-
1دورية أكاديمية
المؤلفون: Eric WFW Alton, David K Armstrong, Deborah Ashby, Katie J Bayfield, Diana Bilton, Emily V Bloomfield, A Christopher Boyd, June Brand, Ruaridh Buchan, Roberto Calcedo, Paula Carvelli, Mario Chan, Seng H Cheng, David S Collie, Steve Cunningham, Heather E Davidson, Gwyneth Davies, Jane C Davies, Lee A Davies, Maria H Dewar, Ann Doherty, Jackie Donovan, Natalie S Dwyer, Hala I Elgmati, Rosanna F Featherstone, Jemyr Gavino, Sabrina Gea-Sorli, Duncan M Geddes, James SR Gibson, Deborah R Gill, Andrew P Greening, Uta Griesenbach, David M Hansell, Katharine Harman, Tracy E Higgins, Samantha L Hodges, Stephen C Hyde, Laura Hyndman, J Alastair Innes, Joseph Jacob, Nancy Jones, Brian F Keogh, Maria P Limberis, Paul Lloyd-Evans, Alan W Maclean, Michelle C Manvell, Dominique McCormick, Michael McGovern, Gerry McLachlan, Cuixiang Meng, M Angeles Montero, Hazel Milligan, Laura J Moyce, Gordon D Murray, Andrew G Nicholson, Tina Osadolor, Javier Parra-Leiton, David J Porteous, Ian A Pringle, Emma K Punch, Kamila M Pytel, Alexandra L Quittner, Gina Rivellini, Clare J Saunders, Ronald K Scheule, Sarah Sheard, Nicholas J Simmonds, Keith Smith, Stephen N Smith, Najwa Soussi, Samia Soussi, Emma J Spearing, Barbara J Stevenson, Stephanie G Sumner-Jones, Minna Turkkila, Rosa P Ureta, Michael D Waller, Marguerite Y Wasowicz, James M Wilson, Paul Wolstenholme-Hogg, on behalf of the UK Cystic Fibrosis Gene Therapy Consortium
المصدر: Efficacy and Mechanism Evaluation, Vol 3, Iss 5 (2016)
مصطلحات موضوعية: cystic fibrosis, gene therapy, liposome, plasmid, clinical trial, randomised controlled trial, cftr, cystic fibrosis transmembrane conductance regulator, Medicine
وصف الملف: electronic resource
-
2دورية أكاديمية
المؤلفون: Kenneth L Clark, Stephen A Hughes, Pallav Bulsara, Jill Coates, Kitty Moores, Joel Parry, Michael Carr, Ruth J Mayer, Paul Wilson, Chris Gruenloh, Daren Levin, Jill Darton, Wolf-Michael Weber, Katja Sobczak, Deborah R Gill, Stephen C Hyde, Lee A Davies, Ian A Pringle, Stephanie G Sumner-Jones, Vasant Jadhav, Sharon Jamison, Walter R Strapps, Victoria Pickering, Mark R Edbrooke
المصدر: Molecular Therapy: Nucleic Acids, Vol 2, Iss C (2013)
مصطلحات موضوعية: cystic fibrosis, ENaC, GSK2225745, siRNA, therapeutic, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
-
3دورية أكاديمية
المؤلفون: Rosie J. Munday, Tiziana Coradin, Rachael Nimmo, Yatish Lad, Stephen C. Hyde, Kyriacos Mitrophanos, Deborah R. Gill
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 239-252 (2022)
مصطلحات موضوعية: lentiviral vector, pseudotype, human airway, Sendai virus, avian influenza virus, sialic acid, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
-
4دورية أكاديمية
المؤلفون: Helena Meyer-Berg, Lucia Zhou Yang, María Pilar de Lucas, Alberto Zambrano, Stephen C. Hyde, Deborah R. Gill
المصدر: Stem Cell Research & Therapy, Vol 11, Iss 1, Pp 1-6 (2020)
مصطلحات موضوعية: human embryonic stem cells, stem cell-based tissue model, gene therapy, rAAV, AAV capsids, AAV serotypes, Medicine (General), R5-920, Biochemistry, QD415-436
وصف الملف: electronic resource
-
5
المؤلفون: Gerry McLachlan, Eric W.F.W. Alton, A. Christopher Boyd, Nora K. Clarke, Jane C. Davies, Deborah R. Gill, Uta Griesenbach, Jack W. Hickmott, Stephen C. Hyde, Kamran M. Miah, Claudia Juarez Molina
المصدر: McLachlan, G, Alton, E W, Boyd, A C, Clark, N, Davies, J C, Gill, D R, Griesenbach, U, Hickmott, J, Hyde, S C, Miah, K & Juarez Molina, C 2022, ' Progress in Respiratory Gene Therapy ', Human Gene Therapy, vol. 33, no. 17-18, pp. 893-912 . https://doi.org/10.1089/hum.2022.172
مصطلحات موضوعية: Peptide Nucleic Acids, lung disease, gene editing, Genetic Vectors, Gene Transfer Techniques, AAV, gene therapy vectors, DNA, Genetic Therapy, Oligonucleotides, Antisense, respiratory, lentivirus, Genetics, Molecular Medicine, RNA, Messenger, RNA, Small Interfering, Molecular Biology
وصف الملف: application/pdf
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ff0eeccb4804c0c9d17243429c478d77
https://doi.org/10.1089/hum.2022.172 -
6
المؤلفون: Helena Lund-Palau, Claudia Ivette Juarez-Molina, Cuixiang Meng, Anushka Bhargava, Aikaterini Pilou, Kiran Aziz, Nora Clarke, Naoko Atsumi, Ali Ashek, Michael R. Wilson, Masao Takata, Simon Padley, Deborah R. Gill, Stephen C. Hyde, Cliff Morgan, Eric W.F.W. Alton, Uta Griesenbach
المصدر: Molecular Therapy - Methods & Clinical Development. 25:382-391
مصطلحات موضوعية: autoimmune pulmonary alveolar proteinosis, PAP, granulocyte-macrophage colony-stimulating factor, lentiviral vector, Genetics, rSIV.F/HN, Molecular Medicine, GM-CSF, surfactant protein, alveolar macrophage, lung gene therapy, gene therapy, Molecular Biology
-
7
المؤلفون: Stephen C. Hyde, Catherine M. Green, Benjamin Wright, Altar M. Munis, Frederic Jackson, Helen Lockstone, Deborah R. Gill
المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 24, Iss, Pp 62-70 (2022)مصطلحات موضوعية: H441, surfactant, Context (language use), QH426-470, Biology, lung, Transcriptome, Alveolar cells, Parenchyma, Gene expression, otorhinolaryngologic diseases, Genetics, medicine, Molecular Biology, QH573-671, Interstitial lung disease, ATI, respiratory system, SALI, ATII, medicine.disease, In vitro, Cell biology, ALI, medicine.anatomical_structure, Cell culture, SPB, parenchyma, Molecular Medicine, Original Article, RNA-seq, Cytology
-
8
المؤلفون: Yue Du, Kamran M Miah, Omar Habib, Helena Meyer-Berg, Catriona C Conway, Mariana A Viegas, Rebecca Dean, Dwiantari Satyapertiwi, Jincun Zhao, Yanqun Wang, Nigel J Temperton, Toby P E Gamlen, Deborah R Gill, Stephen C Hyde
المصدر: Thorax. 77:1229-1236
مصطلحات موضوعية: QR355, Pulmonary and Respiratory Medicine, COVID-19 Vaccines, SARS-CoV-2, COVID-19, biochemical phenomena, metabolism, and nutrition, Antibodies, Viral, Antibodies, Neutralizing, Mice, Humans, Animals, Pandemics, Lung, Aged
وصف الملف: application/pdf
-
9
المؤلفون: Stephen C. Hyde, Julian C. Knight, Fadi Issa, Amy Cross, Damien J. Downes, S N Sansom, Nigel A. Roberts, Peng Hua, Ron Schwessinger, Olga Mielczarek, C. De Andrea, Davies Joj., Altar M. Munis, Antony J. Cutler, Jim R. Hughes, Deborah R. Gill, Ignacio Melero, Jill M. Brown, John A. Todd
المصدر: Nature Genetics. 53:1606-1615
مصطلحات موضوعية: Male, Leucine zipper, Epithelial-Mesenchymal Transition, Locus (genetics), Genome-wide association study, Biology, Polymorphism, Single Nucleotide, 03 medical and health sciences, 0302 clinical medicine, Genetics, Humans, Allele, Enhancer, Lung, Gene, Transcription factor, 030304 developmental biology, 0303 health sciences, SARS-CoV-2, Effector, COVID-19, Epithelial Cells, 3. Good health, Case-Control Studies, 030220 oncology & carcinogenesis, Cancer research, Female, Chromosomes, Human, Pair 3, Genome-Wide Association Study, Transcription Factors
-
10
المؤلفون: null Patricia P. Ogger, null Minerva Garcia Martín, null Christina Michalaki, null Jie Zhou, null Jonathan C. Brown, null Yue Du, null Kamran M. Miah, null Omar Habib, null Stephen C. Hyde, null Deborah R. Gill, null Wendy S. Barclay, null Cecilia Johansson
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::ab2b52f860cd194835530db57e0768f4
https://doi.org/10.1002/eji.202249913/v3/response1