chen C; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Kaminski R; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Sariyer IK; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Mancuso P; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Donadoni M; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Smith MD; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Sariyer R; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Caocci M; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Liao S; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Liu H; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Huo W; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Zhao H; Center for Biostatistics and Epidemiology, Department of Biomedical Education and Data Science, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA., Misamore J; BioQual, Inc., Rockville, MD, USA., Lewis MG; BioQual, Inc., Rockville, MD, USA., Simonyan V; Embleema, Metuchen, NJ, USA., Thompson EE; Embleema, Metuchen, NJ, USA., Xu EY; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Cradick TJ; Excision BioTherapeutics, Inc., San Francisco, CA, USA., Gordon J; Excision BioTherapeutics, Inc., San Francisco, CA, USA. jgordon@excisionbio.com., Khalili K; Department of Microbiology, Immunology, and Inflammation, Center for NeuroVirology and Gene Editing, Lewis Katz School of Medicine, Temple University, Philadelphia, PA, 19140, USA. kkhalili@temple.edu.

المصدر: Gene therapy [Gene Ther] 2024 May; Vol. 31 (5-6), pp. 224-233. Date of Electronic Publication: 2023 Aug 17.

نوع المنشور: Journal Article; Research Support, N.I.H., Extramural

بيانات الدورية: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE

مواضيع طبية MeSH: Simian Immunodeficiency Virus*/genetics , Simian Immunodeficiency Virus*/drug effects , Macaca mulatta* , Gene Editing*/methods , CRISPR-Cas Systems* , Simian Acquired Immunodeficiency Syndrome*/virology , Simian Acquired Immunodeficiency Syndrome*/therapy, Animals ; Tissue Distribution ; Genetic Vectors/genetics ; Genetic Vectors/administration & dosage ; Genetic Vectors/pharmacokinetics ; Genetic Therapy/methods ; Dependovirus/genetics

المؤلفون: Liu H; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA., Chen C; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA., Liao S; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA., Sohaii DK; Center for Cancer and Immunology Research, Children's National Health System, The George Washington University, 7144 13th Place NW, Washington, DC 20012, USA., Cruz CRY; Center for Cancer and Immunology Research, Children's National Health System, The George Washington University, 7144 13th Place NW, Washington, DC 20012, USA., Burdo TH; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA., Cradick TJ; Excision Biotherapeutics, Inc., 499 Jackson Street, San Francisco, CA 94111, USA., Mehta A; Department of Cell and Molecular Pharmacology, Medical University of South Carolina, Basic Science Building, Room 310, 173 Ashley Avenue, Charleston, SC 29425, USA., Barrero C; Department of Pharmaceutical Sciences, School of Pharmacy, Temple University, 3307 N. Broad Street, Philadelphia, PA 19140, USA., Florez M; Department of Pharmaceutical Sciences, School of Pharmacy, Temple University, 3307 N. Broad Street, Philadelphia, PA 19140, USA., Gordon J; Excision Biotherapeutics, Inc., 499 Jackson Street, San Francisco, CA 94111, USA., Grauzam S; Department of Cell and Molecular Pharmacology, Medical University of South Carolina, Basic Science Building, Room 310, 173 Ashley Avenue, Charleston, SC 29425, USA., Dressman J; Department of Cell and Molecular Pharmacology, Medical University of South Carolina, Basic Science Building, Room 310, 173 Ashley Avenue, Charleston, SC 29425, USA., Amini S; Department of Biology, College of Science and Technology, Temple University, 1900 North 12th Street, Philadelphia, PA 19122, USA., Bollard CM; Center for Cancer and Immunology Research, Children's National Health System, The George Washington University, 7144 13th Place NW, Washington, DC 20012, USA., Kaminski R; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA., Khalili K; Center for Neurovirology and Gene Editing, Department of Microbiology, Immunology, and Inflammation, Lewis Katz School of Medicine at Temple University, 3500 N. Broad Street, 7th Floor, Philadelphia, PA 19140, USA.

المصدر: Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2023 May 19; Vol. 32, pp. 1010-1025. Date of Electronic Publication: 2023 May 19 (Print Publication: 2023).

نوع المنشور: Journal Article

بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE

المؤلفون: Schneller JL; National Human Genome Research Institute, NIH, Bethesda, 20892 MD, USA., Lee CM; Department of Bioengineering, Rice University, Houston, TX 77005, USA., Venturoni LE; National Human Genome Research Institute, NIH, Bethesda, 20892 MD, USA., Chandler RJ; National Human Genome Research Institute, NIH, Bethesda, 20892 MD, USA., Li A; Department of Bioengineering, Rice University, Houston, TX 77005, USA., Myung S; National Human Genome Research Institute, NIH, Bethesda, 20892 MD, USA., Cradick TJ; Georgia Institute of Technology, Atlanta, GA 30332, USA., Hurley AE; Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, TX 77030, USA., Lagor WR; Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, TX 77030, USA., Bao G; Department of Bioengineering, Rice University, Houston, TX 77005, USA., Venditti CP; National Human Genome Research Institute, NIH, Bethesda, 20892 MD, USA.

المصدر: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2021 Nov 11; Vol. 23, pp. 619-632. Date of Electronic Publication: 2021 Nov 11 (Print Publication: 2021).

نوع المنشور: Journal Article

بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE

المؤلفون: Cereseto A; Laboratory of Molecular Virology, CIBIO, University of Trento, Trento, Italy., Cradick TJ; Excision Therapeutics, Cambridge, Massachusetts, USA., Davies K; Executive Editor, The CRISPR Journal, New Rochelle, New York, USA.

المصدر: The CRISPR journal [CRISPR J] 2021 Apr; Vol. 4 (2), pp. 166-168.

نوع المنشور: Journal Article; Comment

بيانات الدورية: Publisher: Mary Ann Liebert, Inc Country of Publication: United States NLM ID: 101738191 Publication Model: Print Cited Medium: Internet ISSN: 2573-1602 (Electronic) Linking ISSN: 25731599 NLM ISO Abbreviation: CRISPR J Subsets: MEDLINE

مواضيع طبية MeSH: Anemia, Sickle Cell*/epidemiology , Anemia, Sickle Cell*/therapy , Gene Editing*, CRISPR-Cas Systems ; Humans

المؤلفون: Chaudhari HG; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Penterman J; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Whitton HJ; TScan Therapeutics, Waltham, Massachusetts, USA; and San Francisco, California 94102, USA., Spencer SJ; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Flanagan N; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Lei Zhang MC; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Huang E; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Khedkar AS; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Toomey JM; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Shearer CA; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Needham AW; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Ho TW; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Kulman JD; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA., Cradick TJ; Excision BioTherapeutics, San Francisco, California 94102, USA., Kernytsky A; CRISPR Therapeutics, Inc., Cambridge, Massachusetts, USA; San Francisco, California 94102, USA.

المصدر: The CRISPR journal [CRISPR J] 2020 Dec; Vol. 3 (6), pp. 440-453.

نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: Mary Ann Liebert, Inc Country of Publication: United States NLM ID: 101738191 Publication Model: Print Cited Medium: Internet ISSN: 2573-1602 (Electronic) Linking ISSN: 25731599 NLM ISO Abbreviation: CRISPR J Subsets: MEDLINE

مواضيع طبية MeSH: Gene Editing/*ethics , Gene Editing/*methods , Gene Editing/*trends, Artifacts ; CRISPR-Cas Systems/genetics ; Clustered Regularly Interspaced Short Palindromic Repeats ; Genome, Human/genetics ; Genomic Instability/genetics ; HEK293 Cells ; High-Throughput Nucleotide Sequencing/methods ; Humans ; RNA, Guide, CRISPR-Cas Systems/genetics ; Streptococcus pyogenes/genetics ; Streptococcus pyogenes/pathogenicity

المؤلفون: Antoniani C; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM Unité Mixte de Recherche (UMR)1163, Paris, France.; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France., Meneghini V; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM Unité Mixte de Recherche (UMR)1163, Paris, France.; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France., Lattanzi A; Genethon, INSERM UMR951, Evry, France., Felix T; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM Unité Mixte de Recherche (UMR)1163, Paris, France.; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France., Romano O; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM Unité Mixte de Recherche (UMR)1163, Paris, France.; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France.; Department of Life Sciences, University of Modena and Reggio Emilia, Modena, Italy., Magrin E; Laboratory of Human Lymphohematopoiesis, INSERM UMR1163, Paris, France.; Biotherapy Department, Necker Children's Hospital, Public Assistance Hospitals of Paris, Paris, France., Weber L; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France.; Laboratory of Human Lymphohematopoiesis, INSERM UMR1163, Paris, France., Pavani G; Genethon, INSERM UMR951, Evry, France., El Hoss S; Sorbonne Paris Cité University, Paris Diderot University, INSERM, Institut National de la Transfusion Sanguine, Unité Biologie Intégrée du Globule Rouge, Laboratoire d'Excellence GR-Ex, Paris, France., Kurita R; RIKEN Tsukuba Branch, Ibaraki, Japan., Nakamura Y; RIKEN Tsukuba Branch, Ibaraki, Japan., Cradick TJ; CRISPR Therapeutics, Cambridge, MA., Lundberg AS; CRISPR Therapeutics, Cambridge, MA., Porteus M; Department of Pediatrics, Stanford University, Stanford, CA; and., Amendola M; Genethon, INSERM UMR951, Evry, France., El Nemer W; Sorbonne Paris Cité University, Paris Diderot University, INSERM, Institut National de la Transfusion Sanguine, Unité Biologie Intégrée du Globule Rouge, Laboratoire d'Excellence GR-Ex, Paris, France., Cavazzana M; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France.; Laboratory of Human Lymphohematopoiesis, INSERM UMR1163, Paris, France.; Biotherapy Department, Necker Children's Hospital, Public Assistance Hospitals of Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Public Assistance Hospitals of Paris, Paris, France., Mavilio F; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France.; Department of Life Sciences, University of Modena and Reggio Emilia, Modena, Italy., Miccio A; Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM Unité Mixte de Recherche (UMR)1163, Paris, France.; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France.; Genethon, INSERM UMR951, Evry, France.

المصدر: Blood [Blood] 2018 Apr 26; Vol. 131 (17), pp. 1960-1973. Date of Electronic Publication: 2018 Mar 08.

نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE

مواضيع طبية MeSH: Anemia, Sickle Cell*/genetics , Anemia, Sickle Cell*/metabolism , Anemia, Sickle Cell*/pathology , Anemia, Sickle Cell*/therapy , CRISPR-Cas Systems* , Fetal Hemoglobin*/biosynthesis , Fetal Hemoglobin*/genetics , Gene Editing* , Genetic Loci*, Hematopoietic Stem Cells/*metabolism , beta-Globins/*genetics, Cell Line ; Hematopoietic Stem Cells/pathology ; Humans ; beta-Globins/metabolism

المؤلفون: Lee CM; Department of Bioengineering, Rice University, Houston, Texas, USA., Cradick TJ; Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, Georgia, USA.; Present Address: CRISPR Therapeutics, Cambridge, Massachusetts, USA., Bao G; Department of Bioengineering, Rice University, Houston, Texas, USA.

المصدر: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2016 Mar; Vol. 24 (3), pp. 645-54. Date of Electronic Publication: 2016 Jan 19.

نوع المنشور: Journal Article; Research Support, N.I.H., Extramural

بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

مواضيع طبية MeSH: CRISPR-Cas Systems* , Clustered Regularly Interspaced Short Palindromic Repeats* , Gene Editing* , Genome*, Neisseria meningitidis/*enzymology , Neisseria meningitidis/*genetics, Base Sequence ; Binding Sites ; Gene Targeting ; Genetic Loci ; Humans ; Nucleotide Motifs ; Position-Specific Scoring Matrices ; Protein Binding ; RNA, Guide, CRISPR-Cas Systems ; Substrate Specificity

المؤلفون: Müller M; Institute for Cell and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.; Center for Chronic Immunodeficiency, Medical Center - University of Freiburg, Freiburg, Germany.; Faculty of Biology, University of Freiburg, Freiburg, Germany., Lee CM; Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, Georgia, USA.; Department of Bioengineering, Rice University, Houston, Texas, USA., Gasiunas G; Institute of Biotechnology, Vilnius University, Vilnius, Lithuania., Davis TH; Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, Georgia, USA.; Department of Bioengineering, Rice University, Houston, Texas, USA., Cradick TJ; Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, Georgia, USA.; Current address: CRISPR Therapeutics, Cambridge, Massachusetts, USA., Siksnys V; Institute of Biotechnology, Vilnius University, Vilnius, Lithuania., Bao G; Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, Georgia, USA.; Department of Bioengineering, Rice University, Houston, Texas, USA., Cathomen T; Institute for Cell and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.; Center for Chronic Immunodeficiency, Medical Center - University of Freiburg, Freiburg, Germany., Mussolino C; Institute for Cell and Gene Therapy, Medical Center - University of Freiburg, Freiburg, Germany.; Center for Chronic Immunodeficiency, Medical Center - University of Freiburg, Freiburg, Germany.

المصدر: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2016 Mar; Vol. 24 (3), pp. 636-44. Date of Electronic Publication: 2015 Dec 14.

نوع المنشور: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE

مواضيع طبية MeSH: CRISPR-Cas Systems* , Gene Editing* , Genome, Human*, Streptococcus thermophilus/*enzymology , Streptococcus thermophilus/*genetics, Base Sequence ; Binding Sites ; Cell Line ; Endonucleases/metabolism ; Enzyme Activation ; Genetic Vectors ; Humans ; Protein Binding ; RNA, Guide, CRISPR-Cas Systems ; Substrate Specificity