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1
المؤلفون: Christian F. Meyer, Bart A. Nijmeijer, Valerie Ferreira, Martin de Haan, Margit H. Lampen, Anna Majowicz, Marco Tangelder, Lisa Spronck, Harald Petry, Sander J. H. van Deventer
المصدر: Molecular Therapy. Methods & Clinical Development
مصطلحات موضوعية: 0301 basic medicine, Genetic enhancement, Article, Virus, 03 medical and health sciences, 0302 clinical medicine, hFIX, hemophilia, Genetics, medicine, NABs, Molecular Biology, Factor IX, biology, business.industry, FIX, AAV, gene therapy, Clinical trial, Titer, 030104 developmental biology, 030220 oncology & carcinogenesis, Immunology, biology.protein, Molecular Medicine, anti-AAV NABs, Antibody, business, medicine.drug
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2
المؤلفون: Esperanza Lopez-Franco, Manfred G. Schmidt, Christine Käppel, Christof von Kalle, Irene Gil-Farina, Harald Petry, Gloria González-Aseguinolaza, Jesús Prieto, Lisa Spronck, Stefan Wilkening, Maria Astrid Paneda
المصدر: Molecular Therapy. 23
مصطلحات موضوعية: Pharmacology, viruses, Transgene, Genetic enhancement, Biology, Genome, Virology, law.invention, Viral vector, law, Drug Discovery, Recombinant DNA, Genetics, Molecular Medicine, Multiplex, Vector (molecular biology), Primer (molecular biology), Molecular Biology
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3
المؤلفون: Cynthia Brouwers, Pavlina Konstantinova, Nicole Déglon, Martin de Haan, Charles Richard, Krystof S. Bankiewicz, Bas Blits, Melvin M. Evers, Lisa Spronck, Harald Petry, Jana Miniarikova, Jan Motlik, Amber L. Southwell
المصدر: Journal of Neurology, Neurosurgery & Psychiatry. 87:A91.2-A91
مصطلحات موضوعية: Huntingtin, Genetic enhancement, Transgene, Biology, medicine.disease, Viral vector, Psychiatry and Mental health, nervous system, Huntington's disease, mental disorders, microRNA, Cancer research, medicine, Gene silencing, Surgery, Neurology (clinical), Trinucleotide repeat expansion
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4
المؤلفون: Ana Gloria Gil Royo, María del Mar Municio, Harald Petry, Astrid Pañeda Rodríguez, María Eugenia Cornet, Gloria González-Aseguinolaza, Ismael Aizpun, Marc Sonnemans, Tracy Freeman, Florence Salmon, Lisa Spronck
المصدر: Toxicology Letters. 221:S213-S214
مصطلحات موضوعية: Physics, Transmission (telecommunications), General Medicine, Toxicology, Cell biology
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5
المؤلفون: Florence Salmon, Harald Petry, Lisa Spronck, Jørgen Holm Petersen, Corina Van Der Kruijssen, Bart A. Nijmeijer
المصدر: Blood. 124:4800-4800
مصطلحات موضوعية: Clotting factor, biology, Transgene, Immunology, Cell Biology, Hematology, medicine.disease_cause, Biochemistry, Virus, Andrology, Real-time polymerase chain reaction, Immune system, biology.protein, medicine, Vector (molecular biology), Antibody, Adeno-associated virus
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::56cdc25614741eb67a4f2df3d3e5a638
https://doi.org/10.1182/blood.v124.21.4800.4800 -
6
المؤلفون: Arie Van Oorschot, Jaap Twisk, Stuart G. Beattie, Lisa Spronck Florence Salmon, Marc Sonnemans, Harald Petry, Hans Preusting, Bart A. Nijmeijer
المصدر: Toxicology Letters. 221:S60
مصطلحات موضوعية: Clotting factor, law, Recombinant DNA, General Medicine, Computational biology, Vector (molecular biology), Biology, Toxicology, Virology, Gene, Production system, law.invention
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7دورية أكاديمية
المؤلفون: Nijmeijer, Bart A., Petry, Harald, Sonnemans, Marc A., Beattie, Stuart G., Salmon, Lisa Spronck Florence, Preusting, Hans, Van Oorschot, Arie, Twisk, Jaap
المصدر: In Toxicology Letters 28 August 2013 221 Supplement:S60-S60