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1دورية أكاديمية
المؤلفون: Nathalie M Goemans, Már Tulinius, Marleen van den Hauwe, Anna-Karin Kroksmark, Gunnar Buyse, Rosamund J Wilson, Judith C van Deutekom, Sjef J de Kimpe, Afrodite Lourbakos, Giles Campion
المصدر: PLoS ONE, Vol 11, Iss 9, p e0161955 (2016)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1932-6203
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2
المؤلفون: Nicole A. Datson, Cathaline den Besten, Judith C.T. van Deutekom, Sieto Bosgra, Sjef J. de Kimpe, Jessica A. Sipkens
المصدر: Nucleic Acid Therapeutics. 29:305-322
مصطلحات موضوعية: 0301 basic medicine, Oligonucleotide, business.industry, Duchenne muscular dystrophy, Computational biology, medicine.disease, Biochemistry, Exon skipping, Clinical trial, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, Pharmacokinetics, 030220 oncology & carcinogenesis, Pharmacodynamics, Drug Discovery, Genetics, medicine, Molecular Medicine, Distribution (pharmacology), business, Molecular Biology, Drisapersen
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::75f7c6184e4d7580eb6c29c0db62263d
https://doi.org/10.1089/nat.2019.0805 -
3دورية أكاديمية
المؤلفون: Chantal Beekman, Jessica A Sipkens, Janwillem Testerink, Stavros Giannakopoulos, Dyonne Kreuger, Judith C van Deutekom, Giles V Campion, Sjef J de Kimpe, Afrodite Lourbakos
المصدر: PLoS ONE, Vol 9, Iss 9, p e107494 (2014)
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1932-6203
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4دورية أكاديمية
المؤلفون: Ingrid E C Verhaart, Laura van Vliet-van den Dool, Jessica A Sipkens, Sjef J de Kimpe, Ingrid G M Kolfschoten, Judith C T van Deutekom, Lia Liefaard, Jim E Ridings, Steve R Hood, Annemieke Aartsma-Rus
المصدر: Molecular Therapy: Nucleic Acids, Vol 3, Iss C (2014)
مصطلحات موضوعية: Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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5دورية أكاديمية
المؤلفون: Christa L Tanganyika-de Winter, Hans Heemskerk, Tatyana G Karnaoukh, Maaike van Putten, Sjef J de Kimpe, Judith van Deutekom, Annemieke Aartsma-Rus
المصدر: Molecular Therapy: Nucleic Acids, Vol 1, Iss C (2012)
مصطلحات موضوعية: antisense oligonucleotides, Duchenne muscular dystrophy, dystrophin, exon skipping, mouse models, therapy, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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6
المؤلفون: Zhengning Lin, G. Campion, Sjef J. de Kimpe, Afrodite Lourbakos, Kevin M. Flanigan, Craig M. McDonald, Brenda Wong, R. Wilson
المصدر: Annals of Clinical and Translational Neurology
مصطلحات موضوعية: 0301 basic medicine, business.industry, General Neuroscience, Phases of clinical research, Placebo, 3. Good health, Pulmonary function testing, 03 medical and health sciences, Regimen, 030104 developmental biology, 0302 clinical medicine, Tolerability, Pharmacokinetics, Anesthesia, Medicine, Neurology (clinical), business, Adverse effect, Research Articles, 030217 neurology & neurosurgery, Drisapersen, Research Article
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7
المؤلفون: Nicolas Deconinck, Steve S Hood, Haluk Topaloglu, Lia Liefaard, C. Wardell, Rosamund Wilson, Sjef J. de Kimpe, John E. Kraus, Michelle Eagle, Katie Rolfe, Laurent Servais, Joanna Nakielny, Afrodite Lourbakos, Michela Guglieri, Valeria Ricotti, Giles G Campion, Allison A Morgan, Francesco Muntoni, Volker Straub, Padraig Wright, Thomas Voit, Naashika Quarcoo
المصدر: The Lancet Neurology. 13:987-996
مصطلحات موضوعية: Male, medicine.medical_specialty, Duchenne muscular dystrophy, Population, Anti-Inflammatory Agents, Oligonucleotides, Walking, Real-Time Polymerase Chain Reaction, Eteplirsen, Placebo, law.invention, Dystrophin, Double-Blind Method, Randomized controlled trial, Adrenal Cortex Hormones, law, Internal medicine, Clinical endpoint, medicine, Humans, Child, education, Adverse effect, Drisapersen, education.field_of_study, business.industry, Exons, medicine.disease, Muscular Dystrophy, Duchenne, Treatment Outcome, Area Under Curve, Child, Preschool, Physical therapy, Female, Neurology (clinical), business, Gene Deletion
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8
المؤلفون: G. Campion, Sjef J. de Kimpe, Judith C.T. van Deutekom
المصدر: Drug Discovery Today: Therapeutic Strategies. 10:e149-e156
مصطلحات موضوعية: Pharmacology, Genetics, Oligonucleotide, business.industry, Duchenne muscular dystrophy, medicine.disease, Bioinformatics, Clinical trial, Exon, Safety profile, Dmd gene, Drug Discovery, Antisense oligonucleotides, medicine, Molecular Medicine, Personalized medicine, business
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::9d60a1a4478fc5f13d4398b5ce102dd7
https://doi.org/10.1016/j .ddstr.2013.04.001 -
9
المؤلفون: Gert-Jan B. van Ommen, Christa L. de Winter, Petra Van Kuik-Romeijn, Annemieke Aartsma-Rus, Judith C.T. van Deutekom, Hans Heemskerk, Niki Heuvelmans, Sjef J. de Kimpe, Gerard Johannes Platenburg
المصدر: The Journal of Gene Medicine. 11:257-266
مصطلحات موضوعية: congenital, hereditary, and neonatal diseases and abnormalities, Morpholino, Duchenne muscular dystrophy, Molecular Sequence Data, Phosphorothioate Oligonucleotides, Mice, Exon, In vivo, Drug Discovery, Genetics, medicine, Animals, Humans, Muscular dystrophy, Muscle, Skeletal, Molecular Biology, Genetics (clinical), Base Sequence, biology, Myocardium, Gene Transfer Techniques, Exons, Genetic Therapy, Oligonucleotides, Antisense, medicine.disease, Molecular biology, Exon skipping, Muscular Dystrophy, Duchenne, Mice, Inbred mdx, biology.protein, Molecular Medicine, Dystrophin
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10
المؤلفون: Annemieke Aartsma-Rus, Christa L. de Winter, Laura van Vliet, Sjef J. de Kimpe, Gert-Jan B. van Ommen, Judith C.T. van Deutekom, Anneke A.M. Janson, Hans Heemskerk, Peter A C 't Hoen, Marscha Hirschi
المصدر: Molecular Therapy. 17:548-553
مصطلحات موضوعية: Pharmacology, Base Sequence, Oligonucleotide, RNA Splicing, Exonic splicing enhancer, Original Articles, Oligonucleotides, Antisense, Biology, Molecular biology, Exon skipping, Cell biology, SR protein, Drug Discovery, RNA splicing, Genetics, Thermodynamics, Molecular Medicine, splice, Binding site, Enhancer, Molecular Biology