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1دورية أكاديمية
المؤلفون: Heather L. Gray-Edwards, Anne S. Maguire, Nouha Salibi, Lauren E. Ellis, Taylor L. Voss, Elise B. Diffie, Jey Koehler, Ashley N. Randle, Amanda R. Taylor, Brandon L. Brunson, Thomas S. Denney, Ronald J. Beyers, Atoska S. Gentry, Amanda L. Gross, Ana R. Batista, Miguel Sena-Esteves, Douglas R. Martin
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 258-270 (2020)
مصطلحات موضوعية: gangliosidosis, GM1, lysosomal storage disease, adeno-associated virus, AAV, gene therapy, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2دورية أكاديمية
المؤلفون: Heather L. Gray-Edwards, Xuntian Jiang, Ashley N. Randle, Amanda R. Taylor, Taylor L. Voss, Aime K. Johnson, Victoria J. McCurdy, Miguel Sena-Esteves, Daniel S. Ory, Douglas R. Martin
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 135-142 (2017)
مصطلحات موضوعية: adeno-associated virus, AAV, biomarkers, feline, gene therapy, GM1 gangliosidosis, lipidomics, neurologic disease, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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3
المؤلفون: Ronald J. Beyers, Ana Rita Batista, Heather L. Gray-Edwards, Miguel Sena-Esteves, Thomas S. Denney, Ashley N. Randle, Lauren E. Ellis, Jey W. Koehler, Nouha Salibi, Anne S Maguire, Taylor L. Voss, Amanda L. Gross, Elise B. Diffie, Amanda R. Taylor, Atoska S. Gentry, Douglas R. Martin, Brandon L. Brunson
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 258-270 (2020)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, Cerebellum, Pathology, medicine.medical_specialty, spectroscopy, lcsh:QH426-470, Thalamus, GM1, adeno-associated virus, Gangliosidosis, medicine.disease_cause, Deep cerebellar nuclei, Article, 03 medical and health sciences, 0302 clinical medicine, Genetics, Lysosomal storage disease, Medicine, lcsh:QH573-671, Molecular Biology, Adeno-associated virus, business.industry, lcsh:Cytology, Neurodegeneration, biomarkers, AAV, medicine.disease, gangliosidosis, gene therapy, 3. Good health, Astrogliosis, lcsh:Genetics, 030104 developmental biology, medicine.anatomical_structure, lysosomal storage disease, 030220 oncology & carcinogenesis, Molecular Medicine, business, MRI
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4
المؤلفون: Ashley N. Randle, Aime K. Johnson, Heather L. Gray-Edwards, Xuntian Jiang, Victoria J. McCurdy, Daniel S. Ory, Taylor L. Voss, Miguel Sena-Esteves, Amanda R. Taylor, Douglas R. Martin
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 135-142 (2017)
Molecular Therapy. Methods & Clinical Developmentمصطلحات موضوعية: 0301 basic medicine, GM1 gangliosidosis, lcsh:QH426-470, Genetic enhancement, adeno-associated virus, Biology, medicine.disease_cause, Virus, 03 medical and health sciences, 0302 clinical medicine, Cerebrospinal fluid, Lipidomics, Genetics, medicine, feline, lcsh:QH573-671, Molecular Biology, Adeno-associated virus, CATS, lcsh:Cytology, biomarkers, AAV, gene therapy, neurologic disease, Sphingolipid, Pathophysiology, 3. Good health, carbohydrates (lipids), lcsh:Genetics, 030104 developmental biology, Immunology, lipidomics, Molecular Medicine, Original Article, lipids (amino acids, peptides, and proteins), 030217 neurology & neurosurgery