-
1دورية أكاديمية
المؤلفون: Alisha M. Gruntman, Gwladys Gernoux, Qiushi Tang, Guo-Jie Ye, Dave R. Knop, Gensheng Wang, Janet Benson, Kristen E. Coleman, Allison M. Keeler, Christian Mueller, Louis G. Chicoine, Jeffrey D. Chulay, Terence R. Flotte
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 13, Iss , Pp 233-242 (2019)
وصف الملف: electronic resource
-
2
المؤلفون: Guo-jie Ye, Chunjuan Song, Judith A Newmark, Artur V. Cideciyan, Paulette M. Robinson, William A. Beltran, Adrian M. Timmers, David R. Knop, Jeffrey D. Chulay, Valerie L. Dufour, Mark S. Shearman, Malgorzata Swider, Samuel G. Jacobson, Gustavo D. Aguirre
المصدر: Human Gene Therapy. 31:743-755
مصطلحات موضوعية: congenital, hereditary, and neonatal diseases and abnormalities, genetic structures, viruses, Genetic enhancement, Transgene, Range finding, law.invention, 03 medical and health sciences, 0302 clinical medicine, law, Retinitis pigmentosa, Genetics, medicine, In patient, Molecular Biology, 030304 developmental biology, 0303 health sciences, business.industry, medicine.disease, eye diseases, 030220 oncology & carcinogenesis, Cancer research, Recombinant DNA, Molecular Medicine, sense organs, X-linked retinitis pigmentosa, business, Canine model
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::3d5934e3222dc6e28d819ad2a74f3319
https://doi.org/10.1089/hum.2019.337 -
3
المؤلفون: Qiushi Tang, Gensheng Wang, Christian Mueller, Gwladys Gernoux, Dave R. Knop, Louis G. Chicoine, Terence R. Flotte, Kristen E. Coleman, Allison M. Keeler, Alisha M. Gruntman, Guo-jie Ye, Janet M. Benson, Jeffrey D. Chulay
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 13, Iss, Pp 233-242 (2019)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, Muscle tissue, lcsh:QH426-470, Genetic enhancement, Transgene, Pharmacology, Virus, Article, law.invention, 03 medical and health sciences, 0302 clinical medicine, law, Genetics, Limb perfusion, medicine, Potency, lcsh:QH573-671, Molecular Biology, biology, business.industry, lcsh:Cytology, biology.organism_classification, Rhesus macaque, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, 030220 oncology & carcinogenesis, Recombinant DNA, Molecular Medicine, business
-
4
المؤلفون: Savitri Mandapati, Chunjuan Song, Alok K. Sharma, Mailin Van Hoosear, William W. Hauswirth, Guo-jie Ye, Jeffrey D. Chulay, Adrian M. Timmers, Cayrn Plummer, Ping Zhu, David R. Knop, Kari B. Green, Paulette M. Robinson, Peter Sonnentag, Wen-Tao Deng, Mark S. Shearman, Thomas J. Conlon, Kirsten E. Coleman
المصدر: Human Gene Therapy Clinical Development. 29:188-197
مصطلحات موضوعية: 0301 basic medicine, G-Protein-Coupled Receptor Kinase 1, Genetic enhancement, law.invention, Mice, 03 medical and health sciences, law, Complementary DNA, Retinitis pigmentosa, medicine, Animals, Codon, Eye Proteins, Gene, Research Articles, Genetics (clinical), medicine.diagnostic_test, HEK 293 cells, Genetic Therapy, Retinitis pigmentosa GTPase regulator, Dependovirus, medicine.disease, Molecular biology, eye diseases, 030104 developmental biology, Recombinant DNA, sense organs, Carrier Proteins, Retinitis Pigmentosa, Electroretinography
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3b489755bd2d1a5d95261f2a3fbdae5a
https://doi.org/10.1089/humc.2018.168 -
5
المؤلفون: Chunjuan, Song, Valérie L, Dufour, Artur V, Cideciyan, Guo-Jie, Ye, Malgorzata, Swider, Judith A, Newmark, Adrian M, Timmers, Paulette M, Robinson, David R, Knop, Jeffrey D, Chulay, Samuel G, Jacobson, Gustavo D, Aguirre, William A, Beltran, Mark S, Shearman
المصدر: Hum Gene Ther
مصطلحات موضوعية: Male, Genetic Vectors, Genetic Diseases, X-Linked, Genetic Therapy, Dependovirus, eye diseases, Dogs, Mutation, Animals, Female, Transgenes, Eye Proteins, Retinitis Pigmentosa, Research Articles
URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::e2be0c995000c54107b1d9fc3480798d
https://pubmed.ncbi.nlm.nih.gov/32414297 -
6
المؤلفون: Chunjuan Song, Mark S. Shearman, Guo-jie Ye, Artur V. Cideciyan, Paulette M. Robinson, Gui-Shuang Ying, Gustavo D. Aguirre, Valerie L. Dufour, Malgorzata Swider, Adrian M. Timmers, William A. Beltran, Nicole M. Weinstein, Perry L. Habecker, Wei Pan, David R. Knop, Samuel G. Jacobson, Jeffrey D. Chulay, Amy C. Durham
المصدر: Hum Gene Ther
مصطلحات موضوعية: Retinal degeneration, viruses, Genetic enhancement, Biopsy, Genetic Vectors, Retinitis, Biology, medicine.disease_cause, Virus, law.invention, Cell Line, 03 medical and health sciences, 0302 clinical medicine, Dogs, law, Genes, X-Linked, Research Article—Clinical Development, Genetics, medicine, Electroretinography, Animals, Humans, Vector (molecular biology), Codon, Eye Proteins, Molecular Biology, Adeno-associated virus, 030304 developmental biology, 0303 health sciences, Correction, Genetic Therapy, Dependovirus, medicine.disease, Virology, Immunohistochemistry, eye diseases, 030220 oncology & carcinogenesis, Toxicity, Mutation, Recombinant DNA, Molecular Medicine, Biomarkers, Retinitis Pigmentosa, Tomography, Optical Coherence
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f17baaee2c96a459978db598f5984fe3
https://pubmed.ncbi.nlm.nih.gov/32589471 -
7
المؤلفون: Chantelle Gaskin, Tanaz Farivar, Heikki T Turunen, David R. Knop, Chunjuan Song, Judith A Newmark, Mark S. Shearman, Steven Pennock, Guo-jie Ye, Adrian M. Timmers, Jilin Liu
المصدر: Human gene therapy. 31(1-2)
مصطلحات موضوعية: viruses, medicine.medical_treatment, Genetic Vectors, Inflammation, Genome, Viral, Biology, medicine.disease_cause, Virus, law.invention, 03 medical and health sciences, Mice, 0302 clinical medicine, Immunophenotyping, law, Genes, Reporter, Transduction, Genetic, Genetics, medicine, Animals, Humans, Vector (molecular biology), Transgenes, Molecular Biology, Adeno-associated virus, 030304 developmental biology, 0303 health sciences, Endophthalmitis, Gene Transfer Techniques, Genetic Therapy, Dependovirus, Virology, Immunohistochemistry, Disease Models, Animal, Cytokine, Capsid, Gene Expression Regulation, 030220 oncology & carcinogenesis, Recombinant DNA, Molecular Medicine, Cytokines, Capsid Proteins, medicine.symptom, Biomarkers
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0eafab03a357ba8a3a65e2b0391a695d
https://pubmed.ncbi.nlm.nih.gov/31544533 -
8
المؤلفون: Guo-jie Ye, Chunjuan Song, Mark S. Shearman, Jeff Chulay
المصدر: Human gene therapy. Clinical development. 30(1)
مصطلحات موضوعية: Genetics, Mice, Hum, Animals, Vector (molecular biology), Genetic Therapy, Biology, Dependovirus, Codon optimized, Codon, Gene, Genetics (clinical)
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bac064db1a43ca6451e075a2c6bd6daf
https://pubmed.ncbi.nlm.nih.gov/30888916 -
9
المؤلفون: Terence R. Flotte, Guo-jie Ye, Jeffrey D. Chulay, Bruce C. Schnepp, Philip R. Johnson, Bruce C. Trapnell
المصدر: Human Gene Therapy. 27:32-42
مصطلحات موضوعية: 0301 basic medicine, congenital, hereditary, and neonatal diseases and abnormalities, Sequence analysis, Genetic Vectors, Biology, medicine.disease_cause, Genome, Virus, law.invention, 03 medical and health sciences, Plasmid, law, Genetics, medicine, Humans, Vector (molecular biology), Muscle, Skeletal, Molecular Biology, Gene, Adeno-associated virus, Research Articles, Base Sequence, Genetic Therapy, Dependovirus, Virology, Molecular biology, 030104 developmental biology, Recombinant DNA, Molecular Medicine, Plasmids
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3aa56b9c069103c07ca33f9d82faf645
https://doi.org/10.1089/hum.2015.136 -
10
المؤلفون: Jeffrey D. Chulay, Jim Peterson, Guo-jie Ye, William W. Hauswirth, Nader Sheibani, Shannon E. Boye, Sanford L. Boye, Ewa Budzynski, Zafer Gurel, T Michael Nork, Peter Sonnentag
المصدر: Human Gene Therapy. 27:72-82
مصطلحات موضوعية: 0301 basic medicine, Achromatopsia, genetic structures, Genetic enhancement, Genetic Vectors, Green Fluorescent Proteins, Gene Expression, Color Vision Defects, Biology, Green fluorescent protein, Mice, 03 medical and health sciences, Dogs, Retinal Diseases, Gene expression, Genetics, medicine, Animals, Humans, Vector (molecular biology), Promoter Regions, Genetic, Molecular Biology, Gene, Research Articles, Gene Transfer Techniques, Rod Opsins, Promoter, Genetic Therapy, Dependovirus, medicine.disease, eye diseases, Cell biology, 030104 developmental biology, Retinal Cone Photoreceptor Cells, Molecular Medicine, sense organs, Transducin
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6dc1c5126c6a2fedd4e41af67e1cf7cc
https://doi.org/10.1089/hum.2015.130