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1دورية أكاديمية
المؤلفون: Daniel C. De Souza, Nicolas Hebert, Erica B. Esrick, M. Felicia Ciuculescu, Natasha M. Archer, Myriam Armant, Étienne Audureau, Christian Brendel, Giuseppe Di Caprio, Frédéric Galactéros, Donghui Liu, Amanda McCabe, Emily Morris, Ethan Schonbrun, Dillon Williams, David K. Wood, David A. Williams, Pablo Bartolucci, John M. Higgins
المصدر: Nature Communications, Vol 14, Iss 1, Pp 1-10 (2023)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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المؤلفون: Mary Eapen, Ruta Brazauskas, David A. Williams, Mark C. Walters, Andrew St Martin, Benjamin L. Jacobs, Joseph H. Antin, Kira Bona, Sonali Chaudhury, Victoria H. Coleman-Cowger, Nancy L. DiFronzo, Erica B. Esrick, Joshua J. Field, Courtney D. Fitzhugh, Julie Kanter, Neena Kapoor, Donald B. Kohn, Lakshmanan Krishnamurti, Wendy B. London, Michael A. Pulsipher, Sohel Talib, Alexis A. Thompson, Edmund K. Waller, Ted Wun, Mary M. Horowitz
المصدر: Journal of Clinical Oncology. 41:2227-2237
مصطلحات موضوعية: Cancer Research, Oncology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::4f44a9e2a91572d49b8abe6af4b490cb
https://doi.org/10.1200/jco.22.01203 -
3دورية أكاديمية
المؤلفون: Daniel C. Souza, Nicolas Hebert, Erica B. Esrick, M. Felicia Ciuculescu, Natasha M. Archer, Myriam Armant, Étienne Audureau, Christian Brendel, Giuseppe Caprio, Frédéric Galactéros, Donghui
المصدر: Nature, Nature Communications. 14(1):1-10
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المؤلفون: Erica B. Esrick, Amy Federico, Daniela Abriss, Myriam Armant, Kari Boardman, Christian Brendel, Marioara-Felicia Ciuculescu, Heather Daley, Colleen Dansereau, Augustine Fernandes, Matthew M. Heeney, David G. Justus, Pei-Chi Kao, Annette S. Kim, Donald B. Kohn, Leslie E. Lehmann, Donghui Liu, Wendy B. London, John P Manis, Theodore B. Moore, Emily Morris, Danilo Pellin, Ellen Proeung, Shanna Richard, Gavin D. Roach, Kit L. Shaw, Dayna Terrazas, Shanna L White, David A. Williams
المصدر: Blood. 140:10665-10667
مصطلحات موضوعية: Immunology, Cell Biology, Hematology, Biochemistry
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::e828f889a6fcfac4de9b7fcb45370915
https://doi.org/10.1182/blood-2022-169089 -
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المؤلفون: David G. Justus, Erica B. Esrick, Matthew M. Heeney, Ellen Proeung, Carly Howard, Carlo Brugnara, David A. Williams, John P Manis
المصدر: Blood. 140:5715-5716
مصطلحات موضوعية: Immunology, Cell Biology, Hematology, Biochemistry
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::49992ab00a1033a02d7bc411a5cd1eaa
https://doi.org/10.1182/blood-2022-170450 -
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المؤلفون: Olivier Negre, Swaroopa Guda, Christian Brendel, Chad E. Harris, Martin Bentler, Myriam Armant, Melissa Bonner, Erica B. Esrick, John P. Manis, Helene Trebeden-Negre, Axel Schambach, Alla V. Tsytsykova, Danilo Pellin, Michael Rothe, Lauryn Christiansen, Denise Klatt, David A. Williams, Meaghan McGuinness, Daniela Abriss, Geoff Parsons, Gabor Istvan Veres
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 589-600 (2020)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, fetal hemoglobin, lcsh:QH426-470, Genetic enhancement, Cell, CD34, Biology, Article, Viral vector, Small hairpin RNA, 03 medical and health sciences, 0302 clinical medicine, RNA interference, BCL11A, Fetal hemoglobin, Genetics, medicine, shRNAmiR, lcsh:QH573-671, hemoglobinopathies, Molecular Biology, Gene knockdown, lcsh:Cytology, Sickle cell disease, lentiviral vector, gene therapy, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, HbS, 030220 oncology & carcinogenesis, hemoglobin switch, Cancer research, Molecular Medicine
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المؤلفون: Wendy B. London, Heather Daley, David A. Williams, Erica B. Esrick, Francis J. Pierciey, Luca Biasco, Alessandra Biffi, John P. Manis, Matthew M. Heeney, Myriam Armant, Helene Trebeden-Negre, Cristina Baricordi, Mohammed Asmal, Sarah Nikiforow
المصدر: Blood Advances. 2:2505-2512
مصطلحات موضوعية: Adult, 0301 basic medicine, Oncology, Benzylamines, medicine.medical_specialty, Adolescent, Clinical Trials and Observations, Genetic enhancement, CD34, Pilot Projects, Anemia, Sickle Cell, Cyclams, Immunophenotyping, Young Adult, 03 medical and health sciences, 0302 clinical medicine, Heterocyclic Compounds, Internal medicine, medicine, Humans, Progenitor cell, Hematopoietic Stem Cell Mobilization, Peripheral Blood Stem Cell Transplantation, Dose-Response Relationship, Drug, business.industry, Plerixafor, Genetic Therapy, Hematology, Hematopoietic Stem Cells, Haematopoiesis, 030104 developmental biology, Apheresis, Blood Component Removal, business, 030215 immunology, medicine.drug
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المؤلفون: Erica B, Esrick, Leslie E, Lehmann, Alessandra, Biffi, Maureen, Achebe, Christian, Brendel, Marioara F, Ciuculescu, Heather, Daley, Brenda, MacKinnon, Emily, Morris, Amy, Federico, Daniela, Abriss, Kari, Boardman, Radia, Khelladi, Kit, Shaw, Helene, Negre, Olivier, Negre, Sarah, Nikiforow, Jerome, Ritz, Sung-Yun, Pai, Wendy B, London, Colleen, Dansereau, Matthew M, Heeney, Myriam, Armant, John P, Manis, David A, Williams
المصدر: The New England journal of medicine. 384(3)
مصطلحات موضوعية: Adult, Male, Adolescent, Genetic Vectors, Down-Regulation, Pilot Projects, Anemia, Sickle Cell, Genetic Therapy, Transplantation, Autologous, Repressor Proteins, Young Adult, Gene Knockdown Techniques, Humans, Female, RNA Interference, gamma-Globins, RNA, Small Interfering, Child, Fetal Hemoglobin
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المؤلفون: Erica B. Esrick, Daniel E. Bauer
المصدر: Seminars in Hematology. 55:76-86
مصطلحات موضوعية: 0301 basic medicine, business.industry, Genetic enhancement, Plerixafor, Hematopoietic stem cell, Anemia, Sickle Cell, Genetic Therapy, Hematology, Disease, Bioinformatics, Clinical trial, Transplantation, 03 medical and health sciences, 030104 developmental biology, medicine.anatomical_structure, Genome editing, Fetal hemoglobin, medicine, Humans, business, medicine.drug
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المؤلفون: Jacob Bledsoe, Farid Boulad, Annette S. Kim, Laurie E. Cohen, Kaitlyn Ballotti, Elissa M. Furutani, Maggie Malsch, Marcin W. Wlodarski, Amy Hont, María José Ramírez, Erica B. Esrick, Alexis A. Thompson, Edie Weller, Jessica A. Pollard, Alan D. D'Andrea, Jordi Surrallés, Ashley Kuniholm, Ashley Galvin, Towia A. Libermann, Clinton Carroll, Akiko Shimamura, Kun Lu, Lisa A. Moreau, Shanshan Liu, Helge Hartung, Daria V. Babushok, Sei-Gyung K. Sze, Yu Zhou, Myriam Armant, Markus Grompe, Taizo A. Nakano, Timothy S. Olson
المصدر: Blood. 138:1102-1102
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, business.industry, Immunology, Cell Biology, Hematology, medicine.disease, Biochemistry, Metformin, Fanconi anemia, medicine, Young adult, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::8988dfb489d3161e305f8e7c38eae98c
https://doi.org/10.1182/blood-2021-153598