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1دورية أكاديمية
المؤلفون: Anna Clua, Santiago Grijalvo, Namrata Erande, Swati Gupta, Kristina Yucius, Raimundo Gargallo, Stefania Mazzini, Muthiah Manoharan, Ramon Eritja
المصدر: Molecules, Vol 28, Iss 1, p 98 (2022)
مصطلحات موضوعية: n/a, Organic chemistry, QD241-441
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Anna Clua, Santiago Grijalvo, Namrata Erande, Swati Gupta, Kristina Yucius, Raimundo Gargallo, Stefania Mazzini, Muthiah Manoharan, Ramon Eritja
المصدر: Molecules, Vol 27, Iss 12, p 3944 (2022)
مصطلحات موضوعية: G-quadruplex, N-acetylgalactosamine, antisense, oligonucleotide conjugates, asialoglycoprotein receptor, luciferase gene, Organic chemistry, QD241-441
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Linda L. Kusner, Kristina Yucius, Manjistha Sengupta, Andrew G. Sprague, Dhruv Desai, Tuyen Nguyen, Klaus Charisse, Satya Kuchimanchi, Rajeev Kallanthottathil, Kevin Fitzgerald, Henry J. Kaminski, Anna Borodovsky
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 13, Iss , Pp 484-492 (2019)
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Tatiana I Novobrantseva, Anna Borodovsky, Jamie Wong, Boris Klebanov, Mohammad Zafari, Kristina Yucius, William Querbes, Pei Ge, Vera M Ruda, Stuart Milstein, Lauren Speciner, Rick Duncan, Scott Barros, Genc Basha, Pieter Cullis, Akin Akinc, Jessica S Donahoe, K Narayanannair Jayaprakash, Muthusamy Jayaraman, Roman L Bogorad, Kevin Love, Katie Whitehead, Chris Levins, Muthiah Manoharan, Filip K Swirski, Ralph Weissleder, Robert Langer, Daniel G Anderson, Antonin de Fougerolles, Matthias Nahrendorf, Victor Koteliansky
المصدر: Molecular Therapy: Nucleic Acids, Vol 1, Iss C (2012)
مصطلحات موضوعية: delivery, immune cell, siRNA, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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5
المؤلفون: Pachamuthu Kandasamy, Shohei Mori, Shigeo Matsuda, Namrata Erande, Dhrubajyoti Datta, Jennifer L. S. Willoughby, Nate Taneja, Jonathan O’Shea, Anna Bisbe, Rajar M. Manoharan, Kristina Yucius, Tuyen Nguyen, Ramesh Indrakanti, Swati Gupta, Jason A. Gilbert, Tim Racie, Amy Chan, Ju Liu, Renta Hutabarat, Jayaprakash K. Nair, Klaus Charisse, Martin A. Maier, Kallanthottathil G. Rajeev, Martin Egli, Muthiah Manoharan
المصدر: Journal of Medicinal Chemistry. 66:2506-2523
مصطلحات موضوعية: Drug Discovery, Molecular Medicine
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6
المؤلفون: Tuyen Nguyen, Linda L. Kusner, Kristina Yucius, Anna Borodovsky, Henry J. Kaminski, Klaus Charisse, Kevin Fitzgerald, Rajeev G. Kallanthottathil, Dhruv Desai, Manjistha Sengupta, Andrew Sprague, Satya Kuchimanchi
المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 13, Iss, Pp 484-492 (2019)مصطلحات موضوعية: 0301 basic medicine, Small interfering RNA, lcsh:QH426-470, Disease, Pharmacology, Neuromuscular junction, Article, 03 medical and health sciences, 0302 clinical medicine, RNA interference, Genetics, Medicine, Gene silencing, lcsh:QH573-671, Molecular Biology, myasthenia gravis, business.industry, lcsh:Cytology, complement pathway, medicine.disease, small-interfering RNA, Myasthenia gravis, Complement system, siRNA therapeutic, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, 030220 oncology & carcinogenesis, Concomitant, Molecular Medicine, business
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7
المؤلفون: Theo J.C. Van Berkel, Kun Qian, Muthiah Manoharan, Kallanthottathil G. Rajeev, Vasant Jadhav, Klaus Charisse, Jayaprakash K. Nair, James Butler, Tracy Zimmermann, Amy Chan, Jennifer L. S. Willoughby, Alfica Sehgal, Kristina Yucius, Tim Racie, Tuyen Nguyen, Svetlana Shulga-Morskaya, Martin Maier
المصدر: Molecular Therapy
مصطلحات موضوعية: Liver Cirrhosis, 0301 basic medicine, Acetylgalactosamine, Receptor expression, Drug Evaluation, Preclinical, Asialoglycoprotein Receptor, GalNAc-siRNA, Mice, 03 medical and health sciences, Drug Delivery Systems, RNA interference, Pharmacokinetics, Drug Discovery, Genetics, Animals, Humans, Gene Silencing, RNA, Small Interfering, Receptor, Molecular Biology, Mice, Knockout, Pharmacology, Drug Carriers, Chemistry, Ligand (biochemistry), Cell biology, carbohydrates (lipids), Disease Models, Animal, Protein Subunits, 030104 developmental biology, Gene Expression Regulation, Targeted drug delivery, Biochemistry, Hepatocytes, Molecular Medicine, Female, Original Article, lipids (amino acids, peptides, and proteins), Asialoglycoprotein receptor, Function (biology), Conjugate
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b0582e63f65ca272e916c044b99cff3a
https://doi.org/10.1016/j.ymthe.2017.08.019 -
8
المؤلفون: Kristina Yucius, Stuart Milstein, Nate Taneja, Tuyen Nguyen, Jonathan O'Shea, Anna Borodovsky, Svetlana Shulga-Morskaya, Muthusamy Jayaraman, Kallanthottathil G. Rajeev, Klaus Charisse, Kevin Fitzgerald, Abigail Liebow, William Querbes, Jennifer L. S. Willoughby, Martin Maier, Muthiah Manoharan, Jayaprakash K. Nair
المصدر: ChemBioChem. 16:903-908
مصطلحات موضوعية: Small interfering RNA, Acetylgalactosamine, Stereochemistry, Biochemistry, N-Acetylgalactosamine, Mice, chemistry.chemical_compound, parasitic diseases, Animals, Prealbumin, Gene silencing, Gene Silencing, RNA, Small Interfering, Molecular Biology, Drug Carriers, Chemistry, Oligonucleotide, Organic Chemistry, Ligand (biochemistry), carbohydrates (lipids), Hepatocytes, Molecular Medicine, lipids (amino acids, peptides, and proteins), Asialoglycoprotein receptor, Linker, Conjugate
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9
المؤلفون: Chang G. Peng, Pachamuthu Kandasamy, Kristina Yucius, Stuart Milstein, Rajar M. Manoharan, William Querbes, Kristofer Keiser, Muthiah Manoharan, Martin Maier, Jayaprakash K. Nair, Tuyen Nguyen, Abigail Liebow, Alexander V Kel'in, Jennifer L. S. Willoughby, Klaus Charisse, Shigeo Matsuda, Kallanthottathil G. Rajeev, Philip Kretschmer
المصدر: ACS Chemical Biology. 10:1181-1187
مصطلحات موضوعية: Small interfering RNA, Acetylgalactosamine, Oligonucleotide, RNA, Nucleosides, General Medicine, Biology, Biochemistry, RNAi Therapeutics, Mice, Inbred C57BL, carbohydrates (lipids), Mice, In vivo, RNA interference, parasitic diseases, Hepatocytes, Animals, Molecular Medicine, Gene silencing, lipids (amino acids, peptides, and proteins), Asialoglycoprotein receptor, Gene Silencing, RNA, Small Interfering
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10
المؤلفون: Dhruv Desai, Paul Gedman, Zhizhuang Joe Zhao, Ophelia Rogers, Anna Borodovsky, Kellie D'Angelo, Wendell P Davis, Rohan Degaonkar, Donna M. Williams, Alison R. Moliterno, Kristina Yucius, Jerry L. Spivak
المصدر: Blood. 132:4329-4329
مصطلحات موضوعية: 0301 basic medicine, Thrombocytosis, Immunology, Cell Biology, Hematology, Biology, medicine.disease, Biochemistry, 03 medical and health sciences, Haematopoiesis, Leukemia, 030104 developmental biology, medicine.anatomical_structure, Megakaryocyte, medicine, Cancer research, Platelet, Bone marrow, Progenitor cell, Thrombopoietin
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::b7b9ce8161963c0aaacb941f214dd556
https://doi.org/10.1182/blood-2018-99-117142