المؤلفون: Nguyen CT; Faculty of Technology, Dong Nai Technology University, Bien Hoa City, Vietnam. Electronic address: nguyenthanhcong@dntu.edu.vn., Nguyen Di K; Faculty of Health Sciences, Dong Nai Technology University, Bien Hoa City, Vietnam., Phan HC; Faculty of Health Sciences, Dong Nai Technology University, Bien Hoa City, Vietnam., Kha TC; Faculty of Chemical Engineering and Food Technology, Nong Lam University Ho Chi Minh City, Thu Duc, Ho Chi Minh City, Vietnam. Electronic address: khachantuyen@hcmuaf.edu.vn., Nguyen HC; Southern Military Institute of Preventive Medicine, Go Vap, Ho Chi Minh City, Vietnam.

المصدر: International journal of biological macromolecules [Int J Biol Macromol] 2024 Jun; Vol. 269 (Pt 2), pp. 132217. Date of Electronic Publication: 2024 May 08.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: Elsevier Country of Publication: Netherlands NLM ID: 7909578 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1879-0003 (Electronic) Linking ISSN: 01418130 NLM ISO Abbreviation: Int J Biol Macromol Subsets: MEDLINE

مواضيع طبية MeSH: Gum Arabic*/chemistry , Polysaccharides*/chemistry , Plant Extracts*/chemistry , Drug Compounding*/methods , Fruit*/chemistry , Morinda*/chemistry, Drug Stability ; Hydrogen-Ion Concentration ; Capsules

المؤلفون: Urzi A; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany., Lahmann I; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany., Nguyen LVN; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany., Rost BR; German Center for Neurodegenerative Diseases (DZNE), Berlin, Germany., García-Pérez A; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany., Lelievre N; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany., Merritt-Garza ME; Department of Cell Biology, Laboratory for Translational Cell Biology, Emory University School of Medicine, Atlanta, GA, 30322, USA., Phan HC; Department of Pediatrics, University of Alabama, Birmingham, AL, 35294, USA., Bassell GJ; Department of Cell Biology, Laboratory for Translational Cell Biology, Emory University School of Medicine, Atlanta, GA, 30322, USA., Rossoll W; Department of Neuroscience, Mayo Clinic, Jacksonville, FL, 32224, USA.; Mayo Clinic Graduate School of Biomedical Sciences, Mayo Clinic, Jacksonville, FL, 32224, USA., Diecke S; Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), Technology Platform Pluripotent Stem Cells, 13125, Berlin, Germany., Kunz S; Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), Technology Platform Electron Microscopy, 13125, Berlin, Germany., Schmitz D; German Center for Neurodegenerative Diseases (DZNE), Berlin, Germany.; Berlin Institute of Health, NeuroCure Cluster of Excellence, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany., Gouti M; Stem Cell Modeling of Development & Disease Group, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125, Berlin, Germany. mina.gouti@mdc-berlin.de.

المصدر: Nature communications [Nat Commun] 2023 Dec 19; Vol. 14 (1), pp. 8043. Date of Electronic Publication: 2023 Dec 19.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE

مواضيع طبية MeSH: Muscular Atrophy, Spinal*/pathology , Induced Pluripotent Stem Cells*/pathology, Humans ; Neuromuscular Junction/pathology ; Motor Neurons/physiology ; Muscle Fibers, Skeletal/pathology ; Muscle, Skeletal/pathology

المؤلفون: Verma S; Department of Pediatric Neurology and Neurosciences, Children's Healthcare of Atlanta, and Emory University School of Medicine, Atlanta, Georgia, USA., Nwosu SN; Department of Pediatric Neurology and Neurosciences, Children's Healthcare of Atlanta, and Emory University School of Medicine, Atlanta, Georgia, USA., Razdan R; Department of Pediatric Neurology and Neurosciences, Children's Healthcare of Atlanta, and Emory University School of Medicine, Atlanta, Georgia, USA., Upadhyayula SR; Department of Pediatric Neurology and Neurosciences, Children's Healthcare of Atlanta, and Emory University School of Medicine, Atlanta, Georgia, USA., Phan HC; Department of Pediatric Neurology, The University of Alabama at Birmingham, Birmingham, Alabama, USA., Koroma AA; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Leguizamo I; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Correa NS; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Kuipa M; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Lee D; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Vanderford TH; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA., Gardner MR; Division of Microbiology and Immunology, Emory National Primate Research Center, Emory University, Atlanta, Georgia, USA.; Division of Infectious Diseases, Department of Medicine, Emory University, Atlanta, Georgia, USA.

المصدر: Human gene therapy [Hum Gene Ther] 2023 May; Vol. 34 (9-10), pp. 430-438. Date of Electronic Publication: 2022 Dec 19.

نوع المنشور: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1557-7422 (Electronic) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE

مواضيع طبية MeSH: Antibodies, Neutralizing* , Muscular Dystrophy, Duchenne*, Male ; Humans ; Child ; Antibodies, Viral ; Dependovirus/genetics ; Seroepidemiologic Studies ; Genetic Vectors

المؤلفون: Connolly AM; Nationwide Children's Hospital, Ohio State University College of Medicine, Columbus, OH, USA., Zaidman CM; Department of Neurology, Washington University at St. Louis, St. Louis, MO, USA., Brandsema JF; Division of Neurology, The Children's Hospital of Philadelphia, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Phan HC; Rare Disease Research, LLC, Atlanta, GA, USA., Tian C; Division of Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA., Zhang X; FibroGen, Inc., San Francisco, CA, USA., Li J; FibroGen, Inc., San Francisco, CA, USA., Eisner MD; FibroGen, Inc., San Francisco, CA, USA., Carrier E; FibroGen, Inc., San Francisco, CA, USA.

المصدر: Journal of neuromuscular diseases [J Neuromuscul Dis] 2023; Vol. 10 (4), pp. 685-699.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: IOS Press Country of Publication: Netherlands NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE

مواضيع طبية MeSH: Muscular Dystrophy, Duchenne*/genetics, Humans ; Dystrophin ; Antibodies, Monoclonal/therapeutic use ; Connective Tissue Growth Factor

المؤلفون: Kwon JM; Division of Pediatric Neurology, Department of Neurology, University of Wisconsin-Madison School of Medicine and Public Health, Madison, Wisconsin, USA., Arya K; Division of Neurology, Department of Pediatrics, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA., Kuntz N; Division of Neurology, Department of Pediatrics, Ann and Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA., Phan HC; Rare Disease Research, LLC, Atlanta, Georgia, USA., Sieburg C; Division of Pediatric Neurology, Department of Neurology, University of Wisconsin-Madison School of Medicine and Public Health, Madison, Wisconsin, USA., Swoboda KJ; Department of Neurology, Massachusetts General Hospital, Boston, Massachusetts, USA., Veerapandiyan A; Division of Neurology, Department of Pediatrics, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA., Assman B; Genentech, South San Francisco, California, USA., Bader-Weder S; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Dickendesher TL; Genentech, South San Francisco, California, USA., Hansen J; Genentech, South San Francisco, California, USA., Lin H; Genentech, South San Francisco, California, USA., Yan Y; Genentech, South San Francisco, California, USA., Rao VK; Division of Neurology, Department of Pediatrics, Ann and Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.

مؤلفون مشاركون: US Expanded Access Program Working Group

المصدر: Annals of clinical and translational neurology [Ann Clin Transl Neurol] 2022 Jun; Vol. 9 (6), pp. 810-818. Date of Electronic Publication: 2022 May 14.

نوع المنشور: Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: Wiley Periodicals, Inc on behalf of American Neurological Association Country of Publication: United States NLM ID: 101623278 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2328-9503 (Electronic) Linking ISSN: 23289503 NLM ISO Abbreviation: Ann Clin Transl Neurol Subsets: MEDLINE

مواضيع طبية MeSH: Muscular Atrophy, Spinal*/drug therapy , COVID-19 Drug Treatment*, Adult ; Azo Compounds/therapeutic use ; Child ; Humans ; Pandemics ; Pyrimidines

المؤلفون: Haber G; Division of Cancer Epidemiology and Genetics, National Cancer Institute, Bethesda, Maryland, USA., Conway KM; Department of Epidemiology, University of Iowa, Iowa City, Iowa, USA., Paramsothy P; National Center on Birth Defects and Developmental Disabilities, Centers for Disease Control and Prevention, Atlanta, Georgia, USA., Roy A; Department of Mathematics and Statistics, University of Maryland, Baltimore County, Baltimore, Maryland, USA., Rogers H; Center for Drug Evaluation and Research, Food & Drug Administration, Silver Spring, Maryland, USA., Ling X; Center for Drug Evaluation and Research, Food & Drug Administration, Silver Spring, Maryland, USA., Kozauer N; Center for Drug Evaluation and Research, Food & Drug Administration, Silver Spring, Maryland, USA., Street N; National Center on Birth Defects and Developmental Disabilities, Centers for Disease Control and Prevention, Atlanta, Georgia, USA., Romitti PA; Department of Epidemiology, University of Iowa, Iowa City, Iowa, USA., Fox DJ; Bureau of Environmental and Occupational Epidemiology, New York State Department of Health, Albany, New York, USA., Phan HC; Department of Pediatrics, Division of Neurology, University of Alabama at Birmingham, Birmingham, Alabama, USA., Matthews D; Department of Physical Medicine and Rehabilitation, Children's Hospital Colorado, Aurora, Colorado, USA., Ciafaloni E; Department of Neurology, University of Rochester, Rochester, New York, USA., Oleszek J; Department of Physical Medicine and Rehabilitation, Children's Hospital Colorado, Aurora, Colorado, USA., James KA; School of Public Health, University of Colorado, Boulder, Colorado, USA., Galindo M; Department of Pediatrics, University of Arizona, Tucson, Arizona, USA., Whitehead N; Research Triangle Institute International, Research Triangle Park, North Carolina, USA., Johnson N; Department of Neurology, Virginia Commonwealth University, Richmond, Virginia, USA., Butterfield RJ; Department of Pediatrics and Neurology, University of Utah, Salt Lake City, Utah, USA., Pandya S; Department of Neurology, University of Rochester, Rochester, New York, USA., Venkatesh S; Department of Neurology, University of South Carolina, Columbia, South Carolina, USA., Bhattaram VA; Center for Drug Evaluation and Research, Food & Drug Administration, Silver Spring, Maryland, USA.

المصدر: Muscle & nerve [Muscle Nerve] 2021 Feb; Vol. 63 (2), pp. 181-191. Date of Electronic Publication: 2020 Nov 17.

نوع المنشور: Journal Article; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, U.S. Gov't, P.H.S.

بيانات الدورية: Publisher: John Wiley & Sons Country of Publication: United States NLM ID: 7803146 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1097-4598 (Electronic) Linking ISSN: 0148639X NLM ISO Abbreviation: Muscle Nerve Subsets: MEDLINE

مواضيع طبية MeSH: Mobility Limitation*, Dystrophin/*genetics , Muscular Dystrophy, Duchenne/*genetics , Muscular Dystrophy, Duchenne/*physiopathology, Adolescent ; Adrenal Cortex Hormones/therapeutic use ; Child ; Dependent Ambulation ; Disease Progression ; Exons ; Gene Duplication ; Humans ; Male ; Muscular Dystrophy, Duchenne/drug therapy ; Point Mutation ; Proportional Hazards Models ; Sequence Deletion ; Wheelchairs

المؤلفون: Finkel RS; St. Jude Children's Research Hospital, Memphis, TN and Nemours Children's Hospital, Orlando, FL, USA., McDonald CM; University of California at Davis, Sacramento, CA, USA., Lee Sweeney H; University of Florida College of Medicine, Gainesville, FL, USA., Finanger E; Shriners Hospital for Children, Portland, OR, USA., Neil Knierbein E; University of Michigan, MI, Ann Arbor, MI, USA., Wagner KR; Kennedy Krieger Institute, The Johns Hopkins School of Medicine, Baltimore, MD, USA., Mathews KD; University of Iowa Carver College of Medicine, Iowa City, IA, USA., Marks W; Cook Children's Medical Center, Fort Worth, TX, USA., Statland J; University of Kansas Medical Center, Kansas City, KS, USA., Nance J; Johns Hopkins University, Baltimore, MD, USA., McMillan HJ; Children's Hospital of Eastern Ontario, Ottawa, CA, Canada., McCullagh G; Royal Manchester Children's Hospital, UK., Tian C; Cincinnati Children's Hospital & University of Cincinnati, Cincinnati, OH, USA., Ryan MM; Royal Children's Hospital, Melbourne, Australia., O'Rourke D; Children's Health Ireland at Temple Street, Dublin, Ireland., Müller-Felber W; Dr. v. Haunersches Kinderspital, Munich, Germany., Tulinius M; Queen Silvia Children's Hospital, Gothenburg, Sweden., Burnette WB; Vanderbilt University Medical Center, Nashville, TN, USA., Nguyen CT; CHU Sainte-Justine, Montreal, CA, Canada., Vijayakumar K; Bristol Children's Hospital, Bristol, UK., Johannsen J; University Medical Center Hamburg-Eppendorf, Hamburg, Germany., Phan HC; Rare Disease Research, LLC, Atlanta, GA, USA., Eagle M; Atom International Limited, Newcastle upon Tyne, UK., MacDougall J; University Medical Center Hamburg-Eppendorf, Hamburg, Germany., Mancini M; Catabasis Pharmaceuticals, Inc., Boston, MA, USA., Donovan JM; Catabasis Pharmaceuticals, Inc., Boston, MA, USA.

مؤلفون مشاركون: (For the PolarisDMD Study Group)

المصدر: Journal of neuromuscular diseases [J Neuromuscul Dis] 2021; Vol. 8 (5), pp. 769-784.

نوع المنشور: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial

بيانات الدورية: Publisher: IOS Press Country of Publication: Netherlands NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE

مواضيع طبية MeSH: Arachidonic Acids/*therapeutic use , Muscular Dystrophy, Duchenne/*drug therapy , Salicylamides/*therapeutic use, Administration, Oral ; Child ; Child, Preschool ; Double-Blind Method ; Humans ; Male ; NF-kappa B

المؤلفون: Phan HC; Faculty of Science, Engineering, and Technology, Swinburne University of Technology, Hawthorn, Victoria, Australia hoang.phan@virbac.vn., Wade SA; Faculty of Science, Engineering, and Technology, Swinburne University of Technology, Hawthorn, Victoria, Australia., Blackall LL; School of BioSciences, University of Melbourne, Melbourne, Victoria, Australia.

المصدر: Applied and environmental microbiology [Appl Environ Microbiol] 2020 Jun 17; Vol. 86 (13). Date of Electronic Publication: 2020 Jun 17 (Print Publication: 2020).

نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: American Society for Microbiology Country of Publication: United States NLM ID: 7605801 Publication Model: Electronic-Print Cited Medium: Internet ISSN: 1098-5336 (Electronic) Linking ISSN: 00992240 NLM ISO Abbreviation: Appl Environ Microbiol Subsets: MEDLINE

مواضيع طبية MeSH: Microbiota* , Water Microbiology*, Steel/*chemistry , Water/*chemistry, Corrosion

المؤلفون: Siegel BI; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia., Cakmak A; School of Electrical and Computer Engineering, Georgia Institute of Technology, Atlanta, Georgia., Reinertsen E; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology & Emory University School of Medicine, Atlanta, Georgia., Benoit M; Children's Healthcare of Atlanta, Atlanta, Georgia., Figueroa J; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia., Clifford GD; Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology & Emory University School of Medicine, Atlanta, Georgia.; Department of Biomedical Informatics, Emory University School of Medicine, Atlanta, Georgia., Phan HC; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia.

المصدر: Muscle & nerve [Muscle Nerve] 2020 Feb; Vol. 61 (2), pp. 198-204. Date of Electronic Publication: 2019 Dec 10.

نوع المنشور: Journal Article; Research Support, Non-U.S. Gov't

بيانات الدورية: Publisher: John Wiley & Sons Country of Publication: United States NLM ID: 7803146 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1097-4598 (Electronic) Linking ISSN: 0148639X NLM ISO Abbreviation: Muscle Nerve Subsets: MEDLINE

مواضيع طبية MeSH: Wearable Electronic Devices*, Actigraphy/*instrumentation , Muscular Dystrophy, Duchenne/*diagnosis , Sleep/*physiology, Adolescent ; Child ; Child, Preschool ; Cross-Sectional Studies ; Female ; Humans ; Male ; Monitoring, Physiologic ; Motor Activity ; Muscular Dystrophy, Duchenne/complications ; Muscular Dystrophy, Duchenne/physiopathology ; Quality of Life ; Sleep Wake Disorders/diagnosis ; Sleep Wake Disorders/etiology ; Surveys and Questionnaires ; Walk Test

المؤلفون: Hoang CQ; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam. cuonghqpasteur@gmail.com., Nguyen TTT; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam., Ho NX; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam., Nguyen HD; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam., Nguyen AB; Dong Thap Hospital, 144 Mai Van Khai, My Tan, Cao Lanh City, Dong Thap Province, Vietnam., Nguyen THT; Dong Thap Hospital, 144 Mai Van Khai, My Tan, Cao Lanh City, Dong Thap Province, Vietnam., Phan HC; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam., Phan LT; Pasteur Institute in Ho Chi Minh City, 167 Pasteur Street, District 3, Ho Chi Minh City, Vietnam.

المصدر: BMC infectious diseases [BMC Infect Dis] 2019 Nov 05; Vol. 19 (1), pp. 933. Date of Electronic Publication: 2019 Nov 05.

نوع المنشور: Journal Article

بيانات الدورية: Publisher: BioMed Central Country of Publication: England NLM ID: 100968551 Publication Model: Electronic Cited Medium: Internet ISSN: 1471-2334 (Electronic) Linking ISSN: 14712334 NLM ISO Abbreviation: BMC Infect Dis Subsets: MEDLINE

مواضيع طبية MeSH: Enterovirus/*isolation & purification , Hand, Foot and Mouth Disease/*diagnosis, Adolescent ; Antibodies, Neutralizing/blood ; Child ; Child, Preschool ; Enterovirus/genetics ; Enterovirus/immunology ; Female ; Hand, Foot and Mouth Disease/epidemiology ; Hand, Foot and Mouth Disease/transmission ; Hand, Foot and Mouth Disease/virology ; Humans ; Incidence ; Infant ; Longitudinal Studies ; Male ; RNA, Viral/genetics ; RNA, Viral/metabolism ; Serogroup ; Vietnam/epidemiology