المؤلفون: Christian Brendel, Olivier Negre, Michael Rothe, Swaroopa Guda, Geoff Parsons, Chad Harris, Meaghan McGuinness, Daniela Abriss, Alla Tsytsykova, Denise Klatt, Martin Bentler, Danilo Pellin, Lauryn Christiansen, Axel Schambach, John Manis, Helene Trebeden-Negre, Melissa Bonner, Erica Esrick, Gabor Veres, Myriam Armant, David A. Williams

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 589-600 (2020)

مصطلحات موضوعية: Sickle cell disease, HbS, hemoglobinopathies, gene therapy, lentiviral vector, BCL11A, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050120300450; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/7ebf28bc3d664f328d3cea76508fe211

المؤلفون: Gretchen Lewis, Lauryn Christiansen, Jessica McKenzie, Min Luo, Eli Pasackow, Yegor Smurnyy, Sean Harrington, Philip Gregory, Gabor Veres, Olivier Negre, Melissa Bonner

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 9, Iss , Pp 313-322 (2018)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050118300391; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/67f0223fe78441699cfcbacd86785e3a

المؤلفون: Olivier Negre, Swaroopa Guda, Christian Brendel, Chad E. Harris, Martin Bentler, Myriam Armant, Melissa Bonner, Erica B. Esrick, John P. Manis, Helene Trebeden-Negre, Axel Schambach, Alla V. Tsytsykova, Danilo Pellin, Michael Rothe, Lauryn Christiansen, Denise Klatt, David A. Williams, Meaghan McGuinness, Daniela Abriss, Geoff Parsons, Gabor Istvan Veres

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 589-600 (2020)
Molecular Therapy. Methods & Clinical Development

مصطلحات موضوعية: 0301 basic medicine, fetal hemoglobin, lcsh:QH426-470, Genetic enhancement, Cell, CD34, Biology, Article, Viral vector, Small hairpin RNA, 03 medical and health sciences, 0302 clinical medicine, RNA interference, BCL11A, Fetal hemoglobin, Genetics, medicine, shRNAmiR, lcsh:QH573-671, hemoglobinopathies, Molecular Biology, Gene knockdown, lcsh:Cytology, Sickle cell disease, lentiviral vector, gene therapy, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, HbS, 030220 oncology & carcinogenesis, hemoglobin switch, Cancer research, Molecular Medicine

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::fb8fc0356964dd1fbe99f38977e8a66a
http://www.sciencedirect.com/science/article/pii/S2329050120300450

المؤلفون: Olivier Negre, Jessica McKenzie, Melissa Bonner, Sean Harrington, Yegor Smurnyy, Philip A. Gregory, Lauryn Christiansen, Gabor Istvan Veres, Min Luo, Gretchen Lewis, Eli Pasackow

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 9, Iss, Pp 313-322 (2018)
Molecular Therapy. Methods & Clinical Development

مصطلحات موضوعية: 0301 basic medicine, lcsh:QH426-470, Genetic enhancement, CD34, Article, Viral vector, 03 medical and health sciences, Transduction (genetics), Genetics, medicine, Staurosporine, Progenitor cell, lcsh:QH573-671, Molecular Biology, lentiviral, Chemistry, lcsh:Cytology, transduction, Cell biology, Haematopoiesis, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, HSPC, Molecular Medicine, Bone marrow, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5b41b0595a23dbdf08ec421e71c0725f
http://www.sciencedirect.com/science/article/pii/S2329050118300391

المؤلفون: Holly Horton, Lauryn Christiansen, Amanda Hamel, Olivia Garijo, Bruce E. Torbett, Philip D. Gregory, Garrett C. Heffner, Gretchen Lewis, Yegor Smurnyy, Dakota Campbell, Melissa Bonner, Wenliang Zhang, Gabor Istvan Veres, Seema Shaw, Francis J. Pierciey, Kendrick A. Goss, Mitchell Finer

المصدر: Molecular Therapy

مصطلحات موضوعية: 0301 basic medicine, Genetic enhancement, CD34, Antigens, CD34, Transduction (genetics), Mice, Transduction, Genetic, Drug Discovery, Transgenes, Gene Transfer Techniques, Hematopoietic stem cell, transduction, gene therapy, Cell biology, Globins, Haematopoiesis, medicine.anatomical_structure, Molecular Medicine, Original Article, Genetic Vectors, Transplantation, Heterologous, Anemia, Sickle Cell, Biology, Dinoprostone, Viral vector, Cell Line, 03 medical and health sciences, vector copy number, Genetics, medicine, hemoglobinopathy, Animals, Humans, Progenitor cell, Molecular Biology, Gene Library, Pharmacology, Severe combined immunodeficiency, prostaglandin E2, lentiviral vector, Lentivirus, beta-Thalassemia, Genetic Therapy, Virus Internalization, medicine.disease, Hematopoietic Stem Cells, 030104 developmental biology, Immunology, Leukocyte Common Antigens, hematopoietic stem cell

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::25b0e354eb4ffad2bdd82662970f9a9c
http://europepmc.org/articles/PMC5763075

المؤلفون: Marina Cavazzana, Yves Beuzard, Leila Maouche, Gabor Istvan Veres, Olivier Negre, Emmanuel Payen, Philippe Leboulch, Manfred Schmidt, Beatrix Gillet-Legrand, Anais Paulard, Byoung Y. Ryu, Robert H. Kutner, Annette Deichmann, Mitchell Finer, Christophe Joubert, Francis J. Pierciey, Christof von Kalle, Cynthia C. Bartholomae, Raffaele Fronza, Lauryn Christiansen, Edouard de Dreuzy, Michael Rothe, Celine Courne, Maria Denaro

المصدر: Current Gene Therapy. 15:64-81

مصطلحات موضوعية: medicine.medical_treatment, Genetic enhancement, Thalassemia, CD34, Beta thalassemia, Hematopoietic stem cell transplantation, Biology, medicine.disease, Viral vector, medicine.anatomical_structure, In vivo, Drug Discovery, Immunology, Genetics, medicine, Cancer research, Molecular Medicine, Bone marrow, Molecular Biology, Genetics (clinical)

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::ffe2176935a083d600347aa8833f6f00
https://doi.org/10.2174/1566523214666141127095336

المؤلفون: David R. Williams, Olivier Negre, Erica B. Esrick, Sarah Nikiforow, Christian Brendel, Shanna Richard, Daniela Abriss, Jerome Ritz, Myriam Armant, Maureen Achebe, John P. Manis, Stephen Braunewell, Lauryn Christiansen, Matthew M. Heeney, Marioara F. Ciuculescu, Helene Negre, Heather Daley, Leslie Lehmann, Alessandra Biffi, Renee Maxwell, Stephanie Patriarca, Brenda Mackinnon, Colleen Dansereau

المصدر: Blood. 132:1023-1023

مصطلحات موضوعية: 0301 basic medicine, education.field_of_study, Neutrophil Engraftment, business.industry, Plerixafor, Immunology, Population, Cell Biology, Hematology, medicine.disease, Biochemistry, Sickle cell anemia, Andrology, 03 medical and health sciences, Haematopoiesis, 030104 developmental biology, Fetal hemoglobin, Bluebird Bio, Medicine, Stem cell, business, education, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::da743e43882d46ca58e635b263536838
https://doi.org/10.1182/blood-2018-99-116733

المؤلفون: Yegor Smurnyy, Kendrick A. Goss, Philip A. Gregory, Dakota Campbell, Byoung Y. Ryu, Olivier Negre, Seema Shah, Gretchen Lewis, Holly M. Horton, F. John Pierciey, Lauryn Christiansen, Amanda Hamel, Mitchell Finer, Christopher J. Horvath, Melissa Bonner, Wen Zhang, Gabor Istvan Veres, Garrett C. Heffner

المصدر: Molecular Therapy. 24:S89-S90

مصطلحات موضوعية: 0301 basic medicine, Pharmacology, CD34, Hematopoietic stem cell, Biology, CD38, Molecular biology, Viral vector, Cell biology, 03 medical and health sciences, Haematopoiesis, Transduction (genetics), 030104 developmental biology, medicine.anatomical_structure, Drug Discovery, Genetics, medicine, Molecular Medicine, Progenitor cell, Stem cell, Molecular Biology

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::056edb3e27e49acd3e27becb5a473497
https://doi.org/10.1016/s1525-0016(16)33038-6

المؤلفون: Gretchen Lewis, Philip A. Gregory, Lauryn Christiansen, Seema Shah, Olivier Negre, Melissa Bonner, Dakota Campbell, Amanda Hamel, Gabor Istvan Veres, Holly M. Horton, Christopher Tipper

المصدر: Molecular Therapy. 24:S86-S87

مصطلحات موضوعية: Pharmacology, Genetic enhancement, CD34, Biology, Molecular biology, Viral vector, Haematopoiesis, Transduction (genetics), medicine.anatomical_structure, Drug Discovery, Genetics, medicine, Molecular Medicine, Staurosporine, Bone marrow, Progenitor cell, Molecular Biology, medicine.drug

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::2d629e4fcd0f990ded2e32cdfadce523
https://doi.org/10.1016/s1525-0016(16)33030-1