المؤلفون: Terluk, Marcia R.^{Aff1, Aff2}, Tieu, Julianne^{Aff1, Aff2}, Sahasrabudhe, Siddhee A.^{Aff1, Aff2}, Moser, Ann^{Aff3, Aff4}, Watkins, Paul A.^{Aff3, Aff4}, Raymond, Gerald V.^{Aff4, Aff5}, Kartha, Reena V.^{Aff1, Aff2, IDs13311022012267_cor7}

المصدر: Neurotherapeutics: The Journal of the American Society for Experimental Neurotherapeutics. 19(3):1007-1017

المؤلفون: Eichler, Florian, Duncan, Christine, Musolino, Patricia L, Orchard, Paul J, De Oliveira, Satiro, Thrasher, Adrian J, Armant, Myriam, Dansereau, Colleen, Lund, Troy C, Miller, Weston P, Raymond, Gerald V, Sankar, Raman, Shah, Ami J, Sevin, Caroline, Gaspar, H Bobby, Gissen, Paul, Amartino, Hernan, Bratkovic, Drago, Smith, Nicholas JC, Paker, Asif M, Shamir, Esther, O'Meara, Tara, Davidson, David, Aubourg, Patrick, Williams, David A

المصدر: New England Journal of Medicine. 377(17)

مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Cardiovascular Medicine and Haematology, Transplantation, Rare Diseases, Biotechnology, Genetics, Clinical Research, Stem Cell Research, Stem Cell Research - Nonembryonic - Non-Human, Brain Disorders, Neurosciences, Regenerative Medicine, Stem Cell Research - Nonembryonic - Human, Evaluation of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Development of treatments and therapeutic interventions, 6.2 Cellular and gene therapies, ATP Binding Cassette Transporter, Subfamily D, Member 1, ATP-Binding Cassette Transporters, Adolescent, Adrenoleukodystrophy, Antigens, CD34, Biomarkers, Child, Combined Modality Therapy, Genetic Therapy, Genetic Vectors, Granulocyte Colony-Stimulating Factor, Hematopoietic Stem Cell Transplantation, Hematopoietic Stem Cells, Humans, Lentivirus, Male, Polymerase Chain Reaction, Transplantation, Autologous, Medical and Health Sciences, General & Internal Medicine, Biomedical and clinical sciences, Health sciences

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/2kk2q18z

المؤلفون: Raymond, Gerald V, Pasquali, Marzia, Polgreen, Lynda E, Dickson, Patricia I, Miller, Weston P, Orchard, Paul J, Lund, Troy C

المصدر: Scientific reports. 6(1)

مصطلحات موضوعية: Humans, Mucopolysaccharidosis I, Iduronidase, Glucose, Heparitin Sulfate, Adaptor Proteins, Signal Transducing, Nerve Tissue Proteins, Interleukin-8, Gene Expression, Cerebrospinal Fluid Pressure, Mutation, Adolescent, Child, Child, Preschool, Infant, Female, Male, Chemokine CCL2, Chemokine CXCL12, Biomarkers, Adaptor Proteins, Signal Transducing, Preschool

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/2p66q6xg

المؤلفون: Lund, Troy C., Ng, Michelle, Orchard, Paul J., Loes, Daniel J., Raymond, Gerald V., Gupta, Ashish, Kenny-Jung, Dan, Nascene, David R.

المصدر: In Biology of Blood and Marrow Transplantation October 2020 26(10):1894-1899

المؤلفون: Casasnovas, Carlos^{Aff1, Aff2, Aff3}, Ruiz, Montserrat^{Aff2, Aff3, Aff4}, Schlüter, Agatha^{Aff2, Aff3, Aff4}, Naudí, Alba, Fourcade, Stéphane^{Aff2, Aff3, Aff4}, Veciana, Misericordia, Castañer, Sara, Albertí, Antonia, Bargalló, Nuria^{Aff8, Aff9}, Johnson, Maria, Raymond, Gerald V., Fatemi, Ali, Moser, Ann B., Villarroya, Francesc^{Aff12, Aff13}, Portero-Otín, Manuel, Artuch, Rafael^{Aff3, Aff14}, Pamplona, Reinald, Pujol, Aurora^{Aff2, Aff3, Aff4, Aff15}

المصدر: Neurotherapeutics: The Journal of the American Society for Experimental Neurotherapeutics. 16(4):1167-1182

المؤلفون: Raymond, Gerald V.^{Aff6, Aff7}

المساهمون: Schousboe, Arne, Series editor^Aff1, Beart, Philip, editor^Aff2, Robinson, Michael, editor^Aff3, Rattray, Marcus, editor^Aff4, Maragakis, Nicholas J., editor^Aff5

المصدر: Neurodegenerative Diseases : Pathology, Mechanisms, and Potential Therapeutic Targets. 15:365-382

Degree: M.D.

لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل.

لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل.

المؤلفون: Orchard, Paul J., Markowski, Todd W., Higgins, LeeAnn, Raymond, Gerald V., Nascene, David R., Miller, Weston P., Pierpont, Elizabeth I., Lund, Troy C.^Aff1

المصدر: Scientific Reports. 9(1)

لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل.