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1دورية أكاديمية
المؤلفون: Fabio Ciceri, Régis Peffault de Latour, Raynier Devillier, Patrizia Chiusolo, Aurelie Bauquet, Laura Simons, Pierre Heimendinger, Pierre Gaudeaux, Olivier Negre, Tayebeh-Shabi Soheili, Juliette Paillet, Isabelle Andre, Sebastien Oster, Marina Cavazzana, Frederic Lehmann
المصدر: HemaSphere, Vol 7, p e797368b (2023)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Jaap Jan Boelens, Muhammad Umair Mushtaq, Joseph Mcguirk, Aurelie Bauquet, Laura Simons, Pierre Heimendinger, Pierre Gaudeaux, Isabelle Andre, Juliette Paillet, Olivier Negre, Tayebeh-Shabi Soheili, Sebastien Oster, Marcel R.M. van den Brink, Frederic Lehmann, Marina Cavazzana, Miguel-Angel Perales
المصدر: HemaSphere, Vol 7, p e660193c (2023)
مصطلحات موضوعية: Diseases of the blood and blood-forming organs, RC633-647.5
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Christian Brendel, Olivier Negre, Michael Rothe, Swaroopa Guda, Geoff Parsons, Chad Harris, Meaghan McGuinness, Daniela Abriss, Alla Tsytsykova, Denise Klatt, Martin Bentler, Danilo Pellin, Lauryn Christiansen, Axel Schambach, John Manis, Helene Trebeden-Negre, Melissa Bonner, Erica Esrick, Gabor Veres, Myriam Armant, David A. Williams
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 589-600 (2020)
مصطلحات موضوعية: Sickle cell disease, HbS, hemoglobinopathies, gene therapy, lentiviral vector, BCL11A, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Sowmya Pattabhi, Samantha N. Lotti, Mason P. Berger, Swati Singh, Christopher T. Lux, Kyle Jacoby, Calvin Lee, Olivier Negre, Andrew M. Scharenberg, David J. Rawlings
المصدر: Molecular Therapy: Nucleic Acids, Vol 17, Iss , Pp 277-288 (2019)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Christopher T. Lux, Sowmya Pattabhi, Mason Berger, Cynthia Nourigat, David A. Flowers, Olivier Negre, Olivier Humbert, Julia G. Yang, Calvin Lee, Kyle Jacoby, Irwin Bernstein, Hans-Peter Kiem, Andrew Scharenberg, David J. Rawlings
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 12, Iss , Pp 175-183 (2019)
وصف الملف: electronic resource
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6دورية أكاديمية
المؤلفون: Gretchen Lewis, Lauryn Christiansen, Jessica McKenzie, Min Luo, Eli Pasackow, Yegor Smurnyy, Sean Harrington, Philip Gregory, Gabor Veres, Olivier Negre, Melissa Bonner
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 9, Iss , Pp 313-322 (2018)
وصف الملف: electronic resource
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7
المؤلفون: Olivier Negre
المصدر: Cell and Gene Therapy Insights. 7:63-70
مصطلحات موضوعية: business.industry, Genetic enhancement, Medicine, business, Bioinformatics, General Economics, Econometrics and Finance
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::3ed52645305b8f6f82e9973d070a6018
https://doi.org/10.18609/cgti.2021.019 -
8
المؤلفون: Olivier Negre, Swaroopa Guda, Christian Brendel, Chad E. Harris, Martin Bentler, Myriam Armant, Melissa Bonner, Erica B. Esrick, John P. Manis, Helene Trebeden-Negre, Axel Schambach, Alla V. Tsytsykova, Danilo Pellin, Michael Rothe, Lauryn Christiansen, Denise Klatt, David A. Williams, Meaghan McGuinness, Daniela Abriss, Geoff Parsons, Gabor Istvan Veres
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 589-600 (2020)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, fetal hemoglobin, lcsh:QH426-470, Genetic enhancement, Cell, CD34, Biology, Article, Viral vector, Small hairpin RNA, 03 medical and health sciences, 0302 clinical medicine, RNA interference, BCL11A, Fetal hemoglobin, Genetics, medicine, shRNAmiR, lcsh:QH573-671, hemoglobinopathies, Molecular Biology, Gene knockdown, lcsh:Cytology, Sickle cell disease, lentiviral vector, gene therapy, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, HbS, 030220 oncology & carcinogenesis, hemoglobin switch, Cancer research, Molecular Medicine
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9
المؤلفون: David J. Rawlings, Samantha N. Lotti, Olivier Negre, Kyle Jacoby, Swati Singh, Sowmya Pattabhi, Andrew M. Scharenberg, Calvin Lee, Christopher T. Lux, Mason P. Berger
المصدر: Molecular Therapy: Nucleic Acids, Vol 17, Iss, Pp 277-288 (2019)
Molecular Therapy. Nucleic Acidsمصطلحات موضوعية: 0301 basic medicine, hemoglobin disorders, Reversion, stem cell cures, NBSGW41 mice, Biology, Article, law.invention, Homology directed repair, 03 medical and health sciences, 0302 clinical medicine, Genome editing, law, Drug Discovery, CRISPR, rAAV6, Gene, Ribonucleoprotein, gene editing, Point mutation, lcsh:RM1-950, ssODN, Molecular biology, hematopoietic stem cells, homology-directed repair, 030104 developmental biology, lcsh:Therapeutics. Pharmacology, 030220 oncology & carcinogenesis, Recombinant DNA, Molecular Medicine, sickle cell disease, Crispr/Cas9, in vivo engraftment, CD34, NHEJ versus HDR
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10
المؤلفون: Irwin D. Bernstein, Julia G. Yang, Andrew M. Scharenberg, Christopher T. Lux, Olivier Negre, Sowmya Pattabhi, David A. Flowers, Kyle Jacoby, Mason P. Berger, Hans-Peter Kiem, Calvin Lee, Cynthia Nourigat, Olivier Humbert, David J. Rawlings
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 12, Iss, Pp 175-183 (2019)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, HBG, thalassemia, HBG1, Hereditary persistence of fetal hemoglobin, lcsh:QH426-470, Biology, HSC, Article, 03 medical and health sciences, 0302 clinical medicine, TALEN, Fetal hemoglobin, Genetics, medicine, hemoglobinopathy, lcsh:QH573-671, Molecular Biology, HPFH, gene editing, lcsh:Cytology, Transfection, hemoglobin, medicine.disease, Molecular biology, 3. Good health, SCD, Transplantation, Haematopoiesis, lcsh:Genetics, 030104 developmental biology, 030220 oncology & carcinogenesis, Humanized mouse, Molecular Medicine, sickle cell disease, Stem cell