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1دورية أكاديمية
المؤلفون: Koeberl, Dwight, Schulze, Andreas, Sondheimer, Neal, Lipshutz, Gerald S., Geberhiwot, Tarekegn, Li, Lerong, Saini, Rajnish, Luo, Junxiang, Sikirica, Vanja, Jin, Ling, Liang, Min, Leuchars, Mary, Grunewald, StephanieAff6, IDs41586024072667_cor13
المصدر: Nature: International weekly journal of science. 628(8009):872-877
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2دورية أكاديمية
المؤلفون: Prasad, Suyash, Dimmock, David P, Greenberg, Benjamin, Walia, Jagdeep S, Sadhu, Chanchal, Tavakkoli, Fatemeh, Lipshutz, Gerald S
المصدر: Human Gene Therapy. 33(23-24)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Immunology, Neurosciences, Gene Therapy, Biotechnology, Genetics, Rare Diseases, Prevention, 5.2 Cellular and gene therapies, Development of treatments and therapeutic interventions, Humans, Dependovirus, Genetic Vectors, Genetic Therapy, Immunity, Humoral, Immunosuppressive Agents, Central Nervous System Diseases, CNS, adaptive immunity, adeno-associated virus, gene therapy, immunosuppression, innate immunity, Clinical Sciences, Medical biotechnology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/7b42k4zq
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3دورية أكاديمية
المؤلفون: Koeberl, Dwight, Schulze, Andreas, Sondheimer, Neal, Lipshutz, Gerald S., Geberhiwot, Tarekegn, Li, Lerong, Saini, Rajnish, Luo, Junxiang, Sikirica, Vanja, Jin, Ling, Liang, Min, Leuchars, Mary, Grunewald, StephanieAff6, IDs4158602407646z_cor13
المصدر: Nature: International weekly journal of science. 630(8017):E13-E13
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4دورية أكاديميةAuthor Correction: Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia
المؤلفون: Koeberl, Dwight, Schulze, Andreas, Sondheimer, Neal, Lipshutz, Gerald S., Geberhiwot, Tarekegn, Li, Lerong, Saini, Rajnish, Luo, Junxiang, Sikirica, Vanja, Jin, Ling, Liang, Min, Leuchars, Mary, Grunewald, StephanieAff6, IDs41586024074130_cor13
المصدر: Nature: International weekly journal of science. 629(8011):E10-E10
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5دورية أكاديمية
المؤلفون: Lum, Erik L., Pirzadeh, Afshin, Datta, Nakul, Lipshutz, Gerald S., McGonigle, Andrea M., Hamiduzzaman, Anum, Bjelajac, Natalie, Hale-Durbin, Bethany, Bunnapradist, Suphamai
المصدر: In Kidney Medicine July 2024 6(7)
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6دورية أكاديمية
المؤلفون: Khoja, Suhail, Lambert, Jenna, Nitzahn, Matthew, Eliav, Adam, Zhang, YuChen, Tamboline, Mikayla, Le, Colleen T, Nasser, Eram, Li, Yunfeng, Patel, Puja, Zhuravka, Irina, Lueptow, Lindsay M, Tkachyova, Ilona, Xu, Shili, Nissim, Itzhak, Schulze, Andreas, Lipshutz, Gerald S
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Genetics, Biotechnology, Nutrition, Neurosciences, Brain Disorders, Intellectual and Developmental Disabilities (IDD), AAV, creatine, gene therapy, guanidinoacetate, guanidinoacetate methyltransferase deficiency, Medical biotechnology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/9t36r7q8
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7دورية أكاديمية
المؤلفون: Boonpheng, Boonphiphop, Zuckerman, Jonathan E, Lipshutz, Gerald S, Danovitch, Gabriel M, Phelps, Angela, Pena, Michele, Yabu, Julie M
المصدر: BMC Nephrology. 22(1)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Autoimmune Disease, Diabetes, Kidney Disease, Clinical Research, Transplantation, Renal and urogenital, Metabolic and endocrine, Aged, Blood Glucose, Diabetes Mellitus, Type 1, Diabetic Nephropathies, Humans, Kidney Transplantation, Male, Nephrotic Syndrome, Pancreas Transplantation, Postoperative Complications, Reference Values, Sclerosis, Kidney-pancreas transplant, Diabetic nephropathy, Mesangial sclerosis, Case report, Urology & Nephrology, Clinical sciences, Health services and systems, Nursing
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/02b5x24c
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8دورية أكاديمية
المؤلفون: Schaenman, Joanna, Ahn, Richard, Lee, Christine, Hale-Durbin, Bethany, Abdalla, Basmah, Danovitch, Gabriel, Huynh, Alina, Laviolette, Robert, Shigri, Ahson, Bunnapradist, Suphamai, Kendrick, Elizabeth, Lipshutz, Gerald S., Pham, Phuong-Thu, Lum, Erik L., Yabu, Julie M., Seligman, Ben, Goldwater, Deena
المصدر: In Transplantation Proceedings December 2023 55(10):2372-2377
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9دورية أكاديمية
المؤلفون: Nitzahn, Matthew, Lipshutz, Gerald S
المصدر: Molecular Genetics and Metabolism. 131(3)
مصطلحات موضوعية: Biochemistry and Cell Biology, Biomedical and Clinical Sciences, Biological Sciences, Nutrition, Digestive Diseases, Good Health and Well Being, Ammonia, Carbamoyl-Phosphate Synthase (Ammonia), Carbamoyl-Phosphate Synthase I Deficiency Disease, Homeostasis, Humans, Urea, Urea Cycle Disorders, Inborn, Clinical Sciences, Genetics & Heredity, Genetics, Clinical sciences
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/1pf0r3zq
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10دورية أكاديمية
المؤلفون: Nitzahn, Matthew, Allegri, Gabriella, Khoja, Suhail, Truong, Brian, Makris, Georgios, Häberle, Johannes, Lipshutz, Gerald S
المصدر: Molecular Therapy. 28(7)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Rare Diseases, Digestive Diseases, Gene Therapy, Neurosciences, Brain Disorders, Liver Disease, Nutrition, Genetics, Development of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Ammonia, Animals, Carbamoyl-Phosphate Synthase (Ammonia), Carbamoyl-Phosphate Synthase I Deficiency Disease, DNA Packaging, Dependovirus, Disease Models, Animal, Female, Genetic Therapy, Genetic Vectors, Humans, Mice, Proof of Concept Study, Urea, adeno-associated virus, carbamoyl phosphate synthetase deficiency, gene therapy, hyperammonemia, split AAV, urea cycle disorder, ureagenesis, Biological Sciences, Technology, Medical and Health Sciences, Biotechnology, Clinical sciences, Medical biotechnology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/0tc4j8kr