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1دورية أكاديمية
المؤلفون: Franco Locatelli, Nanxin LI, Suzan Imren, Fengjuan Xuan, Jaime Rubin, Bill Hobbs, Haydar Frangoul
المصدر: HemaSphere, Vol 7, p e6522522 (2023)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Jennifer L. Taylor-Cousar, Marcus A. Mall, Bonnie W. Ramsey, Edward F. McKone, Elizabeth Tullis, Gautham Marigowda, Charlotte M. McKee, David Waltz, Samuel M. Moskowitz, Jessica Savage, Fengjuan Xuan, Steven M. Rowe
المصدر: ERJ Open Research, Vol 5, Iss 2 (2019)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
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المؤلفون: Julie K. Bower, Nataliya Volkova, Neil Ahluwalia, Gurvaneet Sahota, Fengjuan Xuan, Anna Chin, Tanya G. Weinstock, Josh Ostrenga, Alexander Elbert
المصدر: Journal of Cystic Fibrosis.
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Pediatrics, Perinatology and Child Health
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المؤلفون: Edward F. McKone, Chenghao Chu, Claire E. Wainwright, Neil Ahluwalia, Samuel M. Moskowitz, Paul McNally, Edith T. Zemanick, Ronald L. Gibson, Jane Davies, Fengjuan Xuan, Steven M. Rowe, Tanya G. Weinstock, Bonnie W. Ramsey, Elizabeth Tullis, Susanna A McColley, David Waltz, S. Tian, Thang Ho, Jonathan H. Rayment, Sabrina Noel, Marcus A. Mall, Jennifer L. Taylor-Cousar
المصدر: American Journal of Respiratory and Critical Care Medicine. 203:1522-1532
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, business.industry, Critical Care and Intensive Care Medicine, medicine.disease, Cystic fibrosis, Gastroenterology, Ivacaftor, Open label study, Internal medicine, medicine, Tezacaftor, In patient, Allele, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::b290c0c5bcd62ab9c6e67b0b24ad8799
https://doi.org/10.1164/rccm.202102-0509oc -
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المؤلفون: Harry G M Heijerman, Edward F McKone, Damian G Downey, Eva Van Braeckel, Steven M Rowe, Elizabeth Tullis, Marcus A Mall, John J Welter, Bonnie W Ramsey, Charlotte M McKee, Gautham Marigowda, Samuel M Moskowitz, David Waltz, Patrick R Sosnay, Christopher Simard, Neil Ahluwalia, Fengjuan Xuan, Yaohua Zhang, Jennifer L Taylor-Cousar, Karen S McCoy, Karen McCoy, Scott Donaldson, Seth Walker, James Chmiel, Ronald Rubenstein, Deborah K. Froh, Isabel Neuringer, Manu Jain, Kathryn Moffett, Jennifer L. Taylor-Cousar, Bruce Barnett, Gary Mueller, Patrick Flume, Floyd Livingston, Nighat Mehdi, Charlotte Teneback, John Welter, Raksha Jain, Dana Kissner, Kapilkumar Patel, Francisco J. Calimano, Jimmy Johannes, Cori Daines, Thomas Keens, Herschel Scher, Subramanyam Chittivelu, Sudhakar Reddivalam, Ross Carl Klingsberg, Larry G. Johnson, Stijn Verhulst, Patricia Macedo, Damien Downey, Gary Connett, Edward Nash, Nicholas Withers, Timothy Lee, Marleen Bakker, Harry Heijerman, Francois Vermeulen, Christiane Knoop, Elke De Wachter, Renske van der Meer, Petrus Merkus, Christof Majoor
المساهمون: Pulmonology, AII - Inflammatory diseases, Clinical sciences, Physiotherapy, Human Physiology and Anatomy, Pediatrics
المصدر: Lancet, 394(10212), 1940-1948. Elsevier Limited
VX17-445-103 Trial Group 2019, ' Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial ', Lancet, vol. 394, no. 10212, pp. 1940 . https://doi.org/10.1016/S0140-6736(19)32597-8
Lancet
The Lancet, 394(10212), 1940. Elsevier Limitedمصطلحات موضوعية: Male, Indoles, Pyrrolidines, Cystic Fibrosis, Pyridines, Clinical Trial, Phase III, Phases of clinical research, Cystic Fibrosis Transmembrane Conductance Regulator, 030204 cardiovascular system & hematology, Quinolones, Aminophenols, Cystic fibrosis, law.invention, Ivacaftor, chemistry.chemical_compound, 0302 clinical medicine, Randomized controlled trial, law, 030212 general & internal medicine, Pyridines/administration & dosage, Non-U.S. Gov't, Chloride Channel Agonists, Sweat, Child, Chloride Channel Agonists/administration & dosage, Medicine(all), biology, Research Support, Non-U.S. Gov't, Lumacaftor, General Medicine, Indoles/administration & dosage, Clinical Trial, Cystic fibrosis transmembrane conductance regulator, Pyrrolidines/administration & dosage, Quinolones/administration & dosage, Randomized Controlled Trial, Combination, Drug Therapy, Combination, Female, medicine.drug, medicine.medical_specialty, Adolescent, Research Support, Article, Benzodioxoles/administration & dosage, Sweat/chemistry, N.I.H, 03 medical and health sciences, Phase III, Research Support, N.I.H., Extramural, Double-Blind Method, Drug Therapy, Internal medicine, Journal Article, medicine, Aminophenols/administration & dosage, Humans, Benzodioxoles, business.industry, Extramural, medicine.disease, Pyrazoles/administration & dosage, Clinical trial, Regimen, chemistry, biology.protein, Pyrazoles, Cystic Fibrosis Transmembrane Conductance Regulator/genetics, sense organs, Cystic Fibrosis/drug therapy, business
وصف الملف: application/pdf; text/plain
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المؤلفون: Edith T, Zemanick, Jennifer L, Taylor-Cousar, Jane, Davies, Ronald L, Gibson, Marcus A, Mall, Edward F, McKone, Paul, McNally, Bonnie W, Ramsey, Jonathan H, Rayment, Steven M, Rowe, Elizabeth, Tullis, Neil, Ahluwalia, Chenghao, Chu, Thang, Ho, Samuel M, Moskowitz, Sabrina, Noel, Simon, Tian, David, Waltz, Tanya G, Weinstock, Fengjuan, Xuan, Claire E, Wainwright, Susanna A, McColley
المصدر: American Journal of Respiratory and Critical Care Medicine
مصطلحات موضوعية: Male, Indoles, Cystic Fibrosis, Genotype, Editorials, Cystic Fibrosis Transmembrane Conductance Regulator, Genetic Variation, Quinolones, Drug Combinations, Humans, Pyrazoles, Female, Child, Chloride Channel Agonists, Alleles
URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::7b742e3ae048f25e1e4fb2b3abbdc267
https://pubmed.ncbi.nlm.nih.gov/33901406 -
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المؤلفون: Charlotte M. McKee, Marcus A. Mall, Jennifer L. Taylor-Cousar, Fengjuan Xuan, Samuel M. Moskowitz, Edward F. McKone, Gautham Marigowda, Steven M. Rowe, Bonnie W. Ramsey, Jessica H. Savage, Elizabeth Tullis, David Waltz
المصدر: ERJ Open Research, Vol 5, Iss 2 (2019)
ERJ Open Researchمصطلحات موضوعية: Pulmonary and Respiratory Medicine, congenital, hereditary, and neonatal diseases and abnormalities, Cystic Fibrosis, lcsh:Medicine, Pharmacology, medicine.disease_cause, Cystic fibrosis, Ivacaftor, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Medicine, 030212 general & internal medicine, Allele, Regulator gene, Mutation, business.industry, lcsh:R, Lumacaftor, Original Articles, respiratory system, Potentiator, medicine.disease, digestive system diseases, Transmembrane protein, respiratory tract diseases, 3. Good health, 030228 respiratory system, chemistry, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::de7ff6e62545f5529ffc2096dd6494db
https://doi.org/10.1183/23120541.00082-2019 -
8دورية أكاديمية
المؤلفون: Zemanick, Edith T., Taylor-Cousar, Jennifer L., Davies, Jane, Gibson, Ronald L., Mall, Marcus A., McKone, Edward F., McNally, Paul, Ramsey, Bonnie W., Rayment, Jonathan H., Rowe, Steven M., Tullis, Elizabeth, Ahluwalia, Neil, Chenghao Chu, Thang Ho, Moskowitz, Samuel M., Noel, Sabrina, Tian, Simon, Waltz, David, Weinstock, Tanya G., Fengjuan Xuan
المصدر: American Journal of Respiratory & Critical Care Medicine; 6/15/2021, Vol. 203 Issue 12, p1522-1532, 53p
مصطلحات موضوعية: CYSTIC fibrosis treatment, LUNG disease diagnosis, LUNG disease treatment, ALLELES, CHILD care, LAXATIVES, RESEARCH, INDOLE compounds, GENETICS, COMBINATION drug therapy, CLINICAL trials, HETEROCYCLIC compounds, RESEARCH methodology, MEDICAL cooperation, EVALUATION research, CYSTIC fibrosis, COMPARATIVE studies, GENOTYPES, MEMBRANE proteins, QUINOLONE antibacterial agents
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المؤلفون: Friedrich Overkamp, M. Miller, S Kümmel, Christian M. Kurbacher, Thomas Decker, Fengjuan Xuan, J Wilke, A Nusch, Marianne Just, W Abenhardt, F Marmé, Norbert Marschner, Wolfgang Janni, EM Grischke
المصدر: Geburtshilfe und Frauenheilkunde. 76
مصطلحات موضوعية: Gynecology, Oncology, medicine.medical_specialty, Postmenopausal women, business.industry, Letrozole, Advanced breast, Obstetrics and Gynecology, Cancer, Ribociclib, medicine.disease, Prior Therapy, Hormone receptor, Internal medicine, Maternity and Midwifery, Advanced disease, Medicine, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::779f31389849e71636dbc49a34ea5e70
https://doi.org/10.1055/s-0036-1592812 -
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المؤلفون: Anne Favret, Kimberly L. Blackwell, Samit Hirawat, Erik Jakobsen, Carlos L. Arteaga, Emilio Alba, Shani Paluch-Shimon, Pierfranco Conte, Salomon M. Stemmer, Mario Campone, A. Chan, Lowell L. Hart, Thomas Bachelot, Fengjuan Xuan, David Cameron, Sunil Verma, Sibel Blau, Denise A. Yardley, Gabe S. Sonke, Farida Souami, Gabriel N. Hortobagyi, Katarína Petráková, Norbert Marschner, Wolfgang Janni, Fabrice Andre, Cristian Villanueva, Arnd Nusch, Eric P. Winer, Olga Burdaeva, Yoon Sim Yap, Joyce O'Shaughnessy, C. Germa, Michelle Miller, Erik Wist, Eva-Maria Grischke, Ling-Ming Tseng, Howard A. Burris
المصدر: Hortobagyi, G N, Stemmer, S M, Burris, H A, Yap, Y-S, Sonke, G S, Paluch-Shimon, S, Campone, M, Blackwell, K L, André, F, Winer, E P, Janni, W, Verma, S, Conte, P, Arteaga, C L, Cameron, D A, Petrakova, K, Hart, L L, Villanueva, C, Chan, A, Jakobsen, E, Nusch, A, Burdaeva, O, Grischke, E-M, Alba, E, Wist, E, Marschner, N, Favret, A M, Yardley, D, Bachelot, T, Tseng, L-M, Blau, S, Xuan, F, Souami, F, Miller, M, Germa, C, Hirawat, S & O’Shaughnessy, J 2016, ' Ribociclib as First-Line Therapy for HR-Positive, Advanced Breast Cancer ', New England Journal of Medicine, vol. 375, no. 18, pp. 1738-1748 . https://doi.org/10.1056/NEJMoa1609709
مصطلحات موضوعية: 0301 basic medicine, Oncology, Receptor, ErbB-2, Aminopyridines, Kaplan-Meier Estimate, ErbB-2, 0302 clinical medicine, Receptors, Antineoplastic Combined Chemotherapy Protocols, 80 and over, Clinical endpoint, Progesterone, Aged, 80 and over, Medicine (all), Letrozole, General Medicine, Middle Aged, Metastatic breast cancer, Receptors, Estrogen, 030220 oncology & carcinogenesis, Female, Receptors, Progesterone, Receptor, medicine.drug, Adult, medicine.medical_specialty, Breast Neoplasms, Palbociclib, Placebo, Disease-Free Survival, Drug Administration Schedule, 03 medical and health sciences, Double-Blind Method, Internal medicine, Nitriles, medicine, Humans, Aged, Neoplasm Staging, Purines, Triazoles, Gynecology, business.industry, Cancer, Interim analysis, medicine.disease, Estrogen, Clinical trial, 030104 developmental biology, business
وصف الملف: application/pdf
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1d8dab1e35ee3ea5009a3a02e3727218
https://hdl.handle.net/10668/10515