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1دورية أكاديمية
المؤلفون: Sheikh, Omar, Yokota, ToshifumiAff1, IDs0020402103184z_cor2
المصدر: Archives of Toxicology. 96(1):1-9
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2دورية أكاديميةInjection site reactions after long-term subcutaneous delivery of drisapersen: a retrospective study
المؤلفون: Hilhorst, NielsAff1, Spanoudi-Kitrimi, IfigeniaAff1, Goemans, NathalieAff2, Morren, Marie-AnneAff1
المصدر: European Journal of Pediatrics. 178(2):253-258
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3دورية أكاديمية
المصدر: Orphanet Journal of Rare Diseases, Vol 13, Iss 1, Pp 1-13 (2018)
مصطلحات موضوعية: Eteplirsen, Drisapersen, Randomized controlled trial, Pooled estimates, 6-min walk test, Prospectively planned meta-analysis, Medicine
وصف الملف: electronic resource
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4دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
5دورية أكاديمية
المؤلفون: Shimizu-Motohashi, YukoAff1, Murakami, TerumiAff2, Kimura, EnAff3, Komaki, Hirofumi, Watanabe, NorioAff4
المصدر: Orphanet Journal of Rare Diseases. 13(1)
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المؤلفون: Sudhir Agarwal, Rakesh N. Veedu, Bao T. Le
المصدر: RSC Advances. 11:14029-14035
مصطلحات موضوعية: chemistry.chemical_classification, 0303 health sciences, Morpholino, Chemistry, General Chemical Engineering, RNA, General Chemistry, Computational biology, Exon skipping, 03 medical and health sciences, Exon, chemistry.chemical_compound, 0302 clinical medicine, 030220 oncology & carcinogenesis, splice, Nucleotide, DNA, Drisapersen, 030304 developmental biology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::eed747a78bcc6c90aaeb49f99626b468
https://doi.org/10.1039/d1ra00878a -
7دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
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المؤلفون: Nicole A. Datson, Cathaline den Besten, Judith C.T. van Deutekom, Sieto Bosgra, Sjef J. de Kimpe, Jessica A. Sipkens
المصدر: Nucleic Acid Therapeutics. 29:305-322
مصطلحات موضوعية: 0301 basic medicine, Oligonucleotide, business.industry, Duchenne muscular dystrophy, Computational biology, medicine.disease, Biochemistry, Exon skipping, Clinical trial, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, Pharmacokinetics, 030220 oncology & carcinogenesis, Pharmacodynamics, Drug Discovery, Genetics, medicine, Molecular Medicine, Distribution (pharmacology), business, Molecular Biology, Drisapersen
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::75f7c6184e4d7580eb6c29c0db62263d
https://doi.org/10.1089/nat.2019.0805 -
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المصدر: Frontiers in Pharmacology
Frontiers in Pharmacology, Vol 12 (2021)مصطلحات موضوعية: EXPRESSION, medicine.medical_specialty, utrophin upregulation, Duchenne muscular dystrophy, Genetic enhancement, randomized controlled clinical trials, Medizin, myostatin inhibition, Cardiomyopathy, RM1-950, PHASE-2 TRIAL, MYOSTATIN, dystrophin, OPEN-LABEL EXTENSION, DRISAPERSEN, SYSTEMIC DELIVERY, Medicine, Pharmacology (medical), Pharmacology & Pharmacy, GLUCOCORTICOIDS, ANTISENSE OLIGONUCLEOTIDE, Intensive care medicine, duchenne muscular dystrophy, Pharmacology, clinical trials, Science & Technology, RESPIRATORY-FUNCTION, biology, business.industry, medicine.disease, Exon skipping, Clinical trial, Perspective, Antisense oligonucleotides, biology.protein, Life expectancy, IDEBENONE, Therapeutics. Pharmacology, antisense oligonucleotides, business, Dystrophin, Life Sciences & Biomedicine, exon skipping
وصف الملف: Electronic-eCollection
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::317df4bb811a70872a7e3606c985db0b
https://doi.org/10.3389/fphar.2021.735912 -
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المؤلفون: Barry J. Byrne, Olga Mitelman, Sourav Santra, Jerry R. Mendell, Ashish Dugar, Anne M. Connolly, Hoda Z. Abdel-Hamid, Nathalie Goemans, Eugenio Mercuri, Peter Heydemann, Kathryn R. Wagner, Craig M. McDonald, Crystal Proud, Perry B. Shieh, James Signorovitch
المصدر: Journal of neuromuscular diseases. 9(1)
مصطلحات موضوعية: Duchenne muscular dystrophy, Male, Vital capacity, medicine.medical_specialty, Time Factors, 6-minutewalk test, Adolescent, Vital Capacity, Clinical Neurology, Walk Test, Eteplirsen, dystrophin, Pulmonary function testing, Morpholinos, DUCHENNE MUSCULAR-DYSTROPHY, 6-MINUTE WALK TEST, FEV1/FVC ratio, DRISAPERSEN, forced vital capacity, loss of ambulation, Internal medicine, END-POINTS, Outcome Assessment, Health Care, Medicine, Humans, eteplirsen, Prospective Studies, Registries, Mobility Limitation, Child, Retrospective Studies, Science & Technology, business.industry, Proportional hazards model, DISEASE PROGRESSION, Neurosciences, Repeated measures design, NATURAL-HISTORY, Muscular Dystrophy, Duchenne, Neurology, Ambulatory, Disease Progression, TRIAL, Neurosciences & Neurology, Neurology (clinical), business, Life Sciences & Biomedicine, Natural history study
وصف الملف: Print
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::00a25355a896eeef4db17d9cfa0c69a6
https://pubmed.ncbi.nlm.nih.gov/34420980