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1دورية أكاديمية
المؤلفون: De Ravin, Suk See, Wu, Xiaolin, Moir, Susan, Kardava, Lela, Anaya-O’Brien, Sandra, Kwatemaa, Nana, Littel, Patricia, Theobald, Narda, Choi, Uimook, Su, Ling, Marquesen, Martha, Hilligoss, Dianne, Lee, Janet, Buckner, Clarissa M, Zarember, Kol A, O’Connor, Geraldine, McVicar, Daniel, Kuhns, Douglas, Throm, Robert E, Zhou, Sheng, Notarangelo, Luigi D, Hanson, I Celine, Cowan, Mort J, Kang, Elizabeth, Hadigan, Coleen, Meagher, Michael, Gray, John T, Sorrentino, Brian P, Malech, Harry L
المصدر: Science Translational Medicine. 8(335)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Stem Cell Research - Nonembryonic - Human, Biotechnology, Stem Cell Research, Pediatric, Gene Therapy, Genetics, Vaccine Related, Transplantation, Regenerative Medicine, Rare Diseases, Stem Cell Research - Nonembryonic - Non-Human, 2.1 Biological and endogenous factors, Aetiology, Development of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Inflammatory and immune system, Adolescent, Adult, B-Lymphocytes, Child, Genetic Therapy, Genetic Vectors, Hematopoietic Stem Cells, Humans, Interleukin Receptor Common gamma Subunit, Killer Cells, Natural, Lentivirus, Male, T-Lymphocytes, X-Linked Combined Immunodeficiency Diseases, Young Adult, Biological Sciences, Medical and Health Sciences, Medical biotechnology, Biomedical engineering
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/8p97n39f
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2دورية أكاديمية
المؤلفون: McDermott, David H., Liu, Qian, Velez, Daniel, Lopez, Lizbeeth, Anaya-O'Brien, Sandra, Ulrick, Jean, Kwatemaa, Nana, Starling, Judy, Fleisher, Thomas A., Priel, Debra A. Long, Merideth, Melissa A., Giuntoli, Robert L., Evbuomwan, Moses O., Littel, Patricia, Marquesen, Martha M., Hilligoss, Dianne, DeCastro, Rosamma, Grimes, George J., Hwang, Samuel T., Pittaluga, Stefania, Calvo, Katherine R., Stratton, Pamela, Cowen, Edward W., Kuhns, Douglas B., Malech, Harry L., Murphy, Philip M.
المصدر: In Blood 10 April 2014 123(15):2308-2316
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3دورية أكاديمية
المؤلفون: McDermott, David H. *, Liu, Qian, Ulrick, Jean, Kwatemaa, Nana, Anaya-O'Brien, Sandra, Penzak, Scott R., Filho, Joao Oliveira, Priel, Debra A. Long, Kelly, Corin, Garofalo, Mary, Littel, Patricia, Marquesen, Martha M., Hilligoss, Diane, DeCastro, Rosamma, Fleisher, Thomas A., Kuhns, Douglas B., Malech, Harry L., Murphy, Philip M.
المصدر: In Blood 3 November 2011 118(18):4957-4962
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4دورية أكاديمية
المؤلفون: McDermott, David H. *, De Ravin, Suk See, Jun, Hyun Sik, Liu, Qian, Priel, Debra A. Long, Noel, Pierre, Takemoto, Clifford M., Ojode, Teresa, Paul, Scott M., Dunsmore, Kimberly P., Hilligoss, Dianne, Marquesen, Martha, Ulrick, Jean, Kuhns, Douglas B., Chou, Janice Y., Malech, Harry L., Murphy, Philip M.
المصدر: In Blood 14 October 2010 116(15):2793-2802
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5دورية أكاديمية
المؤلفون: Malech, Harry, Free, Almena, Okonkwo, Enola, Littel, Patricia, Rooths, Nicole, Quackenbush, Priscilla, Marquesen, Martha, Hodges, Michael, Patick, Amy, Sperry, Sam, Bin Yao, Rana, Nawaid, Warner, Doug
المصدر: Topics in Antiviral Medicine; Apr2023, Vol. 31 Issue 2, p214-214, 1/3p
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6دورية أكاديمية
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7دورية أكاديمية
المؤلفون: Kang, Elizabeth M., Parta, Mark, Hilligoss, Dianne, Marquesen, Martha, Kelly, Corin, Kwatemaa, Akua, Malech, Harry L.
المصدر: In Biology of Blood and Marrow Transplantation March 2016 22(3) Supplement:S327-S328
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8دورية أكاديمية
المؤلفون: Suk See De Ravin, Xiaolin Wu, Moir, Susan, Kardava, Lela, Anaya-O’Brien, Sandra, Kwatemaa, Nana, Littel, Patricia, Theobald, Narda, Uimook Choi, Ling Su, Marquesen, Martha, Hilligoss, Dianne, Lee, Janet, Buckner, Clarissa M., Zarember, Kol A., O’Connor, Geraldine, McVicar, Daniel, Kuhns, Douglas, Throm, Robert E., Sheng Zhou
المصدر: Science Translational Medicine; 4/20/2016, Vol. 8 Issue 335, p1-11, 11p, 1 Color Photograph, 5 Graphs
مصطلحات موضوعية: GENE therapy, HEMATOPOIETIC stem cells, SEVERE combined immunodeficiency, HEMATOPOIETIC stem cell transplantation, IMMUNE system
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9دورية أكاديمية
المؤلفون: Bryke, Christine R., McDermott, David H., Gao, Ji-Liang, Liu, Qian, Siwicki, Marie, Martens, Craig, Jacobs, Paejonette, Velez, Daniel, Yim, Erin, Hsu, Nancy, Dai, Zunyan, Marquesen, Martha M., Stregevsky, Elina, Kwatemaa, Nana, Theobald, Narda, Long Priel, Debra A., Pittaluga, Stefania, Raffeld, Mark A., Calvo, Katherine R., Maric, Irina, Desmond, Ronan, Holmes, Kevin L., Kuhns, Douglas B., Balabanian, Karl, Bachelerie, Françoise, Porcella, Stephen F., Malech, Harry L., Murphy, Philip M.
المصدر: In Cancer Genetics June 2015 208(6):358-359
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10دورية أكاديمية
المؤلفون: Rudman Spergel, Amanda K., Chen, Clara C., Beegle, Cheryl Ann, Littel, Patricia, Garofalo, Mary, Anaya-O'Brien, Sandra, Marquesen, Martha, Bagci, Ulas, Mollura, Daniel J., Gallin, John I., Malech, Harry L.
المصدر: In The Journal of Allergy and Clinical Immunology February 2015 135(2) Supplement:AB98-AB98