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1دورية أكاديمية
المؤلفون: Agostina Carestia, Seok-Joo Kim, Franziska Horling, Hanspeter Rottensteiner, Christian Lubich, Birgit M. Reipert, Brian A. Crowe, Craig N. Jenne
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 95-108 (2021)
مصطلحات موضوعية: Adeno-associated virus-8, gene therapy, liver, immune response, intravital imaging, inflammation, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Paolo Rossato, Enrica Federti, Alessandro Matte, Helmut Glantschnig, Fabio Canneva, Maria Schuster, Sogue Coulibaly, Gerald Schrenk, Dirk Voelkel, Michael Dockal, Barbara Plaimauer, Immacolata Andolfo, Achille Iolascon, Hanspeter Rottensteiner, Herbert Gritsch, Friedrich Scheiflinger, Werner Hoellriegl, Lucia De Franceschi
المصدر: Haematologica, Vol 107, Iss 11 (2022)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Wenjing Cao, Biao Dong, Franziska Horling, Jenni A. Firrman, Johannes Lengler, Matthias Klugmann, Maurus de la Rosa, Wenman Wu, Qizhao Wang, Hongying Wei, Andrea R. Moore, Sean A. Roberts, Carmen J. Booth, Werner Hoellriegl, Dong Li, Barbara Konkle, Carol Miao, Birgit M. Reipert, Friedrich Scheiflinger, Hanspeter Rottensteiner, Weidong Xiao
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 19, Iss , Pp 486-495 (2020)
مصطلحات موضوعية: factor VIII, AAV, gene therapy, X5, secretion, vector, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Johannes Lengler, Sogue Coulibaly, Bernadette Gruber, Reinhard Ilk, Josef Mayrhofer, Friedrich Scheiflinger, Werner Hoellriegl, Falko G. Falkner, Hanspeter Rottensteiner
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 581-588 (2020)
مصطلحات موضوعية: adeno-associated virus, gene therapy, biopotency, coagulation factor IX, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Alfred Weber, Andrea Engelmaier, Dirk Voelkel, Robert Pachlinger, Friedrich Scheiflinger, Paul E. Monahan, Hanspeter Rottensteiner
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 29-37 (2018)
وصف الملف: electronic resource
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6دورية أكاديمية
المؤلفون: Louis Deforche, Claudia Tersteeg, Elien Roose, Aline Vandenbulcke, Nele Vandeputte, Inge Pareyn, Elien De Cock, Hanspeter Rottensteiner, Hans Deckmyn, Simon F De Meyer, Karen Vanhoorelbeke
المصدر: PLoS ONE, Vol 11, Iss 8, p e0160388 (2016)
وصف الملف: electronic resource
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7دورية أكاديمية
المؤلفون: Rana Grillberger, Veronica C. Casina, Peter L. Turecek, X. Long Zheng, Hanspeter Rottensteiner, Friedrich Scheiflinger
المصدر: Haematologica, Vol 99, Iss 4 (2014)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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8دورية أكاديمية
المؤلفون: Silvia Ferrari, Kristina Palavra, Bernadette Gruber, Johanna A. Kremer Hovinga, Paul Knöbl, Claudine Caron, Caroline Cromwell, Louis Aledort, Barbara Plaimauer, Peter L. Turecek, Hanspeter Rottensteiner, Friedrich Scheiflinger
المصدر: Haematologica, Vol 99, Iss 4 (2014)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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9دورية أكاديمية
المؤلفون: Ygal Benhamou, Cyrielle Assié, Pierre-Yves Boelle, Marc Buffet, Rana Grillberger, Sandrine Malot, Alain Wynckel, Claire Presne, Gabriel Choukroun, Pascale Poullin, François Provôt, Didier Gruson, Mohamed Hamidou, Dominique Bordessoule, Jacques Pourrat, Jean-Paul Mira, Véronique Le Guern, Claire Pouteil-Noble, Cédric Daubin, Philippe Vanhille, Eric Rondeau, Jean-Bernard Palcoux, Christiane Mousson, Cécile Vigneau, Guy Bonmarchand, Bertrand Guidet, Lionel Galicier, Elie Azoulay, Hanspeter Rottensteiner, Agnès Veyradier, Paul Coppo
المصدر: Haematologica, Vol 97, Iss 8 (2012)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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10
المؤلفون: Bruce Ewenstein, Maurus de la Rosa, Barbara A. Konkle, Ivan Bilic, Birgit M. Reipert, Paul E. Monahan, Scott W.J. McPhee, R. Jude Samulski, Hanspeter Rottensteiner, Miguel A. Escobar, Neil C. Josephson, John C. Chapin, Friedrich Scheiflinger, Annette von Drygalski, Guy Young, Christopher E. Walsh
المصدر: Blood
مصطلحات موضوعية: 0301 basic medicine, Oncology, medicine.medical_specialty, CpG Oligodeoxynucleotide, Genetic enhancement, Immunology, Gene Expression, Hemophilia B, Biochemistry, 03 medical and health sciences, 0302 clinical medicine, Immune system, Internal medicine, medicine, Humans, Adverse effect, Prospective cohort study, bcl-2-Associated X Protein, Factor IX, Regulation of gene expression, business.industry, Gene Therapy, Genetic Therapy, Cell Biology, Hematology, Dependovirus, Clinical trial, 030104 developmental biology, 030220 oncology & carcinogenesis, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2e8ff7d5209306c46cbe07c2ddd9a785
https://doi.org/10.1182/blood.2019004625