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المؤلفون: So Hyun Park, Mingming Cao, Yidan Pan, Timothy H. Davis, Lavanya Saxena, Harshavardhan Deshmukh, Yilei Fu, Todd Treangen, Vivien A. Sheehan, Gang Bao
المصدر: Science advances. 8(42)
مصطلحات موضوعية: Gene Editing, Multidisciplinary, Programmed Cell Death 1 Receptor, Humans, CRISPR-Cas Systems, Hematopoietic Stem Cells, Cell Line
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::185888a3783d87264d35c1958c53b894
https://pubmed.ncbi.nlm.nih.gov/36269834 -
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المؤلفون: Yidan Pan, Gang Bao, Timothy H. Davis, Ciaran M. Lee, X. Robert Bao
المصدر: Nat Protoc
مصطلحات موضوعية: High-effeciency, Computer science, In silico, Computational biology, Web tool, Genome, Article, General Biochemistry, Genetics and Molecular Biology, In-vitro, 03 medical and health sciences, 0302 clinical medicine, Genome editing, Dna cleavage, Genome-wide analysis, Animals, Humans, Unbiased detection, CAS9, 030304 developmental biology, Gene Editing, DNA cleavage, 0303 health sciences, Cas9, High-Throughput Nucleotide Sequencing, Genomics, Amplicon, Endonucleases, Zinc finger nuclease, Stem-cells, Double-stranded breaks, Zinc-finger nucleases, CRISPR-Cas Systems, 030217 neurology & neurosurgery, Reference genome
وصف الملف: application/pdf
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المؤلفون: Alexandria M. Doerfler, Christine Beeton, Kelsey E Jarrett, Ang Li, Marco De Giorgi, Mark R. Tanner, William R. Lagor, Timothy H. Davis, Ciaran M. Lee, Gang Bao, Ayrea Hurley
المصدر: Molecular Therapy
مصطلحات موضوعية: AAV-CRISPR, Genetic enhancement, pre-existing immunity, adeno-associated virus, Biology, liver, medicine.disease_cause, Genome, immune response, 03 medical and health sciences, 0302 clinical medicine, Immune system, Genome editing, Drug Discovery, Genetics, medicine, CRISPR, Clustered Regularly Interspaced Short Palindromic Repeats, Gene and molecular therapy, Molecular Biology, Adeno-associated virus, 030304 developmental biology, Gene Editing, Pharmacology, 0303 health sciences, Cas9, somatic genome editing, SaCas9, gene therapy, Virology, Liver regeneration, 030220 oncology & carcinogenesis, Molecular Medicine, Original Article, hepatocytes, CRISPR-Cas Systems, CD8+ T cell
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0a03e82596d4aabb913f05e713551232
https://doi.org/10.1016/j.ymthe.2020.04.017 -
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المؤلفون: Gang Bao, Vivien A. Sheehan, Matthew H. Porteus, Alireza Paikari, So Hyun Park, Waracharee Srifa, Yankai Zhang, Alicia K Chang, Timothy H. Davis, Ciaran M. Lee, Joab Camarena, Daniel P. Dever
المصدر: Nucleic Acids Research
مصطلحات موضوعية: Erythrocytes, medicine.medical_treatment, Anemia, Sickle Cell, Mice, SCID, beta-Globins, Hematopoietic stem cell transplantation, Genome Integrity, Repair and Replication, Biology, Mice, 03 medical and health sciences, 0302 clinical medicine, Mice, Inbred NOD, Cell Line, Tumor, Genetics, medicine, Animals, Humans, Progenitor cell, Cells, Cultured, 030304 developmental biology, Gene Editing, Mice, Knockout, 0303 health sciences, Hematopoietic Stem Cell Transplantation, Genetic Therapy, Hematopoietic Stem Cells, medicine.disease, Sickle cell anemia, 3. Good health, Transplantation, Haematopoiesis, Treatment Outcome, medicine.anatomical_structure, 030220 oncology & carcinogenesis, Cancer research, Bone marrow, CRISPR-Cas Systems, Stem cell, K562 Cells, K562 cells
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::b76f1bd8a03d5ae500c3537167d80c57
https://doi.org/10.1093/nar/gkz475 -
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المؤلفون: Jayakar V. Nayak, Ron Baik, Calvin Kuo, Matthew H. Porteus, Ameen A. Salahudeen, Christopher A. Teran, Zachary M. Sellers, Shayda M. Abazari, Dawn T. Bravo, Jeffrey J. Wine, Lu Chen, Carlos Suárez, Amanda M. Dudek, Tushar J. Desai, Gang Bao, Scott H. Randell, Steven E. Artandi, Timothy H. Davis, Ciaran M. Lee, Sriram Vaidyanathan
المصدر: Mol Ther
مصطلحات موضوعية: Cystic Fibrosis, medicine.medical_treatment, Cystic Fibrosis Transmembrane Conductance Regulator, medicine.disease_cause, Cystic fibrosis, CD19, 03 medical and health sciences, 0302 clinical medicine, Complementary DNA, Drug Discovery, Genetics, medicine, Humans, Molecular Biology, Gene, 030304 developmental biology, Pharmacology, 0303 health sciences, Mutation, biology, Stem Cells, Epithelial Cells, Stem-cell therapy, respiratory system, medicine.disease, Molecular biology, Transmembrane protein, Cystic fibrosis transmembrane conductance regulator, respiratory tract diseases, 030220 oncology & carcinogenesis, biology.protein, Molecular Medicine, Original Article, Stem cell, CRISPR-Cas Systems
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0ca7c86485eaf6ebaa5472a15abfe3b5
https://europepmc.org/articles/PMC8753290/ -
6Examination of CRISPR/Cas9 design tools and the effect of target site accessibility on Cas9 activity
المؤلفون: Timothy H. Davis, Ciaran M. Lee, Gang Bao
المصدر: Exp Physiol
مصطلحات موضوعية: 0301 basic medicine, Active target, Gene Editing, Genome, Computer science, Cas9, General Medicine, Experimental validation, Computational biology, DNA, Bioinformatics, Article, Genome engineering, 03 medical and health sciences, 030104 developmental biology, Target site, CRISPR-Associated Protein 9, CRISPR, Animals, Humans, Guide RNA, CRISPR-Cas Systems, Adaptation (computer science), RNA, Guide, Kinetoplastida
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المؤلفون: Ciaran M, Lee, Haibao, Zhu, Timothy H, Davis, Harshahardhan, Deshmukh, Gang, Bao
المصدر: Methods in molecular biology (Clifton, N.J.). 1498
مصطلحات موضوعية: Gene Editing, Pluripotent Stem Cells, HEK293 Cells, Genome, Human, Humans, Clustered Regularly Interspaced Short Palindromic Repeats, RNA Editing, CRISPR-Cas Systems, Cell Line
URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::c796e883e7632a8d09bdb067d3b19662
https://pubmed.ncbi.nlm.nih.gov/27709565 -
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المؤلفون: Timothy H. Davis, Ciaran M. Lee, Haibao Zhu, Harshahardhan Deshmukh, Gang Bao
المصدر: Methods in Molecular Biology ISBN: 9781493964703
مصطلحات موضوعية: 0301 basic medicine, chemistry.chemical_classification, Genetics, Gene Modification, Computer science, Cas9, HEK 293 cells, 03 medical and health sciences, genomic DNA, 030104 developmental biology, 0302 clinical medicine, chemistry, Genome editing, RNA editing, CRISPR, Human genome, Nucleotide, Induced pluripotent stem cell, 030217 neurology & neurosurgery
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::17ed19b829e1c5324eea2a1aa562a8dc
https://doi.org/10.1007/978-1-4939-6472-7_1 -
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المؤلفون: Yankai Zhang, Matthew H. Porteus, Daniel P. Dever, So Hyun Park, Joab Camarena, Vivian A Sheehan, Gang Bao, Timothy H. Davis, Ciaran M. Lee
المصدر: Blood. 132:2192-2192
مصطلحات موضوعية: Immunology, CD34, Cell Biology, Hematology, Human leukocyte antigen, Biology, Biochemistry, Molecular biology, CD19, Transplantation, Haematopoiesis, medicine.anatomical_structure, medicine, biology.protein, Bone marrow, Stem cell, Progenitor cell
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::537268efffc16f5f144ad3ac6f91a692
https://doi.org/10.1182/blood-2018-99-117371 -
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المؤلفون: Thomas J. Cradick, Timothy H. Davis, Ciaran M. Lee, Toni Cathomen, Maximilian Müller, Gang Bao, Giedrius Gasiunas, Claudio Mussolino, Virginijus Siksnys
مصطلحات موضوعية: 0301 basic medicine, Genetic Vectors, Biology, medicine.disease_cause, Genome, Cell Line, Substrate Specificity, 03 medical and health sciences, Genome editing, Drug Discovery, Genetics, medicine, CRISPR, Humans, Streptococcus thermophilus, Guide RNA, Molecular Biology, Pharmacology, Gene Editing, Binding Sites, Base Sequence, Cas9, Genome, Human, Endonucleases, Enzyme Activation, Protospacer adjacent motif, 030104 developmental biology, Streptococcus pyogenes, Molecular Medicine, Human genome, Original Article, CRISPR-Cas Systems, Protein Binding, RNA, Guide, Kinetoplastida
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::89656265a72303f9d443b756d8d84be6
https://europepmc.org/articles/PMC4786917/