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1دورية أكاديمية
المؤلفون: Eric W. Johnson, Jeffrey J. Sutherland, Emily Meseck, Cameron McElroy, Deepa H. Chand, Francis Fonyuy Tukov, Eloise Hudry, Kelley Penraat
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 208-219 (2023)
مصطلحات موضوعية: adeno-associated virus 9 gene therapy, cerebrospinal fluid, dorsal root ganglia/trigeminal ganglia pathology, dorsal root ganglia toxicity, nonclinical toxicology, neurofilament light chain, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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المصدر: Hemodialysis International.
مصطلحات موضوعية: Nephrology, Hematology
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المؤلفون: Deepa H. Chand, Rui Sun, Karim A. Diab, Damien Kenny, Francis Fonyuy Tukov
المصدر: Gene Therapy.
مصطلحات موضوعية: Genetics, Molecular Medicine, Molecular Biology
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4تقرير
المؤلفون: I M McHardy, S D Connolly, K Horne, E M Cackett, J Gelbord, B M Peterson, M Pahari, N Gehrels, M Goad, P Lira, P Arevalo, R D Baldi, N Brandt, E Breedt, H Chand, G Dewangan, C Done, M Elvis, D Emmanoulopoulos, M M Fausnaugh, S Kaspi, C S Kochanek, K Korista, I E Papadakis, A R Rao, P Uttley, M Vestergaard, M J Ward
المصدر: Monthly Notices of the Royal Astronomical Society. 480(3):2881-2897
URL الوصول: https://ntrs.nasa.gov/citations/81379455959322
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المؤلفون: H Chand, S Hassan, A Cairo, R Palla, F Peyvandi
المصدر: GTH Congress 2023 – 67th Annual Meeting of the Society of Thrombosis and Haemostasis Research – The patient as a benchmark.
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::cd01957cf6a665a9521c3c9ee05244de
https://doi.org/10.1055/s-0042-1760539 -
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المؤلفون: Cahyani Gita Ambarsari, Rachel A. Annunziato, Evamaria Anvari, Carlos E. Araya, Rossella Attini, Rose Mary Ayoob, Justine Bacchetta, Rossana Baracco, Joanne M. Bargman, Antonio Bellasi, Ezequiel Bellorin-Font, William M. Bennett, Scott Bieber, Mei Lin Z. Bissonnette, Geoffrey A. Block, Brendan Bowman, Patrick D. Brophy, Deborah J. Brouwer-Maier, Steven Brunelli, David Bushinsky, Jonathan Casavant, Roberta Cerutti, Vimal Chadha, Christopher T. Chan, Bipan Chand, Deepa H. Chand, Anthony Chang, Chaim Charytan, Joline L.T. Chen, Wei Chen, Andrew I. Chin, Yeoungjee Cho, William R. Clark, John H. Crabtree, Daniel Cukor, Serpil Muge Deger, Lucia Del Vecchio, Alonso R. Diaz, Stephanie L. Donahue, Ramanath Dukkipati, Claire Dunphy, Mohamed Elbokl, Fabrizio Fabrizi, Mohammed K. Faizan, Steven Fishbane, Molly Fisher, William Henry Fissell, Jorge Ignacio Fonseca-Correa, Bethany J. Foster, Seth B. Furgeson, Ashley M. Gefen, Guido Gembillo, F. John Gennari, Marc Ghannoum, Griet Glorieux, Sharlene Anuska Greenwood, Dieter Haffner, Rainer Himmele, Jean L. Holley, Daljit K. Hothi, T. Alp Ikizler, Sarbjit Vanita Jassal, Kirsten L. Johansen, David W. Johnson, Kamyar Kalantar-Zadeh, Pranay Kathuria, Irfan Khan, Paul L. Kimmel, Alan S. Kliger, Timothy Koh Jee Kam, Berfu Korucu, Pelagia Koufaki, Eugene C. Kovalik, Robin A. Kremsdorf, Martin Kreuzer, Mahesh Krishnan, Martin K. Kuhlmann, Danica Lam, Yu-Chi Lapid, Francesco Locatelli, Joseph B. Lockridge, Charmaine E. Lok, Etienne Macedo, John D. Mahan, Harold J. Manley, Kevin J. Martin, Nicola Matthews, Juliet Mayes, Ian E. McCoy, Christopher W. Mcintyre, Rajnish Mehrotra, Ravindra L. Mehta, Mark M. Mitsnefes, Michele H. Mokrzycki, Bogdan Momciu, Liz Mooney, Alvin H. Moss, Vinay Narasimha Krishna, Sharon J. Nessim, Allen R. Nissenson, Vandana Dua Niyyar, Ali Olyaei, Alejandra Orozco-Guillén, David I. Ortiz-Melo, Biff F. Palmer, Suetonia C. Palmer, Patrick S. Parfrey, Jeffery Perl, Giorgina B. Piccoli, Joanne D. Pittard, Connie M. Rhee, Ezequiel Ridruejo, Claudio Rigatto, Matthew B. Rivara, Darren M. Roberts, AnnaMarie Rodriguez, Mariano Rodriguez, Rudolph A. Rodriguez, Claudio Ronco, Mitchell H. Rosner, John H. Sadler, Valeria Saglimbene, Fabio R. Salerno, Domenico Santoro, Franz Schaefer, Christine B. Sethna, Hitesh H. Shah, Jenny I. Shen, Jeffrey Silberzweig, Rossella Siligato, Pamela S. Singer, Michael J.G. Somers, null Soo, Bruce Spinowitz, Deborah Stein, Emily Stonebrook, Giovanni F.M. Strippoli, Cheuk-Chun Szeto, Isaac Teitelbaum, Rebecca Thomas-Chen, Ashita J. Tolwani, Massimo Torreggiani, Avram Z. Traum, Luis G. Tulloch-Palomino, Tushar J. Vachharajani, Rudolph P. Valentini, Peter Noel Van Buren, René G. VanDeVoorde, Raymond Vanholder, Thanh-Mai Vo, Bradley A. Warady, Adam Weinstein, Katherine Wesseling-Perry, James B. Wetmore, Mark E. Williams, Jay B. Wish, Joshua J. Zaritsky
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::72a1da8126fc9020044e15338151d9c7
https://doi.org/10.1016/b978-0-323-79135-9.09989-4 -
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المؤلفون: R. Zanin, A. Seferian, N. Brolatti, A. Govoni, L. Edel, A. Jollet, M. Del Sole, Arseniy Lavrov, M.T. Arnoldi, E. De Vos, Eugenio Mercuri, L. Antonaci, G. Coratti, M. Pedemonte, Haojun Ouyang, K. Groves, O. Schneider, M. Foa, Volker Straub, A.C. Defeldre, G. Comi, Stefania Corti, V. Parente, A. Jonas, R.M. Lofra, Laurent Servais, Riccardo Masson, L. Buscemi, Nicolas Deconinck, S. De Lucia, Aurore Daron, M.C. Pera, Claudio Bruno, E. Pagliano, S. Mouffak, Nuno Mendonca, A. Vanlander, Deepa H. Chand, E. Thompson, H. Van Ruiten, V. Tahon, Giovanni Baranello, S. Tachibana, M. Pane, S. Morando, Francesco Muntoni, R. de Sanctis, V. Schembri, F. Dal Farra, A. Mandelli, Odile Boespflug-Tanguy, Sitra Tauscher-Wisniewski, M. Scoto, F. Abel, F. Magri
المصدر: The Lancet Neurology. 20:832-841
مصطلحات موضوعية: Infusions, medicine.medical_specialty, Neuromuscular disease, Spinal, Population, SMN1, Spinal Muscular Atrophies of Childhood, Muscular Atrophy, Spinal, Settore MED/39 - NEUROPSICHIATRIA INFANTILE, Internal medicine, medicine, Clinical endpoint, Humans, Dosing, Child, Infusions, Intravenous, education, education.field_of_study, Settore MED/48 - SCIENZE INFERMIERISTICHE E TECNICHE NEURO-PSICHIATRICHE E RIABILITATIVE, business.industry, Infant, Genetic Therapy, Spinal muscular atrophy, medicine.disease, gene therapy, Muscular Atrophy, Settore MED/26 - NEUROLOGIA, Clinical research, Pharmaceutical Preparations, Cohort, Neurology (clinical), Intravenous, business, spinal muscular atrrophy
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المؤلفون: Francis Fonyuy Tukov, John W. Day, Richard S. Finkel, Kevin A. Strauss, Deepa H. Chand, Jerry R. Mendell, Aaron Kleyn, Sitra Tauscher-Wisniewski, Sandra P. Reyna, Eugenio Mercuri
المصدر: Drug Safety
مصطلحات موضوعية: medicine.medical_specialty, Thrombotic microangiopathy, Prednisolone, Postmarketing surveillance, Physical examination, Toxicology, Intracardiac injection, Muscular Atrophy, Spinal, Mice, Internal medicine, medicine, Animals, Humans, Pharmacology (medical), Original Research Article, Adverse effect, Pharmacology, Biological Products, Clinical Trials as Topic, medicine.diagnostic_test, business.industry, Genetic Therapy, medicine.disease, Clinical trial, Concomitant, Chemical and Drug Induced Liver Injury, business, medicine.drug
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10دورية أكاديمية
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