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المؤلفون: Sunita Goyal, John Tisdale, Manfred Schmidt, Julie Kanter, Jennifer Jaroscak, Dustin Whitney, Hans Bitter, Philip D. Gregory, Geoffrey Parsons, Marianna Foos, Ashish Yeri, Maple Gioia, Sarah B. Voytek, Alex Miller, Jessie Lynch, Richard A. Colvin, Melissa Bonner
المصدر: New England Journal of Medicine. 386:138-147
مصطلحات موضوعية: Adult, Carcinogenesis, Sequence Analysis, RNA, Genetic Vectors, Lentivirus, Hematopoietic Stem Cell Transplantation, Gene Expression, Anemia, Sickle Cell, Genetic Therapy, beta-Globins, General Medicine, Transplantation, Autologous, Leukemia, Myeloid, Acute, Risk Factors, Humans, Female, Transgenes
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المؤلفون: Olivia Finney, Eric Alonzo, Pingping Mao, Jesus G. Berdeja, Sneha Bhadoriya, Melissa Alsina, Gregory Hopkins, Dipen Sangurdekar, Sebastian Hymson, Nathan Martin, Alison Timm, Shannon Grande, Ashish Yeri, Marianna Foos, Chetanya Pandya, Monica Massaro, Nina Shah, Kevin M. Friedman, Fabio Petrocca, Shari Kaiser, Stephanie Hintzen, Noopur Raje, Tiffany Hu, Hans Bitter, Maple Gioia, Ron Hause
المصدر: Blood. 136:3-4
مصطلحات موضوعية: High peak, biology, Business administration, Immunology, Cell Biology, Hematology, biology.organism_classification, Biochemistry, Clinical study, Kite Pharma, Bluebird Bio, Drug product, CAR T-cell therapy, Business, Bluebird, Clinical evaluation
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::34687fd0824f4c97e9a3ab29e6832b64
https://doi.org/10.1182/blood-2020-142426 -
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المؤلفون: Keri Dufault, Sarfraz Shaikh, Brian Bettencourt, Nenad Svrzikapa, Akin Akinc, Rachel Meyers, Maple Gioia, Yosef Landesman, Satya Kuchimanchi, Xuemei Zhang, Renta Hutabarat, Armand B. Cognetta
المصدر: Silence
مصطلحات موضوعية: Small interfering RNA, Factor VII, Cell, Methodology, Biology, Molecular biology, Reverse transcription polymerase chain reaction, chemistry.chemical_compound, Real-time polymerase chain reaction, medicine.anatomical_structure, chemistry, Pharmacokinetics, In vivo, medicine, Gene silencing, Molecular Biology, Biotechnology
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::1e689fb7d1b9e13e69bafec3f632790f