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1دورية أكاديمية
المؤلفون: Michelle A. Farrar, Ewout Groen, Christiano Alves
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 96-97 (2022)
مصطلحات موضوعية: adeno-associated virus, dorsal root ganglion, gene therapy, neurofilament, toxicity, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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المؤلفون: Nora Tula Detering, Alberto Zambon, Niko Hensel, Rashmi Kothary, Kathryn Swoboda, Thomas H. Gillingwater, Giovanni Baranello, Simon Parson, Mariascristina Scoto, Melissa Bowerman, John Vissing, Brunhilde Wirth, Peter Claus, Janbernd Kirschner, Enrico Bertini, Stefania Corti, Lorenzo Maggi, Ludo van der Pol, Ewout Groen, Charlotte Sumner, Eduardo Tizzano, Susana Quijano Roy, Isabelle Desguerre, Alexander Van Nuijs, Mencia De Lemus, Rivka Smit, Mary Schroth, Ben Tichler, Ksenija Gorni, Deepa Chand
المصدر: Neuromuscular Disorders. 32:697-705
مصطلحات موضوعية: RC925, Neurology, Pediatrics, Perinatology and Child Health, Neurology (clinical), R1, Genetics (clinical)
وصف الملف: application/vnd.openxmlformats-officedocument.wordprocessingml.document