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1دورية أكاديمية
المؤلفون: McDonald, CM, Muntoni, F, Penematsa, V, Jiang, J, Kristensen, A, Bibbiani, F, Goodwin, E, Gordish-Dressman, H, Morgenroth, L, Werner, C, Li, J, Able, R, Trifillis, P, Tulinius, M
المصدر: Journal of comparative effectiveness research. 11(3):139-155
مصطلحات موضوعية: Medicin och hälsovetenskap
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2دورية أكاديمية
المؤلفون: Shieh, PB, Elfring, G, Trifillis, P, Santos, C, Peltz, SW, Parsons, JA, Apkon, S, Darras, BT, Campbell, C, McDonald, CM
المصدر: Journal of comparative effectiveness research. 10(18):1337-1347
مصطلحات موضوعية: Medicin och hälsovetenskap
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3دورية أكاديمية
المؤلفون: Mercuri, Eugenio, Osorio, Andrés, Muntoni, Francesco, Buccella, Filippo, Desguerre, Isabelle, Kirschner, Janbernd, Tulinius, Már, de Resende, Maria, Morgenroth, Lauren, Gordish-Dressman, Heather, Johnson, Shelley, Kristensen, Allan, Werner, Christian, Trifillis, Panayiota, Henricson, Erik, McDonald, Craig
المصدر: Journal of Neurology. 270(8)
مصطلحات موضوعية: Ataluren, Effectiveness, Nonsense mutation Duchenne muscular dystrophy, STRIDE Registry, Safety, Humans, Codon, Nonsense, Muscular Dystrophy, Duchenne, Registries, Disease Progression
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/08q7827w
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4دورية أكاديمية
المؤلفون: Campbell, C, Barohn, RJ, Bertini, E, Chabrol, B, Comi, GP, Darras, BT, Finkel, RS, Flanigan, KM, Goemans, N, Iannaccone, ST, Jones, KJ, Kirschner, J, Mah, JK, Mathews, KD, McDonald, CM, Mercuri, E, Nevo, Y, Pereon, Y, Ben Renfroe, J, Ryan, MM, Sampson, JB, Schara, U, Sejersen, T, Selby, K, Tulinius, M, Vilchez, JJ, Voit, T, Wei, LJ, Wong, BL, Elfring, G, Souza, M, McIntosh, J, Trifillis, P, Peltz, SW, Muntoni, F
المصدر: Journal of comparative effectiveness research. 9(14):973-984
مصطلحات موضوعية: Medicin och hälsovetenskap
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5دورية أكاديمية
المؤلفون: Marden, Jessica, Shieh, Perry, Wong, Brenda, Lane, Henry, Zhang, Adina, Nguyen, Ha, Frean, Molly, Trifillis, Panayiota, Koladicz, Karyn, Signorovitch, James, McDonald, Craig
المصدر: Journal of Comparative Effectiveness Research. 12(4)
مصطلحات موضوعية: Duchenne muscular dystrophy, clinical outcomes, deflazacort, disease milestones, efficacy, prednisone/prednisolone, Child, Humans, Adrenal Cortex Hormones, Disease Progression, Functional Status, Muscular Dystrophy, Duchenne, Prednisone
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/8n5030xk
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6دورية أكاديمية
المؤلفون: Mayer, Oscar, Hor, Kan, Miller, Debra, Goemans, Nathalie, Henricson, Erik, Marden, Jessica, Freimark, Jonathan, Lane, Henry, Zhang, Adina, Frean, Molly, Trifillis, Panayiota, Koladicz, Karyn, Signorovitch, James, McDonald, Craig
المصدر: Journal of Neuromuscular Diseases. 10(1)
مصطلحات موضوعية: Duchenne muscular dystrophy, Treatment outcome, ambulation, deflazacort, prednisone, Male, Humans, Adolescent, Prednisone, Stroke Volume, Longitudinal Studies, Quality of Life, Ventricular Function, Left, Muscular Dystrophy, Duchenne, Disease Progression
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/7cm0x7r4
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7دورية أكاديمية
المؤلفون: Thangarajh, M, Elfring, GL, Trifillis, P, McIntosh, J, Peitz, SW, Ryan, MM, Kornberg, AJ, RodriguezCasero, V, Wray, A, Jones, KJ, North, K, Goemans, N, Buyse, GM, Campbell, C, Mah, J, Sarnat, H, Selby, K, Voit, T, Doppler, V, De Castro, D, Chabrol, B, Levy, N, Halbert, C, Pereon, Y, Magot, A, Perrier, J, Mahe, JY, Schara, U, Lutz, S, Busse, M, Della Marina, A, Kirschner, J, Stanescu, A, Pohl, A, RensingZimmerman, C, Bertini, E, D'Amico, A, Kofler, A, Carlesi, A, Bonetti, AM, Santecchia, L, Emma, F, Bergami, G, Mercuri, EM, Vasco, G, Bianco, F, Mazzone, ES, De Sanctis, R, Alfieri, P, Pane, M, Messina, S, Comi, GP, Magri, F, Lucchini, V, Corti, SP, Moggio, MG, Sciacco, M, Bresolin, N, Prelle, AC, Magri, R, Virgilio, R, Lamperti, C, Nevo, Y, DorWollman, T, Vilchez, J, Muelas, N, Sevilla, T, Smeyers, P, de la Osa, A, Colomer, J, Ortez, CI, Nascimento, A, Febrer, A, Medina, J, Tulinus, M, Thorarinsdottir, B, Darin, N, Sejersen, T, Hovmoller, M, Bushby, K, Straub, V, Guglieri, M, Sarkozy, A, Willis, T, Eagle, M, Mayhew, A, Muntoni, F, Cirak, S, Manzur, AY, Robb, SA, Kinali, M, Quinlivan, RCM, Smith, MR, Pandey, R, Wong, B, Collins, J, Finkel, R, Bonnemann, C, Yang, M, Foley, AR, Yum, S, Sampson, J, Bromberg, M, Swoboda, K, Day, J, Karachunski, P, Mathews, K, Bonthius, D, Laubenthal, KS, Darras, B, Kang, P, Parson, J, Barohn, R, Dasouki, M, Anderson, H, Burns, J, Dimachkie, M, Pasnoor, M, Wang, YX, Ciafaloni, E, Heatwole, C, Connolly, A, Pestronk, A, Al-Lozi, M, Lopate, G, Golumbek, P, Sommerville, B, Wang, L, Wojcicka-Mitchell, A, Godbey, A, Harms, M, Varadachary, A, Iyadurai, S, Rojas, L, Iannacone, S, Khonghatithum, C, Sproule, D, De Vivo, D, Constantinescu, A, McDonald, C, Han, J, Ben Renfroe, Russman, B, Sussman, M, BurnsWechsler, S, Juel, V, Hobson-Webb, L, Smith, E
المصدر: Neurology. 91(13):E1215-E1219
مصطلحات موضوعية: Medicin och hälsovetenskap
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8دورية أكاديمية
المؤلفون: Muntoni, Francesco, Penematsa, Vinay, Jiang, Joel, Kristensen, Allan, Bibbiani, Francesco, Goodwin, Elizabeth, Gordish-Dressman, Heather, Morgenroth, Lauren, Werner, Christian, Li, James, Able, Richard, Trifillis, Panayiota, Tulinius, Már, McDonald, Craig
المصدر: Journal of Comparative Effectiveness Research. 11(3)
مصطلحات موضوعية: Study 019, ataluren, dystrophin, efficacy, loss of ambulation, nonsense mutation Duchenne muscular dystrophy, respiratory function, Codon, Nonsense, Humans, Muscular Dystrophy, Duchenne, Oxadiazoles, Walking
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/2m69426z
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9دورية أكاديمية
المؤلفون: Wei, Lee-Jen, Flanigan, Kevin, Elfring, Gary, Trifillis, Panayiota, Muntoni, Francesco, McDonald, Craig
المصدر: Muscle and Nerve. 64(5)
مصطلحات موضوعية: Duchenne muscular dystrophy, efficacy, motor function, outcome measure, treatment, Clinical Trials, Phase III as Topic, Humans, Muscular Dystrophy, Duchenne, Prednisolone, Prednisone, Randomized Controlled Trials as Topic, Treatment Failure
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/2640p3bs
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10دورية أكاديمية
المؤلفون: Mercuri, EugenioAff1, Aff2, IDs00415023118642_cor1, Osorio, Andrés Nascimento, Muntoni, FrancescoAff4, Aff5, Buccella, Filippo, Desguerre, Isabelle, Kirschner, Janbernd, Tulinius, Már, de Resende, Maria Bernadete Dutra, Morgenroth, Lauren P., Gordish-Dressman, Heather, Johnson, Shelley, Kristensen, Allan, Werner, Christian, Trifillis, Panayiota, Henricson, Erik K., McDonald, Craig M.
المصدر: Journal of Neurology. 270(9):4583-4583