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1دورية أكاديمية
المؤلفون: Bulcaen, Mattijs, Kortleven, Phéline, Liu, Ronald B., Maule, Giulia, Dreano, Elise, Kelly, Mairead, Ensinck, Marjolein M., Thierie, Sam, Smits, Maxime, Ciciani, Matteo, Hatton, Aurelie, Chevalier, Benoit, Ramalho, Anabela S., Casadevall i Solvas, Xavier, Debyser, Zeger, Vermeulen, François, Gijsbers, Rik, Sermet-Gaudelus, Isabelle, Cereseto, Anna, Carlon, Marianne S.
المصدر: In Cell Reports Medicine 21 May 2024 5(5)
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2دورية أكاديمية
المؤلفون: Amistadi, Simone, Maule, Giulia, Ciciani, Matteo, Ensinck, Marjolein M., De Keersmaecker, Liesbeth, Ramalho, Anabela S., Guidone, Daniela, Buccirossi, Martina, Galietta, Luis J.V., Carlon, Marianne S., Cereseto, Anna
المصدر: In Molecular Therapy 7 June 2023 31(6):1647-1660
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3دورية أكاديمية
المؤلفون: Tiroille, Victor, Krug, Adrien, Bokobza, Emma, Kahi, Michel, Bulcaen, Mattijs, Ensinck, Marjolein M., Geurts, Maarten H., Hendriks, Delilah, Vermeulen, François, Larbret, Frédéric, Gutierrez-Guerrero, Alejandra, Chen, Yu, Van Zundert, Indra, Rocha, Susana, Rios, Anne C., Medaer, Louise, Gijsbers, Rik, Mangeot, Philippe E., Clevers, Hans, Carlon, Marianne S., Bost, Frédéric, Verhoeyen, Els
المصدر: In Molecular Therapy - Nucleic Acids June 2023
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4دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
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5دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
6دورية
المؤلفون: Bulcaen, Mattijs, Kortleven, Phéline, Liu, Ronald B., Maule, Giulia, Dreano, Elise, Kelly, Mairead, Ensinck, Marjolein M., Thierie, Sam, Smits, Maxime, Ciciani, Matteo, Hatton, Aurelie, Chevalier, Benoit, Ramalho, Anabela S., Casadevall i Solvas, Xavier, Debyser, Zeger, Vermeulen, François, Gijsbers, Rik, Sermet-Gaudelus, Isabelle, Cereseto, Anna, Carlon, Marianne S.
المصدر: Cell Reports Medicine; May 2024, Vol. 5 Issue: 5
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7دوريةFunctional restoration of a CFTRsplicing mutation through RNA delivery of CRISPR adenine base editor
المؤلفون: Amistadi, Simone, Maule, Giulia, Ciciani, Matteo, Ensinck, Marjolein M., De Keersmaecker, Liesbeth, Ramalho, Anabela S., Guidone, Daniela, Buccirossi, Martina, Galietta, Luis J.V., Carlon, Marianne S., Cereseto, Anna
المصدر: Molecular Therapy; 20230101, Issue: Preprints
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8
المؤلفون: Simone Amistadi, Giulia Maule, Matteo Ciciani, Marjolein M. Ensinck, Liesbeth De Keersmaecker, Anabela S. Ramalho, Daniela Guidone, Martina Buccirossi, Luis J.V. Galietta, Marianne S. Carlon, Anna Cereseto
المساهمون: Amistadi, Simone, Maule, Giulia, Ciciani, Matteo, Ensinck, Marjolein M, De Keersmaecker, Liesbeth, Ramalho, Anabela S, Guidone, Daniela, Buccirossi, Martina, Galietta, Luis Juan Vicente, Carlon, Marianne S, Cereseto, Anna
المصدر: Molecular Therapy.
مصطلحات موضوعية: Pharmacology, base editing, gene editing, organoid, Drug Discovery, Genetics, RNA delivery, primary bronchial epithelial cells, Molecular Medicine, CRISPR-Cas9, gene therapy, Molecular Biology, cystic fibrosi
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6d9d4ec4a3565a8516ca7963facd1b60
https://doi.org/10.1016/j.ymthe.2023.03.004