المؤلفون: Jean-Baptiste Ducloyer, Virginie Pichard, Mathieu Mevel, Anne Galy, Gaelle M. Lefevre, Nicole Brument, Dimitri Alvarez-Dorta, David Deniaud, Alexandra Mendes-Madeira, Lyse Libeau, Caroline Le Guiner, Therese Cronin, Oumeya Adjali, Michel Weber, Guylène Le Meur

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 387-393 (2023)

مصطلحات موضوعية: gene therapy, eye surgery, subretinal injection, air tamponade, fluid-air exchange, intravitreal, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050123000165; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/dc74dd4179c14ad388bcdc95456b14ed

المؤلفون: Juliette Varin, Clément Morival, Noémien Maillard, Oumeya Adjali, Therese Cronin

المصدر: International Journal of Molecular Sciences, Vol 22, Iss 23, p 12818 (2021)

مصطلحات موضوعية: immunogenicity, inflammation, gene therapy, AAV, Biology (General), QH301-705.5, Chemistry, QD1-999

وصف الملف: electronic resource

Relation: https://www.mdpi.com/1422-0067/22/23/12818; https://doaj.org/toc/1661-6596; https://doaj.org/toc/1422-0067

URL الوصول: https://doaj.org/article/416d58a39c6649e9b4c704152ca276c3

المؤلفون: Jean Bennett, Ying Yang, Emeline F. Nandrot, Therese Cronin, Daniel C. Chung

المصدر: Pharmaceuticals, Vol 5, Iss 5, Pp 447-459 (2012)

مصطلحات موضوعية: adeno-associated virus, retinal gene therapy, MFG-E8, avβ5 integrin, photoreceptor outer segments, Medicine, Pharmacy and materia medica, RS1-441

وصف الملف: electronic resource

Relation: http://www.mdpi.com/1424-8247/5/5/447; https://doaj.org/toc/1424-8247

URL الوصول: https://doaj.org/article/3a5311578c3b49d1ac51dca86f92c4bc

المؤلفون: Aurelien Leray, Pierre-Alban Lalys, Juliette Varin, Mohammed Bouzelha, Audrey Bourdon, Dimitri Alvarez-Dorta, Karine Pavageau, Sebastien Depienne, Maia Marchand, Anthony Mellet, Joanna Demilly, Jean-Baptiste Ducloyer, Tiphaine Girard, Bodval Fraysse, Mireille Ledevin, Mickael Guilbaud, Sebastien G. Gouin, Eduard Ayuso, Oumeya Adjali, Thibaut Larcher, Therese Cronin, Caroline Le Guiner, David Deniaud, Mathieu Mevel

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::33fdeaf96dcd33201a922c4fba14ec65
https://doi.org/10.26434/chemrxiv-2023-6xnn8

المؤلفون: C Audrain, Alexandra Mendes-Madeira, E Toublanc, L. Libeau, Carolina Isiegas, Nathalie Provost, J B Ducloyer, M Croyal, C Morival, Therese Cronin, Virginie Pichard, Oumeya Adjali

المساهمون: MOYON, Thomas, Laboratoire de Thérapie Génique Translationnelle des Maladies Génétiques / Translational Research in Gene Therapy - UMR_S 1089 (TARGET), Institut National de la Santé et de la Recherche Médicale (INSERM)-Nantes Université - UFR de Médecine et des Techniques Médicales (Nantes Univ - UFR MEDECINE), Nantes Université - pôle Santé, Nantes Université (Nantes Univ)-Nantes Université (Nantes Univ)-Nantes Université - pôle Santé, Nantes Université (Nantes Univ)-Nantes Université (Nantes Univ), Physiopathologie des Adaptations Nutritionnelles (PhAN), Université de Nantes - UFR de Médecine et des Techniques Médicales (UFR MEDECINE), Université de Nantes (UN)-Université de Nantes (UN)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), Centre hospitalier universitaire de Nantes (CHU Nantes)

المصدر: FASEB Journal
FASEB Journal, 2021, 35 (11), pp.1-17. ⟨10.1096/fj.202002525RRR⟩

مصطلحات موضوعية: Retinal degeneration, Transgene, [SDV]Life Sciences [q-bio], ABCA4, Retinol dehydrogenase, Biochemistry, chemistry.chemical_compound, Exon, Genetics, medicine, NADPH, Animals, Photoreceptor Cells, Vitamin A, Molecular Biology, retinol dehydrogenase, Gene knockdown, biology, Chemistry, Gene Transfer Techniques, Retinal, transgenic rat, medicine.disease, Rats, Cell biology, Stargardt disease, [SDV] Life Sciences [q-bio], Alcohol Oxidoreductases, Disease Models, Animal, retinoid toxicity, Gene Knockdown Techniques, biology.protein, ATP-Binding Cassette Transporters, Rats, Transgenic, NADP, Biotechnology

وصف الملف: application/pdf

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::18a14aab11435485a07c1ec9832814aa
https://hal.inrae.fr/hal-03793154/document

المؤلفون: Mathieu Mével, Virginie Pichard, Mohammed Bouzelha, Dimitri Alvarez-Dorta, Pierre-Alban Lalys, Nathalie Provost, Marine Allais, Alexandra Mendes, Elodie Landagaray, Jean-Baptiste Ducloyer, Estelle Toublanc, Anne Galy, Nicole Brument, Gaëlle M. Lefevre, Sébastien G. Gouin, Carolina Isiegas, Guylène Le Meur, Thérèse Cronin, Caroline Le Guiner, Michel Weber, Philippe Moullier, Eduard Ayuso, David Deniaud, Oumeya Adjali

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101187- (2024)

مصطلحات موضوعية: adeno-associated virus, chemistry, bioconjugation, gene therapy, retina, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000032; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/1edecadd12924319b147b4cab1a426f8

المؤلفون: Oumeya Adjali, Guylène Le Meur, Michel Weber, Therese Cronin, J.-B. Ducloyer

المساهمون: Service d'ophtalmologie [Nantes], Hôtel-Dieu, Laboratoire de Thérapie Génique Translationnelle des Maladies Génétiques (Inserm UMR 1089), Institut National de la Santé et de la Recherche Médicale (INSERM)-Université de Nantes - UFR de Médecine et des Techniques Médicales (UFR MEDECINE), Université de Nantes (UN)-Université de Nantes (UN), Université de Nantes - UFR de Médecine et des Techniques Médicales (UFR MEDECINE), Université de Nantes (UN)-Université de Nantes (UN)-Institut National de la Santé et de la Recherche Médicale (INSERM), Cronin, Therese

المصدر: médecine/sciences
médecine/sciences, EDP Sciences, 2020, 36 (6-7), pp.607-615. ⟨10.1051/medsci/2020095⟩

مصطلحات موضوعية: Blinding, [SDV.BIO]Life Sciences [q-bio]/Biotechnology, Retinal dystrophy, Genetic enhancement, [SDV.BBM.BM] Life Sciences [q-bio]/Biochemistry, Molecular Biology/Molecular biology, Bioinformatics, Marketing authorization, General Biochemistry, Genetics and Molecular Biology, Food and drug administration, 03 medical and health sciences, 0302 clinical medicine, Retinitis pigmentosa, Medicine, Incurable diseases, 030304 developmental biology, [SDV.IB] Life Sciences [q-bio]/Bioengineering, 0303 health sciences, business.industry, [SDV.BBM.BM]Life Sciences [q-bio]/Biochemistry, Molecular Biology/Molecular biology, General Medicine, Leber congenital amaurosis, medicine.disease, [SDV.BIO] Life Sciences [q-bio]/Biotechnology, 3. Good health, 030221 ophthalmology & optometry, [SDV.IB]Life Sciences [q-bio]/Bioengineering, business

وصف الملف: application/pdf

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b5e6bb47941a7e0d317302333277418a
https://www.hal.inserm.fr/inserm-02894145/document

المؤلفون: Noémien Maillard, Oumeya Adjali, Juliette Varin, Clément Morival, Therese Cronin

المصدر: International Journal of Molecular Sciences
International Journal of Molecular Sciences, Vol 22, Iss 12818, p 12818 (2021)

مصطلحات موضوعية: QH301-705.5, Genetic enhancement, Genetic Vectors, Review, immunogenicity, Gene mutation, Bioinformatics, Catalysis, Inorganic Chemistry, chemistry.chemical_compound, Immune system, Retinal Diseases, Transduction, Genetic, medicine, Animals, Humans, Biology (General), Physical and Theoretical Chemistry, QD1-999, Molecular Biology, Spectroscopy, Retina, Innate immune system, business.industry, Immunogenicity, Organic Chemistry, AAV, Retinal, Genetic Therapy, General Medicine, Dependovirus, gene therapy, Computer Science Applications, Clinical trial, Chemistry, medicine.anatomical_structure, chemistry, inflammation, business

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::03489ee3e255c307170221eb12495c46
https://doi.org/10.3390/ijms222312818

المؤلفون: Aurélien Leray, Pierre-Alban Lalys, Juliette Varin, Mohammed Bouzelha, Audrey Bourdon, Dimitri Alvarez-Dorta, Karine Pavageau, Sébastien Depienne, Maia Marchand, Anthony Mellet, Joanna Demilly, Jean-Baptiste Ducloyer, Tiphaine Girard, Bodvaël Fraysse, Mireille Ledevin, Mickaël Guilbaud, Sébastien G. Gouin, Eduard Ayuso, Oumeya Adjali, Thibaut Larcher, Thérèse Cronin, Caroline Le Guiner, David Deniaud, Mathieu Mével

المصدر: Biomedicine & Pharmacotherapy, Vol 171, Iss , Pp 116148- (2024)

مصطلحات موضوعية: Adeno-associated virus, Bioconjugation, Tyrosine, Targeting, Liver, Retina, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S0753332224000295; https://doaj.org/toc/0753-3322

URL الوصول: https://doaj.org/article/1ed978775aad41fbbbc3787da57c93b5

المؤلفون: Tomas S. Aleman, Pavitra S. Ramachandran, Jean Bennett, Zhangyong Wei, Ji Yun Song, Keirnan Willett, Therese Cronin, Jessica I. W. Morgan, Giulia Casal, Rachel M. Huckfeldt, Albert M. Maguire, Vivian S. Lee

مصطلحات موضوعية: 0301 basic medicine, Primates, Cell type, Genetic enhancement, Genetic Vectors, Biology, Virus, Retina, 03 medical and health sciences, chemistry.chemical_compound, Transduction (genetics), 0302 clinical medicine, Immune system, Genetics, medicine, Animals, Humans, Molecular Biology, Review Articles, Retinal Degeneration, Retinal, Genetic Therapy, Dependovirus, Clinical trial, 030104 developmental biology, medicine.anatomical_structure, chemistry, 030220 oncology & carcinogenesis, Immunology, Molecular Medicine

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::2535c8401489a2356504fd62530f58ac
https://europepmc.org/articles/PMC5312498/