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1دورية أكاديمية
المؤلفون: Rojsajjakul, Teerapat, Selvan, Nithya, De, Bishnu, Rosenberg, Jonathan B., Kaminsky, Stephen M., Sondhi, Dolan, Janki, Peter, Crystal, Ronald G., Mesaros, Clementina, Khanna, Richie, Blair, Ian A.Aff1, IDs41598024590600_cor11
المصدر: Scientific Reports. 14(1)
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2دورية أكاديمية
المؤلفون: Butala-Flores, ElizabethAff1, IDs11095023036257_cor1, Nguyen, Thien, Selvan, Nithya, Armstrong, Luke, Miller, Michelle, Kamen, Lynn, Lester, Todd, Wernyj, Roman, Khanna, Richie, McNally, Jim, Hays, Amanda
المصدر: Pharmaceutical Research: An Official Journal of the American Association of Pharmaceutical Scientists. :1-15
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3دورية أكاديمية
المؤلفون: Kishnani, Priya, Tarnopolsky, Mark, Roberts, Mark, Sivakumar, Kumarswamy, Dasouki, Majed, Dimachkie, Mazen M, Finanger, Erika, Goker-Alpan, Ozlem, Guter, Karl A, Mozaffar, Tahseen, Pervaiz, Muhammad Ali, Laforet, Pascal, Levine, Todd, Adera, Matthews, Lazauskas, Richard, Sitaraman, Sheela, Khanna, Richie, Benjamin, Elfrida, Feng, Jessie, Flanagan, John J, Barth, Jay, Barlow, Carrolee, Lockhart, David J, Valenzano, Kenneth J, Boudes, Pol, Johnson, Franklin K, Byrne, Barry
المصدر: Molecular Therapy. 25(5)
مصطلحات موضوعية: Pharmacology and Pharmaceutical Sciences, Biomedical and Clinical Sciences, Rare Diseases, Chronic Liver Disease and Cirrhosis, Digestive Diseases, Liver Disease, 5.1 Pharmaceuticals, 6.1 Pharmaceuticals, Evaluation of treatments and therapeutic interventions, Development of treatments and therapeutic interventions, 1-Deoxynojirimycin, Administration, Oral, Adult, Drug Administration Schedule, Drug Synergism, Drug Therapy, Combination, Enzyme Replacement Therapy, Female, Glycogen Storage Disease Type II, Humans, Infusions, Intravenous, Lysosomes, Male, Middle Aged, Muscle, Skeletal, Patient Safety, Treatment Outcome, alpha-Glucosidases, Pompe disease, enzyme replacement therapy, pharmacokinetics, pharmacological chaperone, Biological Sciences, Technology, Medical and Health Sciences, Biotechnology, Genetics, Clinical sciences, Medical biotechnology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/7kd7w6h0
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4دورية أكاديمية
المؤلفون: Warnock, David G, Bichet, Daniel G, Holida, Myrl, Goker-Alpan, Ozlem, Nicholls, Kathy, Thomas, Mark, Eyskens, Francois, Shankar, Suma, Adera, Mathews, Sitaraman, Sheela, Khanna, Richie, Flanagan, John J, Wustman, Brandon A, Barth, Jay, Barlow, Carrolee, Valenzano, Kenneth J, Lockhart, David J, Boudes, Pol, Johnson, Franklin K
المصدر: PLOS ONE. 10(8)
مصطلحات موضوعية: Pharmacology and Pharmaceutical Sciences, Biomedical and Clinical Sciences, Clinical Trials and Supportive Activities, Clinical Research, Neurosciences, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, 5.1 Pharmaceuticals, Development of treatments and therapeutic interventions, 1-Deoxynojirimycin, Administration, Oral, Adult, Area Under Curve, Demography, Fabry Disease, Humans, Infusion Pumps, Isoenzymes, Male, Middle Aged, Recombinant Proteins, Skin, alpha-Galactosidase, General Science & Technology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/0p1377w3
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5دورية أكاديمية
المؤلفون: Richter, Franziska, Fleming, Sheila M, Watson, Melanie, Lemesre, Vincent, Pellegrino, Lee, Ranes, Brian, Zhu, Chunni, Mortazavi, Farzad, Mulligan, Caitlin K, Sioshansi, Pedrom C, Hean, Sindalana, De La Rosa, Krystal, Khanna, Richie, Flanagan, John, Lockhart, David J, Wustman, Brandon A, Clark, Sean W, Chesselet, Marie-Françoise
المصدر: Neurotherapeutics. 11(4)
مصطلحات موضوعية: Pharmacology and Pharmaceutical Sciences, Biomedical and Clinical Sciences, Neurosciences, Parkinson's Disease, Neurodegenerative, Prevention, Brain Disorders, 5.1 Pharmaceuticals, 2.1 Biological and endogenous factors, Aetiology, Development of treatments and therapeutic interventions, Neurological, Animals, Brain, Disease Models, Animal, Dopaminergic Neurons, Humans, Imino Pyranoses, Male, Mice, Motor Activity, Parkinson Disease, Protein Aggregates, Protein Transport, Substantia Nigra, Tartrates, alpha-Synuclein, beta-Glucosidase, Parkinson's disease, Alpha-synuclein, Acid-beta-glucosidase, Mouse model, Chaperone, Motor behavior, Acid-β-glucosidase, Public Health and Health Services, Neurology & Neurosurgery, Pharmacology and pharmaceutical sciences, Biological psychology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/2pp460nv
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6دورية أكاديمية
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7دورية أكاديمية
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8دورية أكاديمية
المؤلفون: Khanna, Richie, Chang, Seon H., Andrabi, Shaida, Azam, Mohammad, Kim, Anthony, Rivera, Alicia, Brugnara, Carlo, Low, Philip S., Liu, Shih-Chun, Chishti, Athar H.
المصدر: Proceedings of the National Academy of Sciences of the United States of America, 2002 May . 99(10), 6637-6642.
URL الوصول: https://www.jstor.org/stable/3058718
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9دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
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10دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل.