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1دورية أكاديمية
المؤلفون: Liron Elkouby, Sean M. Armour, Raffaella Toso, Marti DiPietro, Robert J. Davidson, Giang N. Nguyen, Mallory Willet, Stephanie Kutza, Joseph Silverberg, Jennifer Frick, Marco Crosariol, Yuhuan Wang, Chuansong Wang, Katherine A. High, Denise E. Sabatino, Xavier M. Anguela
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 24, Iss , Pp 20-29 (2022)
مصطلحات موضوعية: hemophilia A, AAV, optimized vectors, codon optimization, low AAV dose, preclinical development, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2
المؤلفون: Lizbeth M. Hoos, Laura Sepp-Lorenzino, Walter Strapps, John Levorse, Dietmar Seiffert, Karen R. Leander, Marti DiPietro, Yuchen Zhou, Anil Thankappan, Weizhen Wu, Tian-Quan Cai, Zuo Zhang, Zhu Chen, Yiming Xu, Marija Tadin-Strapps, Myung K. Shin, Patrick Andre, Joseph M. Metzger, Kunal Desai, KehDih Lai, Nina Jochnowitz, Ross Bentley
المصدر: Thrombosis and haemostasis. 113(6)
مصطلحات موضوعية: Male, medicine.medical_specialty, Small interfering RNA, Time Factors, Genotype, Haemophilia A, Hemorrhage, 030204 cardiovascular system & hematology, Pharmacology, Transfection, Ferric Compounds, Hemophilia B, Cell Line, Factor IX, Rats, Sprague-Dawley, 03 medical and health sciences, 0302 clinical medicine, Chlorides, Bleeding time, Antithrombotic, medicine, Gene silencing, Animals, Haemophilia B, RNA, Messenger, RNA, Small Interfering, Gene knockdown, Hemostasis, medicine.diagnostic_test, business.industry, Thrombosis, Hematology, medicine.disease, Surgery, Rats, Disease Models, Animal, Phenotype, RNAi Therapeutics, Gene Expression Regulation, Liver, 030220 oncology & carcinogenesis, RNA Interference, Rats, Transgenic, business, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::c451ee47e663a79cf3f2011d6a5ea178
https://pubmed.ncbi.nlm.nih.gov/25790442 -
3
المؤلفون: Xavier M. Anguela, Liron Elkouby, Marti DiPietro, Katherine A. High, Raffaella Toso, Robert J. Davidson, Denise E. Sabatino
المصدر: Blood. 126:199-199
مصطلحات موضوعية: biology, business.industry, Immunology, Wild type, Context (language use), Cell Biology, Hematology, Biochemistry, Virology, Viral vector, Immune system, biology.protein, medicine, Vector (molecular biology), Expression cassette, Antibody, business, Factor IX, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::89e7af0000963c742c359efc12347f0e
https://doi.org/10.1182/blood.v126.23.199.199