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1دورية أكاديمية
المؤلفون: Helena Costa-Verdera, Fanny Collaud, Christopher R. Riling, Pauline Sellier, Jayme M. L. Nordin, G. Michael Preston, Umut Cagin, Julien Fabregue, Simon Barral, Maryse Moya-Nilges, Jacomina Krijnse-Locker, Laetitia van Wittenberghe, Natalie Daniele, Bernard Gjata, Jeremie Cosette, Catalina Abad, Marcelo Simon-Sola, Severine Charles, Mathew Li, Marco Crosariol, Tom Antrilli, William J. Quinn, David A. Gross, Olivier Boyer, Xavier M. Anguela, Sean M. Armour, Pasqualina Colella, Giuseppe Ronzitti, Federico Mingozzi
المصدر: Nature Communications, Vol 12, Iss 1, Pp 1-16 (2021)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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2دورية أكاديمية
المؤلفون: Giulia De Sabbata, Florence Boisgerault, Corrado Guarnaccia, Alessandra Iaconcig, Giulia Bortolussi, Fanny Collaud, Giuseppe Ronzitti, Marcelo Simon Sola, Patrice Vidal, Jeremy Rouillon, Severine Charles, Emanuele Nicastro, Lorenzo D’Antiga, Petr Ilyinskii, Federico Mingozzi, Takashi Kei Kishimoto, Andrés F. Muro
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 169-180 (2021)
وصف الملف: electronic resource
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3دورية أكاديمية
المؤلفون: Pasqualina Colella, Pauline Sellier, Helena Costa Verdera, Francesco Puzzo, Laetitia van Wittenberghe, Nicolas Guerchet, Nathalie Daniele, Bernard Gjata, Solenne Marmier, Severine Charles, Marcelo Simon Sola, Isabella Ragone, Christian Leborgne, Fanny Collaud, Federico Mingozzi
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 12, Iss , Pp 85-101 (2019)
وصف الملف: electronic resource
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4دورية أكاديمية
المؤلفون: Fanny Collaud, Giulia Bortolussi, Laurence Guianvarc’h, Sem J. Aronson, Thierry Bordet, Philippe Veron, Severine Charles, Patrice Vidal, Marcelo Simon Sola, Stephanie Rundwasser, Delphine G. Dufour, Florence Lacoste, Cyril Luc, Laetitia v. Wittenberghe, Samia Martin, Christine Le Bec, Piter J. Bosma, Andres F. Muro, Giuseppe Ronzitti, Matthias Hebben, Federico Mingozzi
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 12, Iss , Pp 157-174 (2019)
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Amine Meliani, Florence Boisgerault, Romain Hardet, Solenne Marmier, Fanny Collaud, Giuseppe Ronzitti, Christian Leborgne, Helena Costa Verdera, Marcelo Simon Sola, Severine Charles, Alban Vignaud, Laetitia van Wittenberghe, Giorgia Manni, Olivier Christophe, Francesca Fallarino, Christopher Roy, Alicia Michaud, Petr Ilyinskii, Takashi Kei Kishimoto, Federico Mingozzi
المصدر: Nature Communications, Vol 9, Iss 1, Pp 1-13 (2018)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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6دورية أكاديمية
المؤلفون: Pasqualina Colella, Pauline Sellier, Manuel J. Gomez, Maria G. Biferi, Guillaume Tanniou, Nicolas Guerchet, Mathilde Cohen-Tannoudji, Maryse Moya-Nilges, Laetitia van Wittenberghe, Natalie Daniele, Bernard Gjata, Jacomina Krijnse-Locker, Fanny Collaud, Marcelo Simon-Sola, Severine Charles, Umut Cagin, Federico Mingozzi
المصدر: EBioMedicine, Vol 61, Iss , Pp 103052- (2020)
مصطلحات موضوعية: Pompe disease, Mouse model, Respiratory function, Spinal cord, Muscle, AAV, Medicine, Medicine (General), R5-920
وصف الملف: electronic resource
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7دورية أكاديمية
المؤلفون: Elena Barbon, Gabriel Ayme, Amel Mohamadi, Jean‐François Ottavi, Charlotte Kawecki, Caterina Casari, Sebastien Verhenne, Solenne Marmier, Laetitia van Wittenberghe, Severine Charles, Fanny Collaud, Cecile V Denis, Olivier D Christophe, Federico Mingozzi, Peter J Lenting
المصدر: EMBO Molecular Medicine, Vol 12, Iss 4, Pp n/a-n/a (2020)
مصطلحات موضوعية: anticoagulation, coagulation, gene therapy, hemophilia, single‐domain antibodies, Medicine (General), R5-920, Genetics, QH426-470
وصف الملف: electronic resource
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8دورية أكاديمية
المؤلفون: Giuseppe Ronzitti, Giulia Bortolussi, Remco van Dijk, Fanny Collaud, Severine Charles, Christian Leborgne, Patrice Vidal, Samia Martin, Bernard Gjata, Marcelo Simon Sola, Laetitia van Wittenberghe, Alban Vignaud, Philippe Veron, Piter J Bosma, Andres F Muro, Federico Mingozzi
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 3, Iss C (2016)
وصف الملف: electronic resource
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9
المؤلفون: Federica Piccardi, Federico Mingozzi, Giovanni Morelli, Giuseppe Ronzitti, Micol Alberti, Ilaria Colombi, Martina Parrini, Anna Rocchi, Marina Nanni, Laura Cancedda, Andrea Contestabile, Shovan Naskar, Severine Charles
المصدر: Molecular Therapy. 29:3072-3092
مصطلحات موضوعية: Male, Down syndrome, Genetic enhancement, Biology, Chloride, Mice, 03 medical and health sciences, 0302 clinical medicine, Chlorides, RNA interference, Drug Discovery, Genetics, medicine, Animals, Homeostasis, Solute Carrier Family 12, Member 2, Molecular Biology, 030304 developmental biology, Neurons, Pharmacology, 0303 health sciences, Gene knockdown, Transporter, Genetic Therapy, medicine.disease, 3. Good health, Cell biology, Disease Models, Animal, Gene Knockdown Techniques, Molecular Medicine, RNA Interference, Down Syndrome, 030217 neurology & neurosurgery, Intracellular, medicine.drug
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::bd4e2553c80950392f377324fb80efde
https://doi.org/10.1016/j.ymthe.2021.05.023 -
10Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor
المؤلفون: Federico Mingozzi, Caterina Casari, Aboud Sakkal, Peter J. Lenting, Cécile V. Denis, Charlotte Kawecki, Severine Charles, Elena Barbon, Giuseppe Ronzitti, Solenne Marmier, Olivier D. Christophe, Fanny Collaud
المصدر: Gene Therapy. 30:245-254
مصطلحات موضوعية: 0301 basic medicine, congenital, hereditary, and neonatal diseases and abnormalities, Transgene, Genetic enhancement, Context (language use), 030204 cardiovascular system & hematology, Biology, Gene delivery, medicine.disease, Cell biology, 03 medical and health sciences, Transduction (genetics), 030104 developmental biology, 0302 clinical medicine, Von Willebrand factor, hemic and lymphatic diseases, Genetics, biology.protein, Von Willebrand disease, medicine, Molecular Medicine, Molecular Biology, Gene