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1دورية أكاديمية
المؤلفون: Cavazza, A, Hendel, A, Bak, RO, Rio, P, Guell, M, Lainscek, D, Arechavala-Gomeza, V, Peng, L, Hapil, FZ, Harvey, J, Ortega, FG, Gonzalez-Martinez, C, Lederer, CW, Mikkelsen, K, Gasiunas, G, Kalter, N, Goncalves, MAFV, Petersen, J, Garanto, A, Montoliu, L, Maresca, M, Seemann, SE, Gorodkin, J, Mazini, L, Sanchez, R, Rodriguez-Madoz, JR, Maldonado-Perez, N, Laura, T, Schmueck-Henneresse, M, Maccalli, C, Grunewald, J, Carmona, G, Kachamakova-Trojanowska, N, Miccio, A, Martin, F, Turchiano, G, Cathomen, T, Luo, YL, Tsai, SQ, Benabdellah, K
المصدر: Molecular therapy. Nucleic acids. 34:102066
مصطلحات موضوعية: Medicin och hälsovetenskap
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2دورية أكاديمية
المؤلفون: Tsai, SQ, Zheng, Z, Nguyen, NT, Liebers, M, Topkar, VV, Thapar, V, Wyvekens, N, Khayter, C, Iafrate, AJ, Le, LP, Aryee, MJ, Joung, JK
المصدر: Nature biotechnology. 33(2):187-197
مصطلحات موضوعية: Medicin och hälsovetenskap
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3دورية أكاديمية
المؤلفون: Costello, Joseph, Maeder, ML, Angstman, JF, Richardson, ME, Linder, SJ, Cascio, VM, Tsai, SQ, Ho, QH, Sander, JD, Reyon, D, Bernstein, BE
URL الوصول: https://escholarship.org/uc/item/8nz114dh
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4دورية أكاديمية
المؤلفون: Kleinstiver, BP, Prew, MS, Tsai, SQ, Topkar, VV, Nguyen, NT, Zheng, ZL, Gonzales, APW, Li, ZY, Peterson, RT, Yeh, JRJ, Aryee, MJ, Joung, JK
المصدر: Nature. 523(7561):481-U249
مصطلحات موضوعية: Medicin och hälsovetenskap
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5مؤتمرDefining Genome-Wide Off-Target Cleavage Profiles of CRISPR-Cas RNA-Guided Nucleases Using GUIDE-Seq
المؤلفون: Tsai, SQ, Zheng, ZL, Nguyen, NT, Liebers, M, Topkar, VV, Thapar, V, Wyvekens, N, Khayter, C
المصدر: MOLECULAR THERAPY. 23:S274-S274
مصطلحات موضوعية: Medicin och hälsovetenskap
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6دورية أكاديمية
المؤلفون: Katta V; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., O'Keefe K; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Li Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Mayurathan T; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Wood RK; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Levine RM; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Powers A; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Mayberry K; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Manquen G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Yao Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Zhang J; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Jang Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Nimmagadda N; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Dempsey EA; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Lee G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Uchida N; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute / National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Health Bethesda, MD, USA., Cheng Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Fazio F; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Lockey T; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Meagher M; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Sharma A; Department of Bone Marrow Transplantation & Cellular Therapy, St. Jude Children's Research Hospital, Memphis, TN, USA., Tisdale JF; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute / National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Health Bethesda, MD, USA., Zhou S; Experimental & Cellular Therapeutics Lab, St. Jude Children's Research Hospital, Memphis, TN, USA., Yen JS; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: shengdar.tsai@stjude.org., Weiss MJ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: shengdar.tsai@stjude.org., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: shengdar.tsai@stjude.org.
المصدر: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Jul 30. Date of Electronic Publication: 2024 Jul 30.
نوع المنشور: Journal Article
بيانات الدورية: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
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7دورية أكاديمية
المؤلفون: Garaudé S; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Marone R; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Lepore R; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland.; Cimeio Therapeutics, Basel, Switzerland., Devaux A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Beerlage A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland.; Department of Hematology, Basel University Hospital, Basel, Switzerland., Seyres D; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Dell' Aglio A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Juskevicius D; Department of Laboratory Medicine, Diagnostic Hematology, Basel University Hospital, Basel, Switzerland., Zuin J; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Burgold T; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Wang S; Division of Hematology, Department of Oncology, Geneva University Hospitals, Geneva, Switzerland., Katta V; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Manquen G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Li Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Larrue C; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland.; Centre de Recherches en Cancérologie de Toulouse, Université de Toulouse, Inserm, CNRS, Toulouse, France., Camus A; Cimeio Therapeutics, Basel, Switzerland., Durzynska I; Ridgeline Discovery, Basel, Switzerland., Wellinger LC; Ridgeline Discovery, Basel, Switzerland., Kirby I; ADC Therapeutics (UK), London, UK., Van Berkel PH; ADC Therapeutics (UK), London, UK., Kunz C; Ridgeline Discovery, Basel, Switzerland., Tamburini J; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland., Bertoni F; Institute of Oncology Research, Faculty of Biomedical Sciences, USI, Bellinzona, Switzerland.; Oncology Institute of Southern Switzerland, Ente Ospedaliero Cantonale, Bellinzona, Switzerland., Widmer CC; Department of Hematology, Basel University Hospital, Basel, Switzerland.; Department of Laboratory Medicine, Diagnostic Hematology, Basel University Hospital, Basel, Switzerland., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Simonetta F; Division of Hematology, Department of Oncology, Geneva University Hospitals, Geneva, Switzerland.; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland., Urlinger S; Cimeio Therapeutics, Basel, Switzerland., Jeker LT; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland. lukas.jeker@unibas.ch.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland. lukas.jeker@unibas.ch.; Innovation Focus Cell Therapy, Basel University Hospital, Basel, Switzerland. lukas.jeker@unibas.ch.
المصدر: Nature [Nature] 2024 Jun; Vol. 630 (8017), pp. 728-735. Date of Electronic Publication: 2024 May 22.
نوع المنشور: Journal Article
بيانات الدورية: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 0410462 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-4687 (Electronic) Linking ISSN: 00280836 NLM ISO Abbreviation: Nature Subsets: MEDLINE
مواضيع طبية MeSH: Hematologic Neoplasms*/drug therapy , Hematologic Neoplasms*/therapy , Hematologic Neoplasms*/immunology , Hematopoiesis*/drug effects , Immunoconjugates*/pharmacology , Immunoconjugates*/therapeutic use , Leukocyte Common Antigens*/immunology , Leukocyte Common Antigens*/metabolism, Animals ; Female ; Humans ; Male ; Mice ; Hematopoietic Stem Cell Transplantation ; Hematopoietic Stem Cells/cytology ; Hematopoietic Stem Cells/drug effects ; Hematopoietic Stem Cells/metabolism ; Cell Line, Tumor ; Antibody Specificity
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8
المصدر: BioRxiv : the preprint server for biology [bioRxiv] 2024 Mar 30. Date of Electronic Publication: 2024 Mar 30.
نوع المنشور: Preprint
بيانات الدورية: Country of Publication: United States NLM ID: 101680187 Publication Model: Electronic Cited Medium: Internet NLM ISO Abbreviation: bioRxiv Subsets: PubMed not MEDLINE
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9
المؤلفون: Shankar K, Zingler-Hoslet I, Shi L, Katta V, Russell BE, Tsai SQ, Capitini CM, Saha K
المصدر: BioRxiv : the preprint server for biology [bioRxiv] 2024 Feb 14. Date of Electronic Publication: 2024 Feb 14.
نوع المنشور: Preprint
بيانات الدورية: Country of Publication: United States NLM ID: 101680187 Publication Model: Electronic Cited Medium: Internet NLM ISO Abbreviation: bioRxiv Subsets: PubMed not MEDLINE
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10دورية أكاديمية
المؤلفون: Alves CRR; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA. calves2@mgh.harvard.edu.; Department of Neurology, Massachusetts General Hospital, Boston, MA, USA. calves2@mgh.harvard.edu.; Department of Neurology, Harvard Medical School, Boston, MA, USA. calves2@mgh.harvard.edu., Ha LL; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA., Yaworski R; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Sutton ER; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Christie KA; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Harvard Medical School, Boston, MA, USA., Reilly A; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Beauvais A; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Doll RM; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA.; Molecular Biosciences/Cancer Biology Program, Heidelberg University and German Cancer Research Center (DKFZ), Heidelberg, Germany., de la Cruz D; Molecular Neurogenetics Unit, Department of Neurology, Massachusetts General Hospital, Charlestown, MA, USA.; Program in Neuroscience, Harvard Medical School, Boston, MA, USA., Maguire CA; Molecular Neurogenetics Unit, Department of Neurology, Massachusetts General Hospital, Charlestown, MA, USA.; Program in Neuroscience, Harvard Medical School, Boston, MA, USA., Swoboda KJ; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Neurology, Massachusetts General Hospital, Boston, MA, USA.; Department of Neurology, Harvard Medical School, Boston, MA, USA., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Kothary R; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada.; Department of Medicine, University of Ottawa, Ottawa, Ontario, Canada., Kleinstiver BP; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.; Department of Pathology, Harvard Medical School, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.
المصدر: Nature biomedical engineering [Nat Biomed Eng] 2024 Feb; Vol. 8 (2), pp. 118-131. Date of Electronic Publication: 2023 Dec 06.
نوع المنشور: Journal Article
بيانات الدورية: Publisher: Springer Nature Country of Publication: England NLM ID: 101696896 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2157-846X (Electronic) Linking ISSN: 2157846X NLM ISO Abbreviation: Nat Biomed Eng Subsets: MEDLINE
مواضيع طبية MeSH: RNA-Binding Proteins*/genetics , RNA-Binding Proteins*/metabolism , Muscular Atrophy, Spinal*/genetics , Muscular Atrophy, Spinal*/therapy, Mice ; Animals ; Humans ; SMN Complex Proteins/genetics ; RNA, Guide, CRISPR-Cas Systems ; Exons/genetics ; Survival of Motor Neuron 2 Protein/genetics