المؤلفون: Mendell, Jerry R.^{Aff1, Aff2, Aff3}, Pozsgai, Eric R., Lewis, Sarah, Griffin, Danielle A., Lowes, Linda P., Alfano, Lindsay N.^{Aff1, Aff2}, Lehman, Kelly J., Church, Kathleen, Reash, Natalie F., Iammarino, Megan A., Sabo, Brenna, Potter, Rachael, Neuhaus, Sarah, Li, Xiaoxi, Stevenson, Herb, Rodino-Klapac, Louise R.^{Aff4, IDs41591023027309_cor16}

المصدر: Nature Medicine. 30(1):199-206

المؤلفون: Potter, Rachael A., Peterson, Ellyn L., Griffin, Danielle, Cooper Olson, Grace, Lewis, Sarah, Cochran, Kyle, Mendell, Jerry R., Rodino-Klapac, Louise R.

المصدر: In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1)

المؤلفون: Seo, Young-Eun, Baine, Stephen H., Kempton, Amber N., Rogers, Oliver C., Lewis, Sarah, Adegboye, Kaitlin, Haile, Alex, Griffin, Danielle A., Peterson, Ellyn L., Pozsgai, Eric R., Potter, Rachael A., Rodino-Klapac, Louise R.

المصدر: In Molecular Therapy - Methods & Clinical Development 9 March 2023 28:284-299

المؤلفون: Mendell, Jerry R.^{Aff3, Aff4}, Sahenk, Zarife^{Aff3, Aff4}, Rodino-Klapac, Louise R.^{Aff3, Aff5}

المساهمون: Duan, Dongsheng, editor^Aff1, Mendell, Jerry R., editor^Aff2

المصدر: Muscle Gene Therapy. :727-743

المؤلفون: Mendell, Jerry R.^{Aff3, Aff4}, Rodino-Klapac, Louise R.^{Aff3, Aff5}, Walker, Christopher^Aff3

المساهمون: Duan, Dongsheng, editor^Aff1, Mendell, Jerry R., editor^Aff2

المصدر: Muscle Gene Therapy. :709-725

المؤلفون: Mendell, Jerry R.^{Aff3, Aff4}, Rodino-Klapac, Louise R.^{Aff3, Aff5}, Shilling, Christopher J.^Aff6

المساهمون: Duan, Dongsheng, editor^Aff1, Mendell, Jerry R., editor^Aff2

المصدر: Muscle Gene Therapy. :681-698

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لا يتم عرض هذه النتيجة على الضيوف.
تسجيل الدخول للوصول الكامل.

المؤلفون: Mendell, Jerry R., Sahenk, Zarife, Lehman, Kelly J., Lowes, Linda P., Reash, Natalie F., Iammarino, Megan A., Alfano, Lindsay N., Lewis, Sarah, Church, Kathleen, Shell, Richard, Potter, Rachael A., Griffin, Danielle A., Hogan, Mark, Wang, Shufang, Mason, Stefanie, Darton, Eddie, Rodino‐Klapac, Louise R.

المصدر: Muscle & Nerve; Jan2024, Vol. 69 Issue 1, p93-98, 6p

المؤلفون: Klimchak, Alexa C., Sedita, Lauren E., Rodino-Klapac, Louise R., Mendell, Jerry R., McDonald, Craig M., Gooch, Katherine L., Malone, Daniel C.

المصدر: Journal of Market Access & Health Policy; Dec2023, Vol. 11 Issue 1, p1-14, 14p

مصطلحات موضوعية: DUCHENNE muscular dystrophy, VALUE (Economics), GENE therapy, ECONOMIC models, NEUROMUSCULAR diseases