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1دورية أكاديمية
المؤلفون: Eleonora Maino, Ori Scott, Samar Z. Rizvi, Wing Suen Chan, Shagana Visuvanathan, Youssif Ben Zablah, Hongbin Li, Ameet S. Sengar, Michael W. Salter, Zhengping Jia, Janet Rossant, Ronald D. Cohn, Bin Gu, Evgueni A. Ivakine
المصدر: Disease Models & Mechanisms, Vol 17, Iss 7 (2024)
مصطلحات موضوعية: mecp2 duplication syndrome, irak1, disease modeling, intellectual disability, interferon, mouse model, Medicine, Pathology, RB1-214
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Sayera Dhaubhadel, Kumkum Ganguly, Ruy M. Ribeiro, Judith D. Cohn, James M. Hyman, Nicolas W. Hengartner, Beauty Kolade, Anna Singley, Tanmoy Bhattacharya, Patrick Finley, Drew Levin, Haedi Thelen, Kelly Cho, Lauren Costa, Yuk-Lam Ho, Amy C. Justice, John Pestian, Daniel Santel, Rafael Zamora-Resendiz, Silvia Crivelli, Suzanne Tamang, Susana Martins, Jodie Trafton, David W. Oslin, Jean C. Beckham, Nathan A. Kimbrel, Million Veteran Program Suicide Exemplar Work Group, Benjamin H. McMahon
المصدر: Scientific Reports, Vol 14, Iss 1, Pp 1-19 (2024)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2045-2322
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3دورية أكاديمية
المؤلفون: Daniel Vargas P. de Almeida, Justine M. Anderson, Daniel C. Danila, Michael J. Morris, Susan F. Slovin, Wassim Abida, Erica D. Cohn, Raymond E. Baser, Howard I. Scher, Karen A. Autio
المصدر: Journal of Immunotherapy and Precision Oncology, Vol 6, Iss 4, Pp 162-169 (2023)
مصطلحات موضوعية: prostate cancer, immune checkpoint inhibitor, patient-reported outcomes, immune-related adverse events, diarrhea, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282, Immunologic diseases. Allergy, RC581-607
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Matthew Rok, Tatianna Wai Ying Wong, Eleonora Maino, Abdalla Ahmed, Grace Yang, Elzbieta Hyatt, Kyle Lindsay, Sina Fatehi, Ryan Marks, Paul Delgado-Olguín, Evgueni A. Ivakine, Ronald D. Cohn
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 246-258 (2023)
مصطلحات موضوعية: CRISPR, Duchenne muscular dystrophy, exon skipping, genome editing, in vivo, cardiomyopathy, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Ori Scott, Shagana Visuvanathan, Emily Reddy, Deeqa Mahamed, Bin Gu, Chaim M. Roifman, Ronald D. Cohn, Cynthia J. Guidos, Evgueni A. Ivakine
المصدر: Frontiers in Immunology, Vol 14 (2023)
مصطلحات موضوعية: STAT1, autoimmunity, chronic activation, T helper, immune dysregulation, Specific pathogen free (SPF), Immunologic diseases. Allergy, RC581-607
وصف الملف: electronic resource
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6دورية أكاديمية
المؤلفون: Ori Scott, Kyle Lindsay, Steven Erwood, Antonio Mollica, Chaim M. Roifman, Ronald D. Cohn, Evgueni A. Ivakine
المصدر: npj Genomic Medicine, Vol 6, Iss 1, Pp 1-15 (2021)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2056-7944
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7دورية أكاديمية
المؤلفون: Stefano C. Previtali, Ronald D. Cohn, Markus A. Ruegg
المصدر: Frontiers in Molecular Neuroscience, Vol 14 (2021)
مصطلحات موضوعية: laminin, mouse model, clinical aspect, therapy, pathogenesis, Neurosciences. Biological psychiatry. Neuropsychiatry, RC321-571
وصف الملف: electronic resource
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8
المؤلفون: Sina Fatehi, Ryan M. Marks, Matthew J. Rok, Lucie Perillat, Evgueni A. Ivakine, Ronald D. Cohn
المصدر: Human Gene Therapy. 34:388-403
مصطلحات موضوعية: Genetics, Molecular Medicine, Molecular Biology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::8454367100364896b13e8aaa7e9196f4
https://doi.org/10.1089/hum.2023.059 -
9دورية أكاديميةTargeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
المؤلفون: Eleonora Maino, Daria Wojtal, Sonia L Evagelou, Aiman Farheen, Tatianna W Y Wong, Kyle Lindsay, Ori Scott, Samar Z Rizvi, Elzbieta Hyatt, Matthew Rok, Shagana Visuvanathan, Amanda Chiodo, Michelle Schneeweiss, Evgueni A Ivakine, Ronald D Cohn
المصدر: EMBO Molecular Medicine, Vol 13, Iss 5, Pp n/a-n/a (2021)
مصطلحات موضوعية: AAVs, CRISPR/Cas9, Duchenne muscular dystrophy, duplication mutations, genome editing, Medicine (General), R5-920, Genetics, QH426-470
وصف الملف: electronic resource
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10دورية أكاديمية
المصدر: BMC Bioinformatics, Vol 19, Iss S18, Pp 9-17 (2018)
مصطلحات موضوعية: Cancer pathology slides, TCGA, Sparse coding, Locally Competitive Algorithm, Unsupervised learning, Transfer learning, Computer applications to medicine. Medical informatics, R858-859.7, Biology (General), QH301-705.5
وصف الملف: electronic resource