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1دورية أكاديمية
المؤلفون: Laura J. Smith, Lindsay A. Schulman, Samantha Smith, Laura Van Lieshout, Carmen M. Barnes, Liana Behmoiras, Meghan Scarpitti, Monicah Kivaa, Khanh L. Duong, Ludo O. Benard, Jeff L. Ellsworth, Nancy Avila, Deiby Faulkner, April Hayes, Jason Lotterhand, Jose Israel Rivas, Arnold V. Sengooba, Alec Tzianabos, Albert B. Seymour, Omar L. Francone
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 224-238 (2022)
مصطلحات موضوعية: gene therapy, adeno-associated virus, AAV, tropism/biodistribution, glycan binding, structure-function relationship, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Seemin S. Ahmed, Hillard Rubin, Minglun Wang, Deiby Faulkner, Arnold Sengooba, Serena N. Dollive, Nancy Avila, Jeff L. Ellsworth, Diana Lamppu, Maria Lobikin, Jason Lotterhand, Laura Adamson-Small, Teresa Wright, Albert Seymour, Omar L. Francone
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 568-580 (2020)
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Jeff L. Ellsworth, Nels Hamacher, Nancy Bagwell, James W. West
المصدر: BioTechniques, Vol 28, Iss 5, Pp 934-937 (2000)
مصطلحات موضوعية: Biology (General), QH301-705.5
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Huei-Mei Chen, Rachel Resendes, Azita Ghodssi, Danielle Sookiasian, Michael Tian, Serena Dollive, Laura Adamson-Small, Nancy Avila, Cagdas Tazearslan, John F Thompson, Jeff L Ellsworth, Omar Francone, Albert Seymour, Jason B Wright
المصدر: PLoS ONE, Vol 15, Iss 5, p e0233373 (2020)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1932-6203
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5دورية أكاديمية
المؤلفون: Jeff L Ellsworth, Jacinthe Gingras, Laura J Smith, Hillard Rubin, Tania A Seabrook, Kruti Patel, Nicole Zapata, Kevin Olivieri, Michael O'Callaghan, Elizabeth Chlipala, Pablo Morales, Albert Seymour
المصدر: PLoS ONE, Vol 14, Iss 11, p e0225582 (2019)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1932-6203
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6
المؤلفون: Minglun Wang, Hillard Rubin, Jason Lotterhand, Omar L. Francone, Maria Lobikin, Seemin Seher Ahmed, Albert B. Seymour, Diana Lamppu, Laura Adamson-Small, Serena Nicole Dollive, Jeff L. Ellsworth, Teresa Leah Wright, Nancy Avila, Arnold Sengooba, Deiby Faulkner
المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 568-580 (2020)مصطلحات موضوعية: 0301 basic medicine, lcsh:QH426-470, Phenylalanine hydroxylase, Genetic enhancement, Metabolite, Transgene, Phenylalanine, Pharmacology, Article, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Genetics, medicine, lcsh:QH573-671, Tyrosine, Molecular Biology, chemistry.chemical_classification, biology, lcsh:Cytology, business.industry, medicine.disease, lcsh:Genetics, 030104 developmental biology, Enzyme, chemistry, Inborn error of metabolism, 030220 oncology & carcinogenesis, biology.protein, Molecular Medicine, business
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7
المؤلفون: Hillard Rubin, Laura J. Smith, Kruti Patel, Tania A. Seabrook, Jeff L. Ellsworth, Jacinthe Gingras, Albert B. Seymour
المصدر: Molecular Genetics and Metabolism. 129:S62
مصطلحات موضوعية: Nervous system, Endocrinology, medicine.anatomical_structure, Endocrinology, Diabetes and Metabolism, Genetics, medicine, Biology, Molecular Biology, Biochemistry, Neuroscience
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8
المؤلفون: Hillard Rubin, Jacinthe Gingras, Kevin Olivieri, Pablo E. Morales, Elizabeth A. Chlipala, Jeff L. Ellsworth, Laura J. Smith, Albert B. Seymour, Michael O'Callaghan, Nicole Zapata, Kruti Patel, Tania A. Seabrook
المصدر: PLoS ONE, Vol 14, Iss 11, p e0225582 (2019)
PLoS ONEمصطلحات موضوعية: Central Nervous System, Pathology, Monkeys, Nervous System, Green fluorescent protein, 0302 clinical medicine, Animal Cells, Ganglia, Spinal, Medicine and Health Sciences, Tissue Distribution, Vector (molecular biology), Routes of Administration, Neurons, Staining, Mammals, 0303 health sciences, Multidisciplinary, Cell Staining, Eukaryota, Dependovirus, Immunohistochemistry, medicine.anatomical_structure, Spinal Cord, Blood-Brain Barrier, Vertebrates, Medicine, Administration, Intravenous, Cellular Types, Anatomy, Neuroglia, Macaque, Research Article, Primates, medicine.medical_specialty, Science, Genetic Vectors, Green Fluorescent Proteins, Central nervous system, Biology, Research and Analysis Methods, Blood–brain barrier, 03 medical and health sciences, Intravenous Injections, Old World monkeys, medicine, Animals, Humans, Cytoplasmic Staining, 030304 developmental biology, Pharmacology, Biology and life sciences, Organisms, Genetic Therapy, Cell Biology, Spinal cord, Neuroanatomy, HEK293 Cells, nervous system, Specimen Preparation and Treatment, Cellular Neuroscience, Amniotes, Tissue tropism, Macaca, 030217 neurology & neurosurgery, Neuroscience
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9Stem cell-derived clade F AAVs mediate high-efficiency homologous recombination-based genome editing
المؤلفون: Laura J. Smith, Jason Wright, Gabriella Clark, Taihra Ul-Hasan, Xiangyang Jin, Abigail Fong, Manasa Chandra, Thia St Martin, Hillard Rubin, David Knowlton, Jeff L. Ellsworth, Yuman Fong, Kamehameha K. Wong, Saswati Chatterjee
المصدر: Proceedings of the National Academy of Sciences of the United States of America. 115(31)
مصطلحات موضوعية: 0301 basic medicine, Genetic Vectors, Locus (genetics), Computational biology, Biology, medicine.disease_cause, Corrections, Homology (biology), 03 medical and health sciences, Genome editing, medicine, Humans, Homologous Recombination, Gene, Adeno-associated virus, BRCA2 Protein, Gene Editing, Multidisciplinary, Hematopoietic stem cell, Dependovirus, Hematopoietic Stem Cells, 030104 developmental biology, medicine.anatomical_structure, Human genome, Homologous recombination, K562 Cells, Interleukin Receptor Common gamma Subunit
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::02fbc8ccc62b56f807738b53d249157c
https://pubmed.ncbi.nlm.nih.gov/30584108 -
10
المصدر: Human Gene Therapy Clinical Development.
مصطلحات موضوعية: 0301 basic medicine, Serotype, Population, Genetic Vectors, Biology, medicine.disease_cause, Serogroup, Cell Line, 03 medical and health sciences, Seroepidemiologic Studies, Cell Line, Tumor, medicine, Seroprevalence, Humans, Luciferase, Clade, education, Adeno-associated virus, Genetics (clinical), education.field_of_study, Racial Groups, Dependovirus, Virology, Antibodies, Neutralizing, United States, Titer, 030104 developmental biology, biology.protein, Antibody
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::373c333d871fcdb7ca1345ea2ca09132
https://doi.org/10.1089/hum.2017.239