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1دورية أكاديمية
المؤلفون: Jaitip Tipanee, Mario Di Matteo, Warut Tulalamba, Ermira Samara-Kuko, Jiri Keirsse, Jo A. Van Ginderachter, Marinee Khim Chuah, Thierry VandenDriessche
المصدر: Molecular Therapy: Nucleic Acids, Vol 19, Iss , Pp 1309-1329 (2020)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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المؤلفون: Jaitip Tipanee, Ermira Samara-Kuko, Thierry Gevaert, Marinee K. Chuah, Thierry VandenDriessche
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Faculty of Medicine and Pharmacy, Radiation Therapy, Clinical sciences
مصطلحات موضوعية: Pharmacology, Receptors, Chimeric Antigen, chimeric antigen receptor, transposon, T-Lymphocytes, Antigens, CD19, Hematopoietic Stem Cell Transplantation, Receptors, Antigen, T-Cell, leukemia, Graft vs Host Disease, Immunotherapy, Adoptive, Biochemistry, Genetics and Molecular Biology (miscellaneous), Mice, Neoplasms, Drug Discovery, oncology, Genetics, Sleeping Beauty, Molecular Medicine, Animals, Immunotherapy, CRISPR-Cas Systems, CRISPR-Cas9, T cell receptor, Molecular Biology
وصف الملف: Print-Electronic
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ac7c20b01c9712273deacef0e8b6d162
https://hdl.handle.net/20.500.14017/b85a3a4c-051f-455c-9710-29d2e688ae6d -
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المؤلفون: Marinee Chuah, Nisha Nair, Dries De Wolf, Ermira Samara-Kuko, Phuong Anh Nguyen, Jeff Landau, Thierry VandenDriessche, Grant E. Blouse, Quang Hong Pham
المساهمون: Basic (bio-) Medical Sciences, Faculty of Medicine and Pharmacy, Division of Gene Therapy & Regenerative Medicine
المصدر: Blood
مصطلحات موضوعية: 0301 basic medicine, Bleeding Time, Genetic enhancement, Immunology, Genetic Vectors, Drug Evaluation, Preclinical, Gene Dosage, Inflammation, 030204 cardiovascular system & hematology, Pharmacology, Biochemistry, Hemophilia B, factor IX Padua, Factor IX, 03 medical and health sciences, CB 2679d-GT, Mice, 0302 clinical medicine, Bleeding time, medicine, Potency, Animals, Humans, Vector (molecular biology), Hemophilia, medicine.diagnostic_test, business.industry, Immunogenicity, AAV, Cell Biology, Hematology, Gene Therapy, Genetic Therapy, Hyperactive Factor IX, Dependovirus, Recombinant Proteins, Mice, Inbred C57BL, 030104 developmental biology, Amino Acid Substitution, Liver, Gain of Function Mutation, Toxicity, medicine.symptom, business, BLOOD Commentary, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::fbd1ae07385b612b03d2749fffad6c7b
https://pubmed.ncbi.nlm.nih.gov/34042982 -
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المؤلفون: Thierry VandenDriessche, Warut Tulalamba, Marinee Khim Chuah, Jo A. Van Ginderachter, Ermira Samara-Kuko, Jaitip Tipanee, Jiri Keirsse, Mario Di Matteo
المساهمون: Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Faculty of Medicine and Pharmacy, Cell Biology and Histology, Cellular and Molecular Immunology, Department of Bio-engineering Sciences
المصدر: Molecular Therapy: Nucleic Acids, Vol 19, Iss, Pp 1309-1329 (2020)
Molecular Therapy. Nucleic Acidsمصطلحات موضوعية: 0301 basic medicine, transposon, Genetic enhancement, NF-KAPPA-B, Research & Experimental Medicine, GROWTH-FACTOR-ALPHA, law.invention, non-viral vector, 0302 clinical medicine, Aurora kinase, law, AURORA KINASE, oncogene, HEPATOCELLULAR-CARCINOMA, Drug Discovery, Medicine(all), TRANSCRIPTIONAL MODULES, miR-17-92, PiggyBac, Gene Therapy, hepatocellular carcinoma, Medicine, Research & Experimental, 030220 oncology & carcinogenesis, Hepatocellular carcinoma, HRAS, Molecular Medicine, Liver cancer, Life Sciences & Biomedicine, Tumor suppressor gene, Biology, Article, CELL-PROLIFERATION, 03 medical and health sciences, microRNA, medicine, C-MYC, neoplasms, Science & Technology, SLEEPING-BEAUTY, Oncogene, lcsh:RM1-950, SOMATIC INTEGRATION, medicine.disease, digestive system diseases, 030104 developmental biology, lcsh:Therapeutics. Pharmacology, PROTEIN NETWORKS, Cancer research, Suppressor, miR-20a
وصف الملف: Print-Electronic
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd233a34f18ec84b306809428ebb9c45
https://doi.org/10.1016/j.omtn.2020.01.015 -
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المؤلفون: Marinee Chuah, Thierry VandenDriessche, Ermira Samara-Kuko, Nisha Nair, Kshitiz Singh, Shilpita Sarcar, Melvin Y Rincon, Hanneke Evens
المساهمون: Faculty of Medicine and Pharmacy, Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Cell Biology and Histology, Medicine and Pharmacy academic/administration
المصدر: Molecular Therapy
مصطلحات موضوعية: truncated gRNA, 0301 basic medicine, gRNA, Genetic Vectors, Biology, liver, Hemophilia B, Deep sequencing, Mice, 03 medical and health sciences, symbols.namesake, Genome editing, Drug Discovery, Genetics, Animals, Humans, CRISPR, Guide RNA, Cas9, Molecular Biology, Gene, Gene Editing, Pharmacology, Sanger sequencing, Binding Sites, factor IX, Base Sequence, Computational Biology, Gene targeting, AAV, Dependovirus, Phenotype, 030104 developmental biology, Organ Specificity, Gene Targeting, symbols, Molecular Medicine, Original Article, hepatocytes, CRISPR-Cas Systems, off-target, Protein Binding, RNA, Guide, Kinetoplastida
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::68bdd7332251bfd63a523f51d2b5bc38
https://doi.org/10.1016/j.ymthe.2018.02.023 -
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المؤلفون: M Chuah, Maurilio Sampaolesi, H. Q. Pham, P. In't Veld, Mariana Loperfido, D. Boon, Melvin Y Rincon, Susan Jarmin, P.j. De Bleser, Ermira Samara-Kuko, Hanneke Evens, Emanuele Berardi, Jaitip Tipanee, Marleen Keyaerts, Thierry VandenDriessche, Shilpita Sarcar, George Dickson, Warut Tulalamba, Tony Lahoutte
المساهمون: Faculty of Medicine and Pharmacy, Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Faculty of Sciences and Bioengineering Sciences, Supporting clinical sciences, Medical Imaging, Nuclear Medicine, Experimental Pathology, Pathology/molecular and cellular medicine, Diabetes Pathology & Therapy, Cell Biology and Histology
المصدر: Nature Communications
NATURE COMMUNICATIONS
Nature Communications, Vol 10, Iss 1, Pp 1-16 (2019)مصطلحات موضوعية: 0301 basic medicine, Male, Chemistry(all), Genetic enhancement, viruses, General Physics and Astronomy, Apoptosis, 02 engineering and technology, Mice, SCID, Transduction (genetics), Mice, Gene expression, chemistry (all), biochemistry, genetics and molecular biology (all), physics and astronomy (all), Medicine and Health Sciences, lcsh:Science, Promoter Regions, Genetic, Multidisciplinary, TRANSCRIPTIONAL MODULES, biology, AAV, 021001 nanoscience & nanotechnology, 3. Good health, Multidisciplinary Sciences, Science & Technology - Other Topics, SKELETAL-MUSCLE, 0210 nano-technology, CANINE, EXPRESSION, Transgene, Science, Genetic Vectors, Computational biology, Physics and Astronomy(all), Muscle disorder, TRANSDUCTION, Article, General Biochemistry, Genetics and Molecular Biology, Viral vector, PROMOTERS, 03 medical and health sciences, DELIVERY, Animals, Humans, Muscle, Skeletal, Science & Technology, Biochemistry, Genetics and Molecular Biology(all), Computational Biology, Biology and Life Sciences, Promoter, General Chemistry, Genetic Therapy, MUSCULAR-DYSTROPHY, CANINE MODEL, MODEL, MICE, 030104 developmental biology, Mutation, biology.protein, lcsh:Q, Follistatin
وصف الملف: Electronic; application/pdf
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المؤلفون: Jaitip Tipanee, Thierry VandenDriessche, Deepak Reyon, Simon Ardui, Peter In't Veld, Kshitiz Singh, J. Keith Joung, Warut Tulalamba, Denis Furling, Sara Seneca, Nisha Nair, Wito De Schrijver, Arnaud F. Klein, Marinee Chuah, Ermira Samara, Hui Wang, Joris Vermeesch, Francesco Tedesco, Yoke Chin Chai, Yanfang Fu, Debanjana Majumdar, Sumitava Dastidar, Mattia F. M. Gerli
المساهمون: Departement of gene therapy & regenerative medecine, Vrijz unversiteit Brussel, Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Faculty of Medicine and Pharmacy, Medicine and Pharmacy academic/administration, Faculty of Sciences and Bioengineering Sciences, Reproduction and Genetics, Clinical sciences, Medical Genetics, Pathology/molecular and cellular medicine, Diabetes Pathology & Therapy, Experimental Pathology
المصدر: Nucleic Acids Research
Nucleic Acids Research, Oxford University Press, 2018, 46, pp.8275-8298. ⟨10.1093/nar/gky548⟩مصطلحات موضوعية: 0301 basic medicine, musculoskeletal diseases, congenital, hereditary, and neonatal diseases and abnormalities, [SDV.BIO]Life Sciences [q-bio]/Biotechnology, Induced Pluripotent Stem Cells, Muscle disorder, Biology, Muscle Development, Myotonic dystrophy, Myoblasts, 03 medical and health sciences, chemistry.chemical_compound, Genome editing, Genetics, medicine, Humans, MBNL1, CRISPR, Child, Cells, Cultured, Gene Editing, Medicine(all), myotonic dystrophy, Cas9, Middle Aged, medicine.disease, Cell biology, 030104 developmental biology, chemistry, RNA splicing, Female, CRISPR-Cas Systems, Trinucleotide Repeat Expansion, Trinucleotide repeat expansion, myogenic cells, myotonic dystrophy patient-derived iPS
وصف الملف: Print
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::cdc601a8d22e5e3104dc8c16a9ef29c3
https://hal.archives-ouvertes.fr/hal-02357315 -
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المؤلفون: Marleen Keyaerts, Shilpita Sarcar, Takis Athanasopoulos, Melvin Y Rincon, George Dickson, Ermira Samara-Kuko, Abel Acosta-Sanchez, Dina Danso-Abeam, Tony Lahoutte, Marinee Chuah, Thierry VandenDriessche, Janka Matrai, Pieter De Bleser
المساهمون: Medical Imaging, Medical Imaging and Physical Sciences, Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Supporting clinical sciences, Cell Biology and Histology
المصدر: Molecular Therapy
MOLECULAR THERAPYمصطلحات موضوعية: LIVER, Transcription, Genetic, Cytomegalovirus, Gene Expression, ADENOASSOCIATED VIRAL VECTORS, DISEASE, Mice, Gene expression, Drug Discovery, Myocytes, Cardiac, Promoter Regions, Genetic, Cardiomyocytes, Genetics, Regulation of gene expression, Genome, Gene Therapy, Dependovirus, Cardiovascular disease, 3. Good health, Cardiovascular Diseases, Molecular Medicine, Original Article, Genetic Engineering, Protein Binding, EXPRESSION, Therapeutic gene modulation, Genetic Vectors, Molecular Sequence Data, Computational biology, Biology, CRMs, Viral vector, Ventricular Myosins, DELIVERY, Animals, Humans, Nucleotide Motifs, Transcription factor, Gene, Molecular Biology, CALCIUM UP-REGULATION, Pharmacology, Reporter gene, Binding Sites, Myocardium, Biology and Life Sciences, Computational Biology, FACTOR-IX, Genetic Therapy, hereditary disease, Treatment, Mice, Inbred C57BL, DNA binding site, MICE, HEMOPHILIA-B, TRANSDUCTION IN-VIVO, Transcription Factors
وصف الملف: application/pdf
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المؤلفون: Maurilio Sampaolesi, George Dickson, Ermira Samara-Kuko, Ilaria Perini, Nisha Nair, Marinee Chuah, Sumitava Dastidar, Mariana Loperfido, Thierry VandenDriessche, Francesco Tedesco, Marc Moore, Takis Athanasopoulos, Mario Di Matteo, Susan Jarmin
المساهمون: Basic (bio-) Medical Sciences, Cell Biology and Histology, Division of Gene Therapy & Regenerative Medicine
المصدر: Nucleic Acids Research
Nucleic acids research, 44 (2مصطلحات موضوعية: 0301 basic medicine, Transposable element, Duchenne muscular dystrophy, Male, Myoblasts, Skeletal, targeted gene modification, Green Fluorescent Proteins, DNA-mediated, cell transformation, nucleic acids transfer, Biology, Transfection, Transposition (music), Dystrophin, 03 medical and health sciences, Dogs, Genetics, medicine, Animals, Humans, Muscular dystrophy, Gene, dystrophic mesoangioblasts, Molecular Biology, Transposase, Cells, Cultured, Medicine(all), Myogenesis, Stem Cells, PiggyBac, Cell Differentiation, Gene Therapy, Genetic Therapy, medicine.disease, Molecular biology, Muscular Dystrophy, Duchenne, 030104 developmental biology, biology.protein, DNA Transposable Elements, genetic neuromuscular disorder, Biologie
وصف الملف: Print-Electronic; 2 full-text file(s): application/pdf; application/pdf
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::20c684de425f6f4394e228467d8fe45c
https://nar.oxfordjournals.org/content/44/2/744.long -
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المؤلفون: Alessio Cantore, Andrea Annoni, Anne Arens, Timothy C. Nichols, Marinee Chuah, Christof von Kalle, Pietro Genovese, Liesbeth De Waele, Thierry VandenDriessche, Ermira Samara-Kuko, Maria Grazia Roncarolo, Manfred G. Schmidt, Luigi Naldini, Cynthia C. Bartholomae, Ling Ma, Wei Wang, Janka Matrai, Martina Damo, Abel Acosta-Sanchez, Kevin Goudy
المساهمون: Cell Biology and Histology, Division of Gene Therapy & Regenerative Medicine, Mátrai, J, Cantore, A, Bartholomae, Cc, Annoni, A, Wang, W, Acosta Sanchez, A, Samara Kuko, E, De Waele, L, Ma, L, Genovese, P, Damo, M, Arens, A, Goudy, K, Nichols, Tc, von Kalle, C, L., Chuah MK, Roncarolo, MARIA GRAZIA, Schmidt, M, Vandendriessche, T, Naldini, Luigi
المصدر: Hepatology (Baltimore, Md.)
Hepatology
Hepatology; Vol 53مصطلحات موضوعية: Risk, Transgene, Genetic enhancement, Genetic Vectors, medicine.disease_cause, liver, in-vivo, adenoassociated virus, Immune tolerance, Insertional mutagenesis, 03 medical and health sciences, Epitopes, Mice, 0302 clinical medicine, Antigen, Liver Biology/Pathobiology, medicine, Immune Tolerance, Animals, Humans, Vector (molecular biology), Hemophilia, Cells, Cultured, 030304 developmental biology, 0303 health sciences, Mutation, therapy, Mice, Inbred BALB C, Hepatology, biology, Integrases, Lentivirus, FACTOR-IX, Virology, nondividing cells, Integrase, Cell biology, 030220 oncology & carcinogenesis, biology.protein, Hepatocytes, Hepatic gene-transfer, Female, delivery, transgene expression, DNA Damage
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