المؤلفون: Margareth C. Ozelo, Katie Wachtel, Yifeng Chen, Benjamin J. Samelson-Jones, Leslie Raffini, Katherine A. High, Margaret V. Ragni, John E.J. Rasko, Xavier M. Anguela, Lindsey A. George, Jennifer Wellman, Alexa R. Runowski, Federico Mingozzi, Maria Hazbon, Klaudia Kuranda

المصدر: Mol Ther

مصطلحات موضوعية: Male, Genetic enhancement, viruses, medicine.disease_cause, Antibodies, Viral, Factor IX, 0302 clinical medicine, Drug Discovery, Vector (molecular biology), Longitudinal Studies, Neutralizing antibody, Adeno-associated virus, 0303 health sciences, biology, Gene Transfer Techniques, Dependovirus, Middle Aged, Treatment Outcome, Liver, 030220 oncology & carcinogenesis, Hepatocellular carcinoma, Molecular Medicine, Original Article, Antibody, Signal Transduction, Adult, Genetic Vectors, Cross Reactions, Hemophilia B, Virus, 03 medical and health sciences, Young Adult, Immune system, Capsid, Genetics, medicine, Humans, Infusions, Intra-Arterial, Molecular Biology, 030304 developmental biology, Pharmacology, business.industry, Genetic Therapy, medicine.disease, Antibodies, Neutralizing, Immunology, biology.protein, Hepatocytes, business, Follow-Up Studies

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4e4ea62b5161a331b808e5546cb819c4
https://pubmed.ncbi.nlm.nih.gov/32559433

المؤلفون: Xiaosong Zhu, Jean Bennett, Chris A. Johnson, Katie Wachtel, Jean Walshire, Zi Fan Yu, Julie Pappas, Taylor Kehoe, Elliott H. Sohn, Jennifer Wellman, Vinit B. Mahajan, Bart P. Leroy, Michelle T. Weckmann, Francesca Simonelli, Okan U. Elci, Dominique Cross, Amy Tillman, J. Fraser Wright, Lindsey A. George, Kathleen A. Marshall, Julia A. Haller, Maria C. Davis, Edwin M. Stone, Janet Wittes, Laura E. Dingfield, Dina Y. Gewaily, Sarah McCague, Leslie Raffini, Katherine A. High, Albert M. Maguire, Hannah Reichert, Arlene V. Drack, Daniel C. Chung, Wanda Pfeifer, F. Parker Hudson, Stephen R. Russell

المساهمون: Russell, Stephen, Bennett, Jean, Wellman, Jennifer A, Chung, Daniel C, Yu, Zi-fan, Tillman, Amy, Wittes, Janet, Pappas, Julie, Elci, Okan, Mccague, Sarah, Cross, Dominique, Marshall, Kathleen A, Walshire, Jean, Kehoe, Taylor L, Reichert, Hannah, Davis, Maria, Raffini, Leslie, George, Lindsey A, Hudson, F. Parker, Dingfield, Laura, Zhu, Xiaosong, Haller, Julia A, Sohn, Elliott H, Mahajan, Vinit B, Pfeifer, Wanda, Weckmann, Michelle, Johnson, Chri, Gewaily, Dina, Drack, Arlene, Stone, Edwin, Wachtel, Katie, Simonelli, Francesca, Leroy, Bart P, Wright, J. Fraser, High, Katherine A, Maguire, Albert M.

المصدر: The Lancet. 390:849-860

مصطلحات موضوعية: Male, cis-trans-Isomerases, 0301 basic medicine, medicine.medical_specialty, Adolescent, Genetic Vectors, Population, Phases of clinical research, law.invention, 03 medical and health sciences, Randomized controlled trial, law, Internal medicine, Retinal Dystrophies, medicine, Humans, education, Adverse effect, education.field_of_study, business.industry, Medicine (all), Genetic Therapy, General Medicine, United States, Visual field, Clinical trial, Treatment Outcome, 030104 developmental biology, Meridian (perimetry, visual field), RPE65, Mutation, Physical therapy, Female, business

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::4f182894740f3f23311e678456a122ca
https://doi.org/10.1016/s0140-6736(17)31868-8

المؤلفون: Johannes C.M. Van der Loo, Jerome M. Teitel, Benjamin J. Samelson-Jones, Adam Cuker, Xavier M. Anguela, Marcus E. Carr, Catherine E. McGuinn, Yifeng Chen, Linda B. Couto, Adam Giermasz, Suvankar Majumdar, Katie Wachtel, Jonathan M. Ducore, Stefan Tiefenbacher, Margaret V. Ragni, J. Fraser Wright, Olga Zelenaia, Katherine A. High, Yun Liu, John E.J. Rasko, Daniel Takefman, Lisa M. Sullivan, Angela Winters, Daniel Hui, Alvin Luk, Spencer K. Sullivan, Valder R. Arruda, Lindsey A. George

المصدر: The New England journal of medicine. 377(23)

مصطلحات موضوعية: 0301 basic medicine, Adult, Male, medicine.medical_specialty, Adolescent, Genetic Vectors, Hemorrhage, Gastroenterology, Hemophilia B, Factor IX, 03 medical and health sciences, Young Adult, Internal medicine, medicine, Humans, Vector (molecular biology), Transgenes, Adverse effect, Normal range, Clotting factor, Baseline values, business.industry, Hemophilia B Gene, General Medicine, Genetic Therapy, Dependovirus, Middle Aged, 030104 developmental biology, Commentary, Specific activity, business, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::6bbb2657407ff2d3c3546fcc638e6677
https://pubmed.ncbi.nlm.nih.gov/29274719

المؤلفون: Xavier M. Anguela, Katie Wachtel, Judith Kadosh, Stacy E. Croteau, Marcus E. Carr, Lindsey A. George, Leonard A. Valentino, Matthew S. Evans, Federico Mingozzi, Linda B. Couto, Daniel Takefman, Kathleen B Reape, Daniel J. Hui, Alexa R. Runoski, Amy Macdougall, Katherine A. High, Cynthia Campbell-Baird, Marcelyne Joseney-Antoine, Ben J. Samelson-Jones, Howard Hait, Summer Tompkins, Spencer K. Sullivan, Ashlyn Eaton Bassiri, M. Elaine Eyster, Kayla Douglas, Margaret V. Ragni

المصدر: Blood. 132:487-487

مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, business.operation, business.industry, Immunology, Gene transfer, Cell Biology, Hematology, Octapharma, medicine.disease, Biochemistry, Asymptomatic, 03 medical and health sciences, Safety profile, 030104 developmental biology, Methylprednisolone, Internal medicine, Cohort, medicine, Elevated transaminases, medicine.symptom, business, Adverse effect, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::0b9ceb3979e02dffcffbb36210b302ec
https://doi.org/10.1182/blood-2018-99-115495

المؤلفون: Andres Castillo, Deborah Moorad-Doctor, Ruthie H Ratcliffe, Gregory E. Garcia, Harry Singh, Katie Wachtel

المصدر: Journal of Analytical Toxicology. 31:69-74

مصطلحات موضوعية: Pyridinium Compounds, Health, Toxicology and Mutagenesis, Guinea Pigs, Ion chromatography, Toxicology, Injections, Intramuscular, High-performance liquid chromatography, Analytical Chemistry, chemistry.chemical_compound, Drug Stability, Cations, Oximes, Blood plasma, Animals, Environmental Chemistry, Chromatography, High Pressure Liquid, Whole blood, Detection limit, Chemical Health and Safety, Chromatography, Dose-Response Relationship, Drug, Reproducibility of Results, Chromatography, Ion Exchange, chemistry, Area Under Curve, Pyridinium, Quantitative analysis (chemistry), Half-Life

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b9ce7c545849a0ad2779867985467146
https://doi.org/10.1093/jat/31.2.69

المؤلفون: Katie Wachtel, Marcus E. Carr, Katherine A. High, Lisa M. Sullivan, Spencer K. Sullivan, Adam Giermasz, Yifeng Chen, Aline M. Galvão, Linda B. Couto, Alvin Luk, J. Fraser Wright, Jerome M. Teitel, Jonathan M. Ducore, Daniel J. Hui, Adam Cuker, Xavier M. Anguela, Catherine E. McGuinn, Suvankar Majumdar, Daniel Takefman, Lindsey A. George, Teresa Urich

المصدر: Blood. 128:3-3

مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, medicine.medical_treatment, Immunology, medicine.disease_cause, Biochemistry, 03 medical and health sciences, 0302 clinical medicine, Hemophilias, Quality of life, Breakthrough bleeding, Internal medicine, Medicine, Adverse effect, Adeno-associated virus, Factor IX, business.industry, Immunosuppression, Cell Biology, Hematology, Hemarthrosis, medicine.disease, 030104 developmental biology, 030220 oncology & carcinogenesis, medicine.symptom, business, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::baa66563c186ef4b38fd1a219c80514e
https://doi.org/10.1182/blood.v128.22.3.3