المؤلفون: Matsuzaki, Shu^{Aff1, Aff2}, Sakuma, Tetsushi^{Aff1, IDs11626024008501_cor2}, Yamamoto, Takashi

المصدر: In Vitro Cellular & Developmental Biology - Animal. 60(7):697-707

المؤلفون: Schneider, Ronen, Mansour, Bshara, Kolvenbach, Caroline M.^{Aff1, Aff2}, Buerger, Florian, Salmanullah, Daanya, Lemberg, Katharina, Merz, Lea M.^{Aff1, Aff3}, Mertens, Nils D., Saida, Ken, Yousef, Kirollos, Franken, Gijs A. C., Bao, Aaron, Yu, Seyoung, Hölzel, Selina, Nicolas-Frank, Camille, Steinsapir, Andrew, Goncalves, Kevin A., Shril, Shirlee, Hildebrandt, Friedhelm^{Aff1, IDs40620024019878_cor19}

المصدر: Journal of Nephrology. :1-10

المؤلفون: Shannon M. McNamee, Monica Akula, Zoe Love, Neelaab Nasraty, Kaden Nystuen, Pushpendra Singh, Arun K. Upadhyay, Margaret M. DeAngelis, Neena B. Haider

المصدر: Scientific Reports, Vol 14, Iss 1, Pp 1-14 (2024)

مصطلحات موضوعية: Gene replacement, AAV, Retinitis pigmentosa, rd7, Mouse, Electroretinography, Medicine, Science

وصف الملف: electronic resource

Relation: https://doaj.org/toc/2045-2322

URL الوصول: https://doaj.org/article/760fb0df93694cf99cd9a1e2ee8b751e

المؤلفون: Minskaia, Ekaterina^{Aff1, IDS0006297923120179_cor1}, Galieva, Alima, Egorov, Alexander D., Ivanov, Roman, Karabelsky, Alexander

المصدر: Biochemistry (Moscow). 88(12-13):2157-2178

المؤلفون: Toro, Walter^{Aff1, IDs1232502302685w_cor1}, Yang, Min, Georgieva, Mihaela, Anderson, Annika, LaMarca, Nicole, Patel, Anish, Akbarnejad, Hanane, Dabbous, Omar

المصدر: Advances in Therapy. 40(12):5315-5337

المؤلفون: Lynch, Michael R., author

المصدر: Evolutionary Cell Biology : The Origins of Cellular Architecture, 2024, ill.

الإتاحة: https://doi.org/10.1093/oso/9780192847287.003.0019

المؤلفون: Anna Mateu-Bosch, Eulàlia Segur-Bailach, Emma Muñoz-Moreno, María José Barallobre, Maria Lourdes Arbonés, Sabrina Gea-Sorlí, Frederic Tort, Antonia Ribes, Judit García-Villoria, Cristina Fillat

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 3, Pp 101276- (2024)

مصطلحات موضوعية: glutaric aciduria, metabolic disease, viral vectors, gene replacement, adeno-associated virus, AAV, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000925; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/592b220094f1481fa456c9ea81e1525a

المؤلفون: Wang, Ming^{Aff1, Aff2, Aff3}, Ding, Fangrong, Wang, Haiping, Li, Ling, Dai, Yunping^{Aff2, IDs12915023016770_cor5}, Sun, ZhaoLin^{Aff1, Aff2, Aff3, IDs12915023016770_cor6}, Li, Ning^{Aff2, Aff3, IDs12915023016770_cor7}

المصدر: BMC Biology. 21(1)

المؤلفون: M. Zhong, B. Balakrishnan, A.J. Guo, K. Lai

المصدر: Molecular Genetics and Metabolism Reports, Vol 38, Iss , Pp 101035- (2024)

مصطلحات موضوعية: Inherited phosphomannomutase 2 deficiency (PMM2-CDG), Congenital disorders of glycosylation, AAV9 gene replacement therapy, Primary fibroblast cell model, Medicine (General), R5-920, Biology (General), QH301-705.5

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2214426923000812; https://doaj.org/toc/2214-4269

URL الوصول: https://doaj.org/article/d41aef350c394227aee71af1f7777a11

المؤلفون: Ming Wang, Fangrong Ding, Haiping Wang, Ling Li, Yunping Dai, ZhaoLin Sun, Ning Li

المصدر: BMC Biology, Vol 21, Iss 1, Pp 1-17 (2023)

مصطلحات موضوعية: Bovine, Precise gene editing, Point mutation, Targeted deletion, Gene tagging, Gene replacement, Biology (General), QH301-705.5

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1741-7007

URL الوصول: https://doaj.org/article/7a89b29a834a4dd6be08d91b8da714c5