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1دورية أكاديمية
المؤلفون: Kirti Prasad, Nivedhitha Devaraju, Anila George, Nithin Sam Ravi, Joshua Paul, Gokulnath Mahalingam, Vignesh Rajendiran, Lokesh Panigrahi, Vigneshwaran Venkatesan, Kartik Lakhotiya, Yogapriya Periyasami, Aswin Anand Pai, Yukio Nakamura, Ryo Kurita, Poonkuzhali Balasubramanian, Saravanabhavan Thangavel, Shaji R. Velayudhan, Gregory A. Newby, Srujan Marepally, Alok Srivastava, Kumarasamypet M. Mohankumar
المصدر: Molecular Therapy: Nucleic Acids, Vol 35, Iss 2, Pp 102205- (2024)
مصطلحات موضوعية: MT: RNA/DNA Editing, genome editing, base editor, β-thalassemia mutations, HbE/CD26(G>A), gene correction, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Katarina Kulhankova, Soumba Traore, Xue Cheng, Hadrien Benk-Fortin, Stéphanie Hallée, Mario Harvey, Joannie Roberge, Frédéric Couture, Sajeev Kohli, Thomas J. Gross, David K. Meyerholz, Garrett R. Rettig, Bernice Thommandru, Gavin Kurgan, Christine Wohlford-Lenane, Dennis J. Hartigan-O’Connor, Bradley P. Yates, Gregory A. Newby, David R. Liu, Alice F. Tarantal, David Guay, Paul B. McCray
المصدر: Nature Communications, Vol 14, Iss 1, Pp 1-16 (2023)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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3دورية أكاديمية
المؤلفون: Anya T. Joynt, Erin W. Kavanagh, Gregory A. Newby, Shakela Mitchell, Alice C. Eastman, Kathleen C. Paul, Alyssa D. Bowling, Derek L. Osorio, Christian A. Merlo, Shivani U. Patel, Karen S. Raraigh, David R. Liu, Neeraj Sharma, Garry R. Cutting
المصدر: Molecular Therapy: Nucleic Acids, Vol 33, Iss , Pp 335-350 (2023)
مصطلحات موضوعية: MT: RNA/DNA Editing, canonical splice site variant, CSSV, CRISPR-Cas9-mediated adenine base editing, ABE, primary airway epithelial cells, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Ashley L. Cooney, Christian M. Brommel, Soumba Traore, Gregory A. Newby, David R. Liu, Paul B. McCray, Patrick L. Sinn
المصدر: Frontiers in Genome Editing, Vol 5 (2023)
مصطلحات موضوعية: adeno-associated virus capsid, gene therapy, cystic fibrosis, airway epithelia, base editing, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Meha Kabra, Pawan K. Shahi, Yuyuan Wang, Divya Sinha, Allison Spillane, Gregory A. Newby, Shivani Saxena, Yao Tong, Yu Chang, Amr A. Abdeen, Kimberly L. Edwards, Cole O. Theisen, David R. Liu, David M. Gamm, Shaoqin Gong, Krishanu Saha, Bikash R. Pattnaik
المصدر: The Journal of Clinical Investigation, Vol 133, Iss 19 (2023)
مصطلحات موضوعية: Ophthalmology, Medicine
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1558-8238
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6دورية أكاديمية
المؤلفون: Elliot H. Choi, Susie Suh, Andrzej T. Foik, Henri Leinonen, Gregory A. Newby, Xin D. Gao, Samagya Banskota, Thanh Hoang, Samuel W. Du, Zhiqian Dong, Aditya Raguram, Sajeev Kohli, Seth Blackshaw, David C. Lyon, David R. Liu, Krzysztof Palczewski
المصدر: Nature Communications, Vol 13, Iss 1, Pp 1-14 (2022)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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7دورية أكاديمية
المؤلفون: Chang Li, Aphrodite Georgakopoulou, Gregory A. Newby, Kelcee A. Everette, Evangelos Nizamis, Kiriaki Paschoudi, Efthymia Vlachaki, Sucheol Gil, Anna K. Anderson, Theodore Koob, Lishan Huang, Hongjie Wang, Hans-Peter Kiem, David R. Liu, Evangelia Yannaki, André Lieber
المصدر: JCI Insight, Vol 7, Iss 19 (2022)
مصطلحات موضوعية: Hematology, Stem cells, Medicine
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2379-3708
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8دورية أكاديمية
المؤلفون: Pan Gao, Qing Lyu, Amr R. Ghanam, Cicera R. Lazzarotto, Gregory A. Newby, Wei Zhang, Mihyun Choi, Orazio J. Slivano, Kevin Holden, John A. Walker, Anastasia P. Kadina, Rob J. Munroe, Christian M. Abratte, John C. Schimenti, David R. Liu, Shengdar Q. Tsai, Xiaochun Long, Joseph M. Miano
المصدر: Genome Biology, Vol 22, Iss 1, Pp 1-21 (2021)
مصطلحات موضوعية: Mouse, CRISPR, Prime editing, Genome editing, Transcription, Gene expression, Biology (General), QH301-705.5, Genetics, QH426-470
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1474-760X
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9دورية أكاديمية
المؤلفون: Tingting Jiang, Jordana M. Henderson, Kevin Coote, Yi Cheng, Hillary C. Valley, Xiao-Ou Zhang, Qin Wang, Luke H. Rhym, Yueying Cao, Gregory A. Newby, Hermann Bihler, Martin Mense, Zhiping Weng, Daniel G. Anderson, Anton P. McCaffrey, David R. Liu, Wen Xue
المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-9 (2020)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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10
المؤلفون: Daniel Reichart, Gregory A. Newby, Hiroko Wakimoto, Mingyue Lun, Joshua M. Gorham, Justin J. Curran, Aditya Raguram, Daniel M. DeLaughter, David A. Conner, Júlia D. C. Marsiglia, Sajeev Kohli, Lukas Chmatal, David C. Page, Nerea Zabaleta, Luk Vandenberghe, David R. Liu, Jonathan G. Seidman, Christine Seidman
المصدر: Nature Medicine. 29:412-421
مصطلحات موضوعية: General Medicine, General Biochemistry, Genetics and Molecular Biology