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1دورية أكاديمية
المؤلفون: Mistry, Pramod K, Lukina, Elena, Turkia, Hadhami Ben, Shankar, Suma P, Feldman, Hagit, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Lau, Heather, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Foster, Meredith C, Gaemers, Sebastiaan JM, Peterschmitt, M Judith
المصدر: American Journal of Hematology. 96(9)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Hematology, Clinical Research, Rare Diseases, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Adult, Double-Blind Method, Enzyme Inhibitors, Female, Gaucher Disease, Humans, Liver, Male, Organ Size, Placebo Effect, Pyrrolidines, Spleen, Treatment Outcome, Young Adult, Cardiorespiratory Medicine and Haematology, Immunology, Cardiovascular medicine and haematology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/88h92743
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2دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
3دورية أكاديمية
المؤلفون: Zheng, Melanie, Hakim, Aaron, Konkwo, Chigoziri, Deaton, Aimee M., Ward, Lucas D., Silveira, Marina G., Assis, David N., Liapakis, AnnMarie, Jaffe, Ariel, Jiang, Z. Gordon, Curry, Michael P., Lai, Michelle, Cho, Michael H., Dykas, Daniel, Bale, Allen, Mistry, Pramod K., Vilarinho, Silvia
المصدر: In eBioMedicine September 2023 95
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4دورية أكاديمية
المؤلفون: Cox, Timothy M., Charrow, Joel, Lukina, Elena, Mistry, Pramod K., Foster, Meredith C., Peterschmitt, M. Judith
المصدر: In Genetics in Medicine February 2023 25(2)
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5دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
6دورية أكاديمية
المؤلفون: Verma, I. C., El-Beshlawy, A., Tylki-Szymańska, A., Martins, A., Duan, Y.-L.Aff5, Aff6, Collin-Histed, T., van der Linde, M. Schoneveld, Mansour, R., Dũng, V. C., Mistry, Pramod K.Aff11, IDs13023022021921_cor10
المصدر: Orphanet Journal of Rare Diseases. 17(1)
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7دورية أكاديمية
المؤلفون: Mistry, Pramod K, Lukina, Elena, Turkia, Hadhami Ben, Shankar, Suma P, Baris, Hagit, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Pastores, Gregory, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Gaemers, Sebastiaan JM, Tayag, Regina, Peterschmitt, M Judith
المصدر: American Journal of Hematology. 92(11)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Clinical Research, Clinical Trials and Supportive Activities, Hematology, 6.1 Pharmaceuticals, Evaluation of treatments and therapeutic interventions, Enzyme Inhibitors, Enzyme Replacement Therapy, Follow-Up Studies, Gaucher Disease, Glucosylceramidase, Humans, Liver, Organ Size, Pyrrolidines, Spleen, Treatment Outcome, Cardiorespiratory Medicine and Haematology, Immunology, Cardiovascular medicine and haematology
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/3vt8j9ht
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8دورية أكاديمية
لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل. -
9دورية أكاديمية
المؤلفون: Mistry, Pramod K, Lukina, Elena, Turkia, Hadhami Ben, Amato, Dominick, Baris, Hagit, Dasouki, Majed, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Pastores, Gregory, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Shankar, Suma, Solano, Maria Helena, Ross, Leorah, Angell, Jennifer, Peterschmitt, M Judith
المصدر: JAMA. 313(7)
مصطلحات موضوعية: Digestive Diseases, Clinical Trials and Supportive Activities, Hematology, Clinical Research, 6.1 Pharmaceuticals, Evaluation of treatments and therapeutic interventions, Administration, Oral, Adult, Double-Blind Method, Enzyme Inhibitors, Female, Gaucher Disease, Glucosyltransferases, Humans, Male, Organ Size, Pyrrolidines, Spleen, Splenomegaly, Young Adult, Medical and Health Sciences, General & Internal Medicine
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/1pb8689v
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10دورية أكاديمية
المؤلفون: Angeli, Paolo, Belcher, Justin, Gambino, Carmine, Salaheldin, Mohamed, Treepraertsuk, Sombat, Puthumana, Jeremy, Lugon, Nicolas Chong, Xu, Yunshan, Deng, Yanhong, Mistry, Pramod K., Parikh, Chirag R.
المصدر: In Kidney International Reports July 2024 9(7):2278-2281