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1دورية أكاديمية
المؤلفون: Nancy Chen, David E. Ehmann, Robert Crooker, Katayoun Derakhchan, Xiaodong Fang, Brian Felice, Elizabeth J. Galbreath, Charles Glaus, Hongbo Gu, Yan Huang, Christine Li, Xing Li, Nan Liu, Kathleen Palmieri, Damir Simic, Joseph Sypek, Susan Thompson, Christopher T. Winkelmann, Vivian W. Choi
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 29, Iss , Pp 286-302 (2023)
مصطلحات موضوعية: gene therapy, AAV, MPS II, cross-correction, non-human primates, iduronate-2-sulfatase, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2
المؤلفون: Rimi Hazra, Bohong Zhang, Solomon F. Ofori-Acquah, Samit Ghosh, Matthew Crouthamel, Bethany Flage, Joseph Sypek, Sun Xiuxia, Clark Pan
المصدر: Blood. 134:74-74
مصطلحات موضوعية: medicine.medical_specialty, Respiratory distress, business.industry, Immunology, Hemopexin, Cell Biology, Hematology, Lung injury, medicine.disease, Biochemistry, Acute chest syndrome, Sickle cell anemia, Heme oxygenase, chemistry.chemical_compound, Endocrinology, chemistry, Internal medicine, medicine, business, Heme, Hemin
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::6099caa24571ca08fbaa0c0dfcbc077b
https://doi.org/10.1182/blood-2019-127198 -
3
المؤلفون: Angela W. Norton, Pranavkumar Shivakumar, Andrea Iskenderian, Kevin Holmes, Sridevi Gutta, Reena Mourya, Nazanin Navabi, Rizwana Islam, Joseph Sypek, Haojing Rong
المصدر: Gastroenterology. 156:S-1507
مصطلحات موضوعية: medicine.medical_specialty, Hepatology, Biliary atresia, business.industry, Liver fibrosis, Internal medicine, Gastroenterology, medicine, medicine.disease, business
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4
المؤلفون: Dawn A Savio, Anita R Halpern, Yuchuan Wu, Wei Li, Joseph Sypek, Elaine M Quinet
المصدر: Circulation. 118
مصطلحات موضوعية: Physiology (medical), cardiovascular system, Cardiology and Cardiovascular Medicine
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::2a27b1643f3b5972a62bb0b01423c978
https://doi.org/10.1161/circ.118.suppl_18.s_473-c -
5دورية أكاديمية
المؤلفون: Wei Li, Jianchang Li, Yuchuan Wu, Fabio Rancati, Stefania Vallese, Luca Raveglia, Junjun Wu, Rajeev Hotchandani, Nathan Fuller, Kristina Cunningham, Paul Morgan, Susan Fish, Rustem Krykbaev, Xin Xu, Steve Tam, Samuel J. Goldman, William Abraham, Cara Williams, Joseph Sypek, Tarek S. Mansour
المصدر: Journal of Medicinal Chemistry; Sep2009, Vol. 52 Issue 17, p5408-5419, 12p
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6دورية أكاديمية
المؤلفون: Wei Li, Jianchang Li, Yuchuan Wu, Junjun Wu, Rajeev Hotchandani, Kristina Cunningham, Iain McFadyen, Joel Bard, Paul Morgan, Franklin Schlerman, Xin Xu, Steve Tam, Samuel J. Goldman, Cara Williams, Joseph Sypek, Tarek S. Mansour
المصدر: Journal of Medicinal Chemistry; Apr2009, Vol. 52 Issue 7, p1799-1802, 4p