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1دورية أكاديمية
المؤلفون: Mark A. Brimble, Pei-Hsin Cheng, Stephen M. Winston, Isaiah L. Reeves, Aisha Souquette, Yunyu Spence, Junfang Zhou, Yong-Dong Wang, Christopher L. Morton, Marcus Valentine, Paul G. Thomas, Amit C. Nathwani, John T. Gray, Andrew M. Davidoff
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 24, Iss , Pp 280-291 (2022)
مصطلحات موضوعية: Adeno-associated virus, gene therapy, rAAV, P5, vectorology, contamination, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Jenny A. Greig, Jayme M.L. Nordin, Christine Draper, Deirdre McMenamin, Edward A. Chroscinski, Peter Bell, John T. Gray, Laura K. Richman, James M. Wilson
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 237-244 (2018)
وصف الملف: electronic resource
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المؤلفون: Laura K. Richman, Jayme M.L. Nordin, Peter Bell, Edward A. Chroscinski, James M. Wilson, Jenny A. Greig, Christine Draper, John T. Gray, Deirdre McMenamin
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss, Pp 237-244 (2018)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, lcsh:QH426-470, Bilirubin, Crigler–Najjar syndrome, Genetic enhancement, adeno-associated virus, Pharmacology, liver, medicine.disease_cause, Article, 03 medical and health sciences, chemistry.chemical_compound, Genetics, medicine, lcsh:QH573-671, Molecular Biology, Adeno-associated virus, Crigler-Najjar Syndrome, Clinical pathology, lcsh:Cytology, business.industry, Jaundice, medicine.disease, Effective dose (pharmacology), lcsh:Genetics, 030104 developmental biology, chemistry, Knockout mouse, Molecular Medicine, bilirubin, medicine.symptom, business
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4
المؤلفون: David L. Mack, Jean-Baptiste Dupont, Ana Buj-Bello, Michael W. Lawlor, Robert W. Grange, John T. Gray, Jianjun Guo, Martin K. Childers
مصطلحات موضوعية: 0303 health sciences, Pathology, medicine.medical_specialty, Gene transfer, Spinal muscular atrophy, Biology, medicine.disease, X-linked myotubular myopathy, Biceps, 3. Good health, law.invention, Transcriptome, 03 medical and health sciences, 0302 clinical medicine, law, Gene expression, medicine, Recombinant DNA, Gene, 030217 neurology & neurosurgery, 030304 developmental biology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4005986ac78bc21c9d069085cd04e9ae
https://doi.org/10.1101/499384 -
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المؤلفون: Suyash Prasad, Tim Stinchcombe, Salvador Rico, Christina Chaivorapol, Emma James, Jacqueline Brassard, John T. Gray, Garrett Heffner, Fulvio Mavilio, Justine Cunningham, Michelle Eggers
المصدر: Molecular Genetics and Metabolism. 129:S106
مصطلحات موضوعية: business.industry, Endocrinology, Diabetes and Metabolism, Skeletal muscle, Disease, Bioinformatics, Biochemistry, Novel gene, Endocrinology, medicine.anatomical_structure, Genetics, Clinical safety, Medicine, business, Molecular Biology
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المؤلفون: Vincent J Carson, Michael D Fox, Kevin A. Strauss, Michael W. Lawlor, Han-Zhong Feng, John T. Gray, Karlla W. Brigatti, J P Jin
مصطلحات موضوعية: 0301 basic medicine, Male, Pathology, medicine.medical_specialty, Muscle Hypotonia, Biology, Myopathies, Nemaline, Muscle hypertrophy, 03 medical and health sciences, Mice, 0302 clinical medicine, Atrophy, Nemaline myopathy, Troponin T, Genetics, medicine, Animals, Humans, Protein Isoforms, Pathology, Molecular, Myopathy, Child, Muscle, Skeletal, Molecular Biology, Genetics (clinical), Muscle contracture, Muscle Weakness, Homozygote, Infant, Newborn, Muscle weakness, General Medicine, medicine.disease, 030104 developmental biology, Phenotype, Codon, Nonsense, Old Order Amish, Original Article, Female, medicine.symptom, Amish, 030217 neurology & neurosurgery
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d291c14cdf88ffb2ef1086937e2e0794
https://europepmc.org/articles/PMC6121192/ -
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المؤلفون: Yimei Li, John T. Gray, C H Pui, Paul Eldridge, Duangchan Suwannasaen, Wing Keung Chan, Wing Leung, Robert E. Throm, Jim Houston
المصدر: Leukemia
مصطلحات موضوعية: Cancer Research, Adoptive cell transfer, T-Lymphocytes, Antigens, CD19, Drug Resistance, Graft vs Host Disease, chemical and pharmacologic phenomena, Biology, Cell therapy, Mice, Antigen, NK-92, immune system diseases, Recurrence, hemic and lymphatic diseases, Cell Line, Tumor, Neoplasms, medicine, Animals, Humans, Leukemia, hemic and immune systems, Hematology, Histone-Lysine N-Methyltransferase, medicine.disease, Flow Cytometry, Haematopoiesis, Receptors, Antigen, Oncology, Drug Resistance, Neoplasm, Immunology, Leukocytes, Mononuclear, Myeloid-Lymphoid Leukemia Protein, Leukocyte Common Antigens, Original Article, Stem cell, Immunologic Memory, Signal Transduction
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المؤلفون: Garrett Heffner, Archana Belle, Lucy James, John T. Gray, Jennifer Ton
المصدر: Molecular Genetics and Metabolism. 123:S55-S56
مصطلحات موضوعية: biology, business.industry, Endocrinology, Diabetes and Metabolism, Disease, Gene delivery, Pharmacology, Biochemistry, Endocrinology, Alpha-glucosidase, Genetics, biology.protein, Medicine, business, Molecular Biology
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المؤلفون: Miranda Mei, Hui Meng, Chanchal Sadhu, Benedikt Schoser, John T. Gray, Lucy James, Jennifer Ton, Tim Stinchcombe, Christina Chaivorapol, Garrett Heffner, Michael W. Lawlor, Suyash Prasad
المصدر: Molecular Genetics and Metabolism. 126:S70
مصطلحات موضوعية: medicine.medical_specialty, Glycogen, Endocrinology, Diabetes and Metabolism, Genetic enhancement, Transgene, Skeletal muscle, Promoter, Biology, Biochemistry, chemistry.chemical_compound, Endocrinology, medicine.anatomical_structure, chemistry, Internal medicine, Genetics, medicine, Acid alpha-glucosidase, Vector (molecular biology), Respiratory system, Molecular Biology
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المؤلفون: John T. Gray, Perdeep K. Mehta, Michael R. Greene, Yoon-Sang Kim, Timothy D. Lockey, Brian P. Sorrentino, Paul Eldridge
المصدر: Human Gene Therapy Methods. 23:297-308
مصطلحات موضوعية: Genetic Vectors, Transplantation, Heterologous, CD34, Antigens, CD34, Biology, X-Linked Combined Immunodeficiency Diseases, Applied Microbiology and Biotechnology, Cell Line, Viral vector, Mice, Transduction (genetics), Bioreactors, Transduction, Genetic, Genetics, medicine, Animals, Humans, Myeloid Cells, Lymphocytes, Research Articles, Genetics (clinical), Pharmacology, Severe combined immunodeficiency, Lentivirus, Hematopoietic Stem Cell Transplantation, Genetic Therapy, Hematopoietic Stem Cells, medicine.disease, Virology, Molecular biology, Transplantation, Disease Models, Animal, Haematopoiesis, Cell culture, Molecular Medicine, Female, Stem cell
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5427f870d66281d2bd5787cae2780160
https://doi.org/10.1089/hgtb.2012.150