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1دورية أكاديمية
المؤلفون: Laura J. Smith, Lindsay A. Schulman, Samantha Smith, Laura Van Lieshout, Carmen M. Barnes, Liana Behmoiras, Meghan Scarpitti, Monicah Kivaa, Khanh L. Duong, Ludo O. Benard, Jeff L. Ellsworth, Nancy Avila, Deiby Faulkner, April Hayes, Jason Lotterhand, Jose Israel Rivas, Arnold V. Sengooba, Alec Tzianabos, Albert B. Seymour, Omar L. Francone
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 224-238 (2022)
مصطلحات موضوعية: gene therapy, adeno-associated virus, AAV, tropism/biodistribution, glycan binding, structure-function relationship, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2
المؤلفون: Tania Seabrook, Kruti Patel, Laura J. Smith, Thia St-Martin, Liana Behmoiras, Monicah Kivaa, Katherine Gall, Meghan Scarpatti, Lindsay Schulman, Victor Zhivich, Minglun Wang, Daisy Huynh, Jeffrey Ellsworth, Jingyan Zhao, Shiva Krupa, Omar Francone, Albert Seymour, Jacinthe Gingras
المصدر: Molecular Genetics and Metabolism. 135:S110
مصطلحات موضوعية: Endocrinology, Endocrinology, Diabetes and Metabolism, Genetics, Molecular Biology, Biochemistry
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3
المؤلفون: Victor Zhivivh, Nancy Avila, Jingyan Zhao, Omar L. Francone, Jacinthe Gingras, Kruti Patel, Albert B. Seymour, Monicah Kivaa, Liana Behmoiras, Tania A. Seabrook, Laura Smith, Steve Woodcock, Alec Tzianabos, Arnold Sengooba, Lindsay Schulman, Deiby Faulkner, Serena Nicole Dollive, Jennifer Newman, Yvonne White, Sean Smith
المصدر: Molecular Genetics and Metabolism. 132:S147
مصطلحات موضوعية: Endocrinology, business.industry, Endocrinology, Diabetes and Metabolism, Genetic enhancement, Immunology, Genetics, medicine, Hunter syndrome, Mucopolysaccharidosis type II, medicine.disease, business, Molecular Biology, Biochemistry
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4HMI-203: Investigational gene therapy for mucopolysaccharidosis type II (MPS II), or Hunter syndrome
المؤلفون: Albert B. Seymour, Monicah Kivaa, Liana Behmoiras, Laura Smith, Lindsay Schulman, Sean Smith, Serena Nicole Dollive, Kruti Patel, Deiby Faulkner, Nancy Avila, Victor Zhivich, Omar L. Francone, Yvonne White, Alec Tzianabos, Arnold Sengooba, Tania A. Seabrook, Jenn Newman, Jacinthe Gingras, Steve Woodcock, Jingyan Zhao
المصدر: Molecular Genetics and Metabolism. 132:S82
مصطلحات موضوعية: Oncology, medicine.medical_specialty, business.industry, Endocrinology, Diabetes and Metabolism, Hunter syndrome, INVESTIGATIONAL GENE THERAPY, medicine.disease, Biochemistry, Endocrinology, Internal medicine, Genetics, medicine, Mucopolysaccharidosis type II, business, Molecular Biology
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5
المؤلفون: Michael Mercaldi, Thia St-Martin, Jennifer Newman, Tania A. Seabrook, Albert B. Seymour, Liana Behmoiras, Nancy Avila, Katie Gall, Teresa Leah Wright, Israel Rivas, Jason Lotterhand, Omar L. Francone, Shiva Krupa, Jacinthe Gingras
المصدر: Molecular Genetics and Metabolism. 132:S43
مصطلحات موضوعية: Metachromatic leukodystrophy, Pathology, medicine.medical_specialty, Endocrinology, business.industry, Endocrinology, Diabetes and Metabolism, Genetics, medicine, medicine.disease, business, Molecular Biology, Biochemistry, Gene