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1دورية أكاديمية
المؤلفون: Lewis E. Fry, Robert E. MacLaren
المصدر: Genes, Vol 14, Iss 12, p 2160 (2023)
وصف الملف: electronic resource
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2دورية أكاديمية
المصدر: International Journal of Molecular Sciences, Vol 21, Iss 7, p 2329 (2020)
مصطلحات موضوعية: CRISPR interference, CRISPRi, CRISPR/Cas9, RNAi, knock-down, gene therapy, Biology (General), QH301-705.5, Chemistry, QD1-999
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Lewis E. Fry, Caroline F. Peddle, Alun R. Barnard, Michelle E. McClements, Robert E. MacLaren
المصدر: International Journal of Molecular Sciences, Vol 21, Iss 3, p 777 (2020)
مصطلحات موضوعية: inherited retinal degeneration, retinitis pigmentosa, retinal disease, rna editing, adar, crispr, gene therapy, gene editing, base editing, genome engineering, Biology (General), QH301-705.5, Chemistry, QD1-999
وصف الملف: electronic resource
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4
المؤلفون: Robert E MacLaren, Ariel Kantor, Michelle E. McClements, Lewis E Fry, Kanmin Xue, Ruofan Connie Han
المصدر: Expert opinion on orphan drugs
مصطلحات موضوعية: Retinal degeneration, Genetic enhancement, Article, Choroideremia, 03 medical and health sciences, 0302 clinical medicine, Gene replacement, nonsense suppression, medicine, CRISPR, Pharmacology (medical), Pharmacology, Toxicology and Pharmaceutics (miscellaneous), Gene, business.industry, REP1, Health Policy, AAV, medicine.disease, gene therapy, eye diseases, Cell biology, 030220 oncology & carcinogenesis, Rab, antisense oligonucleotides, CHM, business, 030217 neurology & neurosurgery, Intracellular
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5
المؤلفون: Satheesh Kumar, Lewis E. Fry, Jiang-Hui Wang, Keith R. Martin, Alex W. Hewitt, Fred K. Chen, Guei-Sheung Liu
المصدر: Progress in Retinal and Eye Research. 92:101110
مصطلحات موضوعية: Ophthalmology, Sensory Systems
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6
المؤلفون: Lewis E Fry, Daniel Chiu, Thomas L Edwards, John R Rocke, Jonathan Yeoh, William K Atkins, Jack X. Kane, Rohan W Essex MBiostat, Amy M Sheridan, David Fabinyi, Edward Roufail, Myra B McGuinness, Penelope J Allen
المصدر: Ophthalmology. 127:1429-1431
مصطلحات موضوعية: medicine.medical_specialty, genetic structures, medicine.medical_treatment, Intraocular lens, Prosthesis Design, Refraction, Ocular, 03 medical and health sciences, Fixation (surgical), Ocular physiology, 0302 clinical medicine, Lens Implantation, Intraocular, Ophthalmology, medicine, Humans, Prosthesis design, 030304 developmental biology, Haptic technology, Lenses, Intraocular, 0303 health sciences, business.industry, Suture Techniques, Refractive Errors, Refraction, eye diseases, Intraocular lenses, 030221 ophthalmology & optometry, sense organs, business, Sclera
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7
المؤلفون: Robert E MacLaren, Ariel Kantor, Lewis E Fry, Kanmin Xue, Ahmed M. Salman, Caroline F Peddle, Jasmina Cehajic-Kapetanovic, Michelle E. McClements
المصدر: Progress in Molecular Biology and Translational Science ISBN: 9780323853019
مصطلحات موضوعية: 0301 basic medicine, Genetic enhancement, Translational medicine, Retinal, Disease, Computational biology, Biology, Genome engineering, Novel gene, 03 medical and health sciences, chemistry.chemical_compound, 030104 developmental biology, 0302 clinical medicine, chemistry, CRISPR, 030217 neurology & neurosurgery
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::5ee8a6ce59a41c330d4e9f44db249dcb
https://doi.org/10.1016/bs.pmbts.2021.01.024 -
8Promoter Orientation within an AAV-CRISPR Vector Affects Cas9 Expression and Gene Editing Efficiency
المؤلفون: Michelle E. McClements, Alun R. Barnard, Caroline F Peddle, Marta Stevanovic, Lewis E Fry, Robert E MacLaren
المصدر: CRISPR J
مصطلحات موضوعية: Gene Editing, Staphylococcus aureus, Cas9, Transgene, viruses, Genetic Vectors, Promoter, Biology, Dependovirus, Cell biology, Transduction (genetics), Genome editing, Transcription (biology), CRISPR-Associated Protein 9, Genetics, CRISPR, Clustered Regularly Interspaced Short Palindromic Repeats, Guide RNA, CRISPR-Cas Systems, Promoter Regions, Genetic, Research Articles, Biotechnology, RNA, Guide, Kinetoplastida
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::eaded0a3b8340efb482c6e9753adac33
https://europepmc.org/articles/PMC7469699/ -
9
المصدر: International Journal of Molecular Sciences
International Journal of Molecular Sciences, Vol 21, Iss 2329, p 2329 (2020)مصطلحات موضوعية: Transcription, Genetic, knock-down, Genetic enhancement, Induced Pluripotent Stem Cells, Gene Expression, Computational biology, Review, Biology, Catalysis, lcsh:Chemistry, Inorganic Chemistry, dCas9, Retinal Diseases, RNA interference, transcriptional repression, Gene silencing, CRISPR, Animals, Humans, Clustered Regularly Interspaced Short Palindromic Repeats, Gene Silencing, Physical and Theoretical Chemistry, lcsh:QH301-705.5, Molecular Biology, Gene, CRISPR interference, CRISPR/Cas9, Spectroscopy, Alleles, Cas9, KRAB, Organic Chemistry, CRISPRi, General Medicine, Genetic Therapy, gene therapy, Computer Science Applications, Transplantation, lcsh:Biology (General), lcsh:QD1-999, Gene Knockdown Techniques, RNAi, RNA Interference, retinal disease, CRISPR-Cas Systems, RNA, Guide, Kinetoplastida
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10
المؤلفون: Peter van Wijngaarden, Steven Petrou, Flora Hui, Eamonn T Fahy, Lewis E Fry, Jessica Tang, Vicki Chrysostomou, Jonathan G Crowston
المصدر: Progress in Retinal and Eye Research. 65:77-92
مصطلحات موضوعية: Retinal Ganglion Cells, Intraocular pressure, medicine.medical_specialty, genetic structures, Open angle glaucoma, Glaucoma, Neuroprotection, 03 medical and health sciences, 0302 clinical medicine, Ophthalmology, Optic Nerve Diseases, medicine, Animals, Humans, Intraocular Pressure, Coma, Retina, Neuronal Plasticity, business.industry, Recovery of Function, medicine.disease, eye diseases, Sensory Systems, Disease Models, Animal, medicine.anatomical_structure, Retinal ganglion cell, 030221 ophthalmology & optometry, Optic nerve, sense organs, medicine.symptom, business, 030217 neurology & neurosurgery